A phase Ib study of sonidegib (LDE225), an oral small molecule inhibitor of smoothened or Hedgehog pathway, in combination with docetaxel in triple negative advanced breast cancer patients: GEICAM/2012-12 (EDALINE) study.


Journal

Investigational new drugs
ISSN: 1573-0646
Titre abrégé: Invest New Drugs
Pays: United States
ID NLM: 8309330

Informations de publication

Date de publication:
02 2019
Historique:
received: 05 04 2018
accepted: 24 05 2018
pubmed: 28 6 2018
medline: 22 1 2020
entrez: 28 6 2018
Statut: ppublish

Résumé

Up-regulation of the Hedgehog (Hh) pathway is implicated in the genesis of a wide range of tumors including triple negative breast cancer (TNBC). Sonidegib is a potent and selective oral inhibitor of Smo, a key component of the Hh signaling pathway. We designed a phase I clinical study to explore the combination of sonidegib plus docetaxel (fixed dose at 75 mg/m

Identifiants

pubmed: 29948356
doi: 10.1007/s10637-018-0614-9
pii: 10.1007/s10637-018-0614-9
doi:

Substances chimiques

Biphenyl Compounds 0
Pyridines 0
SMO protein, human 0
Smoothened Receptor 0
sonidegib 0RLU3VTK5M
Docetaxel 15H5577CQD

Banques de données

ClinicalTrials.gov
['NCT02027376']

Types de publication

Clinical Trial, Phase I Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

98-108

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Auteurs

Manuel Ruiz-Borrego (M)

Department of Medical Oncology, Hospital Universitario Virgen del Rocío, Sevilla, Spain.

Begoña Jimenez (B)

Department of Medical Oncology, Hospital Clínico Universitario Virgen de la Victoria, IBIMA, Málaga, Spain.

Silvia Antolín (S)

Department of Medical Oncology, Complejo Hospitalario Universitario A Coruña, A Coruña, Spain.

Jose A García-Saenz (JA)

Department of Medical Oncology, IdISSC, CIBERONC-ISCIII, Hospital Clínico San Carlos, Madrid, Spain.

Jesús Corral (J)

Department of Medical Oncology, Hospital Universitario Virgen del Rocío, Sevilla, Spain.

Yolanda Jerez (Y)

Department of Medical Oncology, Instituto de Investigación Sanitaria Gregorio Marañón, Madrid, Spain.

José Trigo (J)

Department of Medical Oncology, Hospital Clínico Universitario Virgen de la Victoria, IBIMA, Málaga, Spain.

Ander Urruticoechea (A)

Department of Medical Oncology, Fundación Onkologikoa, San Sebastián, Spain.

Helena Colom (H)

Department of Biopharmaceutics and Pharmacokinetics, School of Pharmacy, University of Barcelona, Barcelona, Spain.

Nuria Gonzalo (N)

Department of Pharmacy, IDIBELL, Catalan Institute of Oncology, Hospital Duran i Reynals, L'Hospitalet de Llobregat, Barcelona, Spain.

Carmen Muñoz (C)

Department of Pharmacy, IDIBELL, Catalan Institute of Oncology, Hospital Duran i Reynals, L'Hospitalet de Llobregat, Barcelona, Spain.

Sara Benito (S)

GEICAM, Spanish Breast Cancer Group, San Sebastián de los Reyes, Madrid, Spain.

Rosalía Caballero (R)

GEICAM, Spanish Breast Cancer Group, San Sebastián de los Reyes, Madrid, Spain.

Susana Bezares (S)

GEICAM, Spanish Breast Cancer Group, San Sebastián de los Reyes, Madrid, Spain.

Eva Carrasco (E)

GEICAM, Spanish Breast Cancer Group, San Sebastián de los Reyes, Madrid, Spain.

Federico Rojo (F)

Department of Pathology, Instituto de Investigación Sanitaria Fundación Jiménez Díaz, Centro de Investigación Biomédica en Red de Oncología, CIBERONC-ISCIII, Madrid, Spain.

Miguel Martín (M)

Department of Medical Oncology, Instituto de Investigación Sanitaria Gregorio Marañón, Universidad Complutense, Centro de Investigación Biomédica en Red de Oncología, CIBERONC-ISCIII, C/Dr. Esquerdo 46, 28009, Madrid, Spain. mmartin@geicam.org.

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Classifications MeSH