Dupilumab progressively improves systemic and cutaneous abnormalities in patients with atopic dermatitis.


Journal

The Journal of allergy and clinical immunology
ISSN: 1097-6825
Titre abrégé: J Allergy Clin Immunol
Pays: United States
ID NLM: 1275002

Informations de publication

Date de publication:
01 2019
Historique:
received: 22 12 2017
revised: 19 07 2018
accepted: 14 08 2018
pubmed: 9 9 2018
medline: 13 11 2019
entrez: 9 9 2018
Statut: ppublish

Résumé

Dupilumab is an IL-4 receptor α mAb inhibiting signaling of IL-4 and IL-13, key drivers of type 2-driven inflammation, as demonstrated by its efficacy in patients with atopic/allergic diseases. This placebo-controlled, double-blind trial (NCT01979016) evaluated the efficacy, safety, and effects of dupilumab on molecular/cellular lesional and nonlesional skin phenotypes and systemic type 2 biomarkers of patients with moderate-to-severe atopic dermatitis (AD). Skin biopsy specimens and blood were evaluated from 54 patients randomized 1:1 to weekly subcutaneous doses of 200 mg of dupilumab or placebo for 16 weeks. Dupilumab (vs placebo) significantly improved clinical signs and symptoms of AD, was well tolerated, and progressively shifted the lesional transcriptome toward a nonlesional phenotype (weeks 4-16). Mean improvements in a meta-analysis-derived AD transcriptome (genes differentially expressed between lesional and nonlesional skin) were 68.8% and 110.8% with dupilumab and -10.5% and 55.0% with placebo (weeks 4 and 16, respectively; P < .001). Dupilumab significantly reduced expression of genes involved in type 2 inflammation (IL13, IL31, CCL17, CCL18, and CCL26), epidermal hyperplasia (keratin 16 [K16] and MKi67), T cells, dendritic cells (ICOS, CD11c, and CTLA4), and T Dupilumab-mediated inhibition of IL-4/IL-13 signaling through IL-4 receptor α blockade significantly and progressively improved disease activity, suppressed cellular/molecular cutaneous markers of inflammation and systemic measures of type 2 inflammation, and reversed AD-associated epidermal abnormalities.

Sections du résumé

BACKGROUND
Dupilumab is an IL-4 receptor α mAb inhibiting signaling of IL-4 and IL-13, key drivers of type 2-driven inflammation, as demonstrated by its efficacy in patients with atopic/allergic diseases.
OBJECTIVE
This placebo-controlled, double-blind trial (NCT01979016) evaluated the efficacy, safety, and effects of dupilumab on molecular/cellular lesional and nonlesional skin phenotypes and systemic type 2 biomarkers of patients with moderate-to-severe atopic dermatitis (AD).
METHODS
Skin biopsy specimens and blood were evaluated from 54 patients randomized 1:1 to weekly subcutaneous doses of 200 mg of dupilumab or placebo for 16 weeks.
RESULTS
Dupilumab (vs placebo) significantly improved clinical signs and symptoms of AD, was well tolerated, and progressively shifted the lesional transcriptome toward a nonlesional phenotype (weeks 4-16). Mean improvements in a meta-analysis-derived AD transcriptome (genes differentially expressed between lesional and nonlesional skin) were 68.8% and 110.8% with dupilumab and -10.5% and 55.0% with placebo (weeks 4 and 16, respectively; P < .001). Dupilumab significantly reduced expression of genes involved in type 2 inflammation (IL13, IL31, CCL17, CCL18, and CCL26), epidermal hyperplasia (keratin 16 [K16] and MKi67), T cells, dendritic cells (ICOS, CD11c, and CTLA4), and T
CONCLUSION
Dupilumab-mediated inhibition of IL-4/IL-13 signaling through IL-4 receptor α blockade significantly and progressively improved disease activity, suppressed cellular/molecular cutaneous markers of inflammation and systemic measures of type 2 inflammation, and reversed AD-associated epidermal abnormalities.

Identifiants

pubmed: 30194992
pii: S0091-6749(18)31266-1
doi: 10.1016/j.jaci.2018.08.022
pii:
doi:

Substances chimiques

Antibodies, Monoclonal 0
Antibodies, Monoclonal, Humanized 0
FLG protein, human 0
Filaggrin Proteins 0
dupilumab 420K487FSG

Banques de données

ClinicalTrials.gov
['NCT01979016']

Types de publication

Clinical Trial, Phase II Journal Article Multicenter Study Randomized Controlled Trial Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

155-172

Informations de copyright

Copyright © 2018 The Authors. Published by Elsevier Inc. All rights reserved.

Auteurs

Emma Guttman-Yassky (E)

Department of Dermatology, Icahn School of Medicine at Mount Sinai, New York, NY; Laboratory for Investigative Dermatology, Rockefeller University, New York, NY. Electronic address: Emma.Guttman@mountsinai.org.

Robert Bissonnette (R)

Innovaderm Research, Montreal, Quebec, Canada.

Benjamin Ungar (B)

Department of Dermatology, Icahn School of Medicine at Mount Sinai, New York, NY; Laboratory for Investigative Dermatology, Rockefeller University, New York, NY.

Mayte Suárez-Fariñas (M)

Department of Dermatology, Icahn School of Medicine at Mount Sinai, New York, NY; Laboratory for Investigative Dermatology, Rockefeller University, New York, NY; Department of Population Health Science and Policy, Icahn School of Medicine at Mount Sinai, New York, NY.

Marius Ardeleanu (M)

Regeneron Pharmaceuticals, Tarrytown, NY.

Hitokazu Esaki (H)

Department of Dermatology, Graduate School of Medical Sciences, Kyushu University, Fukuoka, Japan.

Maria Suprun (M)

Department of Population Health Science and Policy, Icahn School of Medicine at Mount Sinai, New York, NY.

Yeriel Estrada (Y)

Department of Dermatology, Icahn School of Medicine at Mount Sinai, New York, NY.

Hui Xu (H)

Department of Dermatology, Icahn School of Medicine at Mount Sinai, New York, NY.

Xiangyu Peng (X)

Department of Dermatology, Icahn School of Medicine at Mount Sinai, New York, NY.

Jonathan I Silverberg (JI)

Department of Dermatology, Preventive Medicine and Medical Social Sciences, Northwestern University Feinberg School of Medicine, Chicago, Ill.

Alan Menter (A)

Department of Dermatology, Baylor University Medical Center, Dallas, Tex.

James G Krueger (JG)

Laboratory for Investigative Dermatology, Rockefeller University, New York, NY.

Rick Zhang (R)

Regeneron Pharmaceuticals, Tarrytown, NY.

Usman Chaudhry (U)

Regeneron Pharmaceuticals, Tarrytown, NY.

Brian Swanson (B)

Sanofi, Bridgewater, NJ.

Neil M H Graham (NMH)

Regeneron Pharmaceuticals, Tarrytown, NY.

Gianluca Pirozzi (G)

Sanofi, Bridgewater, NJ.

George D Yancopoulos (GD)

Regeneron Pharmaceuticals, Tarrytown, NY.

Jennifer D D Hamilton (JD)

Regeneron Pharmaceuticals, Tarrytown, NY.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH