Newborn Screening for Severe Combined Immunodeficiency in the United States: Lessons Learned.


Journal

Immunology and allergy clinics of North America
ISSN: 1557-8607
Titre abrégé: Immunol Allergy Clin North Am
Pays: United States
ID NLM: 8805635

Informations de publication

Date de publication:
02 2019
Historique:
entrez: 24 11 2018
pubmed: 24 11 2018
medline: 18 12 2019
Statut: ppublish

Résumé

In the United States, significant improvement in diagnosis and outcomes for children affected with severe combined immunodeficiency has followed institution of newborn screening using an assay to measure T-cell receptor excision circles in newborn dried blood spot specimens. Key to this outcome is the avoidance of infectious complications in infants with severe combined immunodeficiency.

Identifiants

pubmed: 30466767
pii: S0889-8561(18)30072-9
doi: 10.1016/j.iac.2018.08.002
pii:
doi:

Substances chimiques

Receptors, Antigen, T-Cell 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

1-11

Subventions

Organisme : NIGMS NIH HHS
ID : R01 GM107132
Pays : United States
Organisme : NIAID NIH HHS
ID : R01 AI105776
Pays : United States
Organisme : NIAID NIH HHS
ID : U54 AI082973
Pays : United States

Informations de copyright

Copyright © 2018 Elsevier Inc. All rights reserved.

Auteurs

Morna J Dorsey (MJ)

Department of Pediatrics, University of California San Francisco, 555 Mission Bay Boulevard South, San Francisco, CA 94158, USA. Electronic address: Morna.Dorsey@ucsf.edu.

Jennifer M Puck (JM)

Department of Pediatrics, University of California San Francisco, Box 3118, 555 Mission Bay Boulevard South, Rm SC-252K, San Francisco, CA 94143, USA.

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Classifications MeSH