Impact of Genetic Variation on Pravastatin Systemic Exposure in Pediatric Hypercholesterolemia.


Journal

Clinical pharmacology and therapeutics
ISSN: 1532-6535
Titre abrégé: Clin Pharmacol Ther
Pays: United States
ID NLM: 0372741

Informations de publication

Date de publication:
06 2019
Historique:
received: 02 08 2018
accepted: 20 11 2018
pubmed: 15 12 2018
medline: 5 3 2020
entrez: 15 12 2018
Statut: ppublish

Résumé

This study investigated the impact of SLCO1B1 genotype on pravastatin systemic exposure in children and adolescents with hypercholesterolemia. Participants (8-20 years) with at least one allelic variant of SLCO1B1 c.521T>C (521TC, n = 15; 521CC, n = 2) and wild-type controls (521TT, n = 15) completed a single oral dose pharmacokinetic study. Interindividual variability of pravastatin acid (PVA) exposure within SLCO1B1 genotype groups exceeded the approximately twofold difference in mean PVA exposure observed between SLCO1B1 genotype groups (P > 0.05, q > 0.10). The 3'α-iso-pravastatin acid and lactone isomer formation in the acidic environment of the stomach prior to absorption also was variable and affected PVA exposure in all genotype groups. The SLCO1B1 c.521 gene variant contributing to variability in systemic exposure to PVA in our pediatric cohort was comparable to previous studies in adults. However, other demographic and physicochemical factors seem to also contribute to interindividual variability in the dose-exposure relationship.

Identifiants

pubmed: 30549267
doi: 10.1002/cpt.1330
doi:

Substances chimiques

Hydroxymethylglutaryl-CoA Reductase Inhibitors 0
Liver-Specific Organic Anion Transporter 1 0
SLCO1B1 protein, human 0
Pravastatin KXO2KT9N0G

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1501-1512

Informations de copyright

© 2019 The Authors Clinical Pharmacology & Therapeutics © 2019 American Society for Clinical Pharmacology and Therapeutics.

Auteurs

Jonathan B Wagner (JB)

Ward Family Heart Center, Children's Mercy, Kansas City, Missouri, USA.
Division of Clinical Pharmacology, Medical Toxicology and Therapeutic Innovation, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

Susan Abdel-Rahman (S)

Division of Clinical Pharmacology, Medical Toxicology and Therapeutic Innovation, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

Roger Gaedigk (R)

Division of Clinical Pharmacology, Medical Toxicology and Therapeutic Innovation, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

Andrea Gaedigk (A)

Division of Clinical Pharmacology, Medical Toxicology and Therapeutic Innovation, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

Geetha Raghuveer (G)

Ward Family Heart Center, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

Vincent S Staggs (VS)

Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.
Health Services & Outcomes Research, Children's Mercy, Kansas City, Missouri, USA.

Ralph Kauffman (R)

Division of Clinical Pharmacology, Medical Toxicology and Therapeutic Innovation, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

Leon Van Haandel (L)

Division of Clinical Pharmacology, Medical Toxicology and Therapeutic Innovation, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

J Steven Leeder (JS)

Division of Clinical Pharmacology, Medical Toxicology and Therapeutic Innovation, Children's Mercy, Kansas City, Missouri, USA.
Department of Pediatrics, University of Missouri-Kansas City School of Medicine, Kansas City, Missouri, USA.

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Classifications MeSH