Development of a Novel Anti-CD19 Chimeric Antigen Receptor: A Paradigm for an Affordable CAR T Cell Production at Academic Institutions.

4-1BB CD19 T cell chimeric antigen receptor immunotherapy leukemia lymphoma preclinical studies

Journal

Molecular therapy. Methods & clinical development
ISSN: 2329-0501
Titre abrégé: Mol Ther Methods Clin Dev
Pays: United States
ID NLM: 101624857

Informations de publication

Date de publication:
15 Mar 2019
Historique:
received: 31 08 2018
accepted: 29 11 2018
entrez: 10 1 2019
pubmed: 10 1 2019
medline: 10 1 2019
Statut: epublish

Résumé

Genetically modifying autologous T cells to express an anti-CD19 chimeric antigen receptor (CAR) has shown impressive response rates for the treatment of CD19+ B cell malignancies in several clinical trials (CTs). Making this treatment available to our patients prompted us to develop a novel CART19 based on our own anti-CD19 antibody (A3B1), followed by CD8 hinge and transmembrane region, 4-1BB- and CD3z-signaling domains. We show that A3B1 CAR T cells are highly cytotoxic and specific against CD19+ cells

Identifiants

pubmed: 30623002
doi: 10.1016/j.omtm.2018.11.010
pii: S2329-0501(18)30122-0
pmc: PMC6319086
doi:

Types de publication

Journal Article

Langues

eng

Pagination

134-144

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Auteurs

Maria Castella (M)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.

Anna Boronat (A)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.

Raquel Martín-Ibáñez (R)

Stem Cells and Regenerative Medicine Laboratory, Production and Validation Center of Advanced Therapies (Creatio), Department of Biomedical Sciences, University of Barcelona, Casanova 143, 08036 Barcelona, Spain.

Vanina Rodríguez (V)

Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Physiopathology and Molecular Bases in Hematology Group, IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.

Guillermo Suñé (G)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.

Miguel Caballero (M)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut de Recerca Pediàtrica Hospital Sant Joan de Déu, Universidad de Barcelona, Passeig de Sant Joan de Déu, 2, 08950 Esplugues de Llobregat, Barcelona, Spain.

Berta Marzal (B)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.

Lorena Pérez-Amill (L)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.

Beatriz Martín-Antonio (B)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.

Julio Castaño (J)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Casanova 143, 08036 Barcelona, Spain.

Clara Bueno (C)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Casanova 143, 08036 Barcelona, Spain.

Olga Balagué (O)

Department of Pathology, Hospital Clínic, IDIBAPS, Villarroel 170, 08036 Barcelona, Spain.

Europa Azucena González-Navarro (EA)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.

Carles Serra-Pages (C)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Universitat de Barcelona, Casanova 143, 08036 Barcelona, Spain.

Pablo Engel (P)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Immunology Unit, Department of Biomedical Sciences, University of Barcelona, Casanova 143, 08036 Barcelona, Spain.

Ramon Vilella (R)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.

Daniel Benitez-Ribas (D)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.

Valentín Ortiz-Maldonado (V)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.

Joan Cid (J)

Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Department of Hemotherapy and Hemostasis, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.

Jaime Tabera (J)

Unit of Advanced Therapies, Hospital Clinic de Barcelona, Blood and Tissue Bank -BST-, Passeig del Taulat, 106, 08005 Barcelona, Spain.

Josep M Canals (JM)

Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Stem Cells and Regenerative Medicine Laboratory, Production and Validation Center of Advanced Therapies (Creatio), Department of Biomedical Sciences, University of Barcelona, Casanova 143, 08036 Barcelona, Spain.
Universitat de Barcelona, Casanova 143, 08036 Barcelona, Spain.

Miquel Lozano (M)

Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Department of Hemotherapy and Hemostasis, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.

Tycho Baumann (T)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.

Anna Vilarrodona (A)

Unit of Advanced Therapies, Hospital Clinic de Barcelona, Blood and Tissue Bank -BST-, Passeig del Taulat, 106, 08005 Barcelona, Spain.

Esteve Trias (E)

Unit of Advanced Therapies, Hospital Clinic de Barcelona, Blood and Tissue Bank -BST-, Passeig del Taulat, 106, 08005 Barcelona, Spain.

Elías Campo (E)

Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Physiopathology and Molecular Bases in Hematology Group, IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Department of Pathology, Hospital Clínic, IDIBAPS, Villarroel 170, 08036 Barcelona, Spain.
Universitat de Barcelona, Casanova 143, 08036 Barcelona, Spain.
Centro de Investigación Biomedica en Red de Cancer (ISCIII-CIBERONC), Barcelona, Spain.

Pablo Menendez (P)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Casanova 143, 08036 Barcelona, Spain.
Centro de Investigación Biomedica en Red de Cancer (ISCIII-CIBERONC), Barcelona, Spain.
Institució Catalana de Recerca i Estudis Avancats (ICREA), Barcelona, Spain.

Álvaro Urbano-Ispizua (Á)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Casanova 143, 08036 Barcelona, Spain.
Universitat de Barcelona, Casanova 143, 08036 Barcelona, Spain.

Jordi Yagüe (J)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Universitat de Barcelona, Casanova 143, 08036 Barcelona, Spain.

Patricia Pérez-Galán (P)

Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Physiopathology and Molecular Bases in Hematology Group, IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Centro de Investigación Biomedica en Red de Cancer (ISCIII-CIBERONC), Barcelona, Spain.

Susana Rives (S)

Institut de Recerca Pediàtrica Hospital Sant Joan de Déu, Universidad de Barcelona, Passeig de Sant Joan de Déu, 2, 08950 Esplugues de Llobregat, Barcelona, Spain.

Julio Delgado (J)

Department of Hematology, ICMHO, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Universitat de Barcelona, Casanova 143, 08036 Barcelona, Spain.
Centro de Investigación Biomedica en Red de Cancer (ISCIII-CIBERONC), Barcelona, Spain.

Manel Juan (M)

Department of Immunology, CDB, Hospital Clínic de Barcelona, Villarroel 170, 08036 Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer - IDIBAPS, Rosselló 153, 08036 Barcelona, Spain.
Institut de Recerca Pediàtrica Hospital Sant Joan de Déu, Universidad de Barcelona, Passeig de Sant Joan de Déu, 2, 08950 Esplugues de Llobregat, Barcelona, Spain.
Universitat de Barcelona, Casanova 143, 08036 Barcelona, Spain.

Classifications MeSH