Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia.
Journal
Nature medicine
ISSN: 1546-170X
Titre abrégé: Nat Med
Pays: United States
ID NLM: 9502015
Informations de publication
Date de publication:
02 2019
02 2019
Historique:
received:
25
07
2018
accepted:
13
11
2018
pubmed:
22
1
2019
medline:
11
5
2019
entrez:
22
1
2019
Statut:
ppublish
Résumé
ß-thalassemia is caused by ß-globin gene mutations resulting in reduced (β
Identifiants
pubmed: 30664781
doi: 10.1038/s41591-018-0301-6
pii: 10.1038/s41591-018-0301-6
doi:
Types de publication
Clinical Trial, Phase I
Clinical Trial, Phase II
Journal Article
Research Support, Non-U.S. Gov't
Langues
eng
Sous-ensembles de citation
IM