L-Cysteine supplementation prevents liver transplantation in a patient with TRMU deficiency.

TRMU cysteine hepatopathy liver transplant mitochondrial

Journal

Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422

Informations de publication

Date de publication:
Jun 2019
Historique:
received: 27 11 2018
revised: 22 01 2019
accepted: 23 01 2019
entrez: 12 2 2019
pubmed: 12 2 2019
medline: 12 2 2019
Statut: epublish

Résumé

Early recognition of rare mitochondrial respiratory chain defects has become readily available with the routine use of whole exome sequencing. Patients with oxidative phosphorylation defects present with a heterogenous phenotype, often rapidly progressive, and lethal. Clinicians aim for prompt identification of the specific molecular defect to provide timely management, decrease morbidity, and potentially improve survival rates. More recently, bi-allelic pathogenic variants in the

Identifiants

pubmed: 30740308
doi: 10.1016/j.ymgmr.2019.100453
pii: S2214-4269(18)30133-2
pii: 100453
pmc: PMC6355510
doi:

Types de publication

Case Reports

Langues

eng

Pagination

100453

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Auteurs

Claudia Soler-Alfonso (C)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, United States.
Texas Children's Hospital, Houston, TX, United States.

Nishita Pillai (N)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, United States.
Texas Children's Hospital, Houston, TX, United States.

Erin Cooney (E)

University of Texas Medical Branch, Galveston, TX, United States.

Krupa R Mysore (KR)

Department of Pediatric Gastroenterology, Baylor College of Medicine, Houston, TX, United States.

Suzanne Boyer (S)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, United States.
Texas Children's Hospital, Houston, TX, United States.

Fernando Scaglia (F)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, United States.
Texas Children's Hospital, Houston, TX, United States.
Joint BCM-CUHK Center of Medical Genetics, Prince of Wales Hospital, Hong Kong SAR.

Classifications MeSH