Dupilumab provides important clinical benefits to patients with atopic dermatitis who do not achieve clear or almost clear skin according to the Investigator's Global Assessment: a pooled analysis of data from two phase III trials.


Journal

The British journal of dermatology
ISSN: 1365-2133
Titre abrégé: Br J Dermatol
Pays: England
ID NLM: 0004041

Informations de publication

Date de publication:
07 2019
Historique:
accepted: 18 02 2019
pubmed: 23 2 2019
medline: 29 8 2020
entrez: 22 2 2019
Statut: ppublish

Résumé

In the U.S.A., an Investigator's Global Assessment (IGA) score of ≤ 1 (clear or almost clear skin) has been the standard measure in regulatory outcomes for registration clinical trials in atopic dermatitis (AD), including those supporting the recent approval of dupilumab. To evaluate the treatment effect of dupilumab in patients with IGA > 1 at the end of treatment, using other validated outcome measures for AD signs, symptoms and quality of life. LIBERTY AD SOLO 1 and 2 were two 16-week, randomized, double-blind trials enrolling adult patients with moderate-to-severe AD (IGA ≥ 3) inadequately controlled with topical treatment. We performed a post hoc analysis in patients receiving dupilumab 300 mg every 2 weeks (q2w) or placebo. Outcome measures in patients with IGA > 1 included Eczema Area and Severity Index (EASI), pruritus numerical rating scale (NRS), affected body surface area (BSA), Patient-Oriented Eczema Measure (POEM) and Dermatology Life Quality Index (DLQI). The trials were registered at ClinicalTrials.gov: NCT02277743 and NCT02277769. At week 16, 278 of 449 dupilumab q2w-treated patients (median age 36·0 years) and 396 of 443 placebo-treated patients had IGA > 1. Among patients with IGA > 1 at week 16, dupilumab significantly improved several outcome measures compared with placebo: EASI (-48·9% vs. -11·3%, P < 0·001), pruritus NRS (-35·2% vs. -9·1%, P < 0·001), affected BSA (-23·1% vs. -4·5%, P < 0·001), POEM score ≥ 4-point improvement (57·4% vs. 21·0%, P < 0·001) and DLQI score ≥ 4-point improvement (59·3% vs. 24·4%, P < 0·001). In patients with IGA > 1 at week 16, dupilumab induced statistically significant benefits in multiple validated outcome measures compared with placebo. The IGA ≤ 1 end point significantly underestimates clinically relevant dupilumab treatment effects.

Sections du résumé

BACKGROUND
In the U.S.A., an Investigator's Global Assessment (IGA) score of ≤ 1 (clear or almost clear skin) has been the standard measure in regulatory outcomes for registration clinical trials in atopic dermatitis (AD), including those supporting the recent approval of dupilumab.
OBJECTIVES
To evaluate the treatment effect of dupilumab in patients with IGA > 1 at the end of treatment, using other validated outcome measures for AD signs, symptoms and quality of life.
METHODS
LIBERTY AD SOLO 1 and 2 were two 16-week, randomized, double-blind trials enrolling adult patients with moderate-to-severe AD (IGA ≥ 3) inadequately controlled with topical treatment. We performed a post hoc analysis in patients receiving dupilumab 300 mg every 2 weeks (q2w) or placebo. Outcome measures in patients with IGA > 1 included Eczema Area and Severity Index (EASI), pruritus numerical rating scale (NRS), affected body surface area (BSA), Patient-Oriented Eczema Measure (POEM) and Dermatology Life Quality Index (DLQI). The trials were registered at ClinicalTrials.gov: NCT02277743 and NCT02277769.
RESULTS
At week 16, 278 of 449 dupilumab q2w-treated patients (median age 36·0 years) and 396 of 443 placebo-treated patients had IGA > 1. Among patients with IGA > 1 at week 16, dupilumab significantly improved several outcome measures compared with placebo: EASI (-48·9% vs. -11·3%, P < 0·001), pruritus NRS (-35·2% vs. -9·1%, P < 0·001), affected BSA (-23·1% vs. -4·5%, P < 0·001), POEM score ≥ 4-point improvement (57·4% vs. 21·0%, P < 0·001) and DLQI score ≥ 4-point improvement (59·3% vs. 24·4%, P < 0·001).
CONCLUSIONS
In patients with IGA > 1 at week 16, dupilumab induced statistically significant benefits in multiple validated outcome measures compared with placebo. The IGA ≤ 1 end point significantly underestimates clinically relevant dupilumab treatment effects.

Identifiants

pubmed: 30791102
doi: 10.1111/bjd.17791
pmc: PMC6849829
doi:

Substances chimiques

Antibodies, Monoclonal, Humanized 0
Placebos 0
dupilumab 420K487FSG

Banques de données

ClinicalTrials.gov
['NCT02277743', 'NCT02277769']

Types de publication

Clinical Trial, Phase III Journal Article Randomized Controlled Trial

Langues

eng

Sous-ensembles de citation

IM

Pagination

80-87

Commentaires et corrections

Type : CommentIn

Informations de copyright

© 2019 The Authors. British Journal of Dermatology published by John Wiley & Sons Ltd on behalf of British Association of Dermatologists.

Références

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pubmed: 26685719
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Auteurs

J I Silverberg (JI)

Department of Dermatology, Preventive Medicine and Medical Social Sciences, Northwestern University Feinberg School of Medicine, NMH/Arkes Family Pavilion Suite, 1600, 676 N. Saint Clair, Chicago, IL, 60611, U.S.A.

E L Simpson (EL)

Department of Dermatology, Oregon Health & Science University, Portland, OR, U.S.A.

M Ardeleanu (M)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY, U.S.A.

D Thaçi (D)

University of Lübeck, Lübeck, Germany.

S Barbarot (S)

Service de Dermatologie, Centre Hospitalier Universitaire (CHU) de Nantes, Nantes, France.

J Bagel (J)

Eczema Treatment Center of Central New Jersey, East Windsor, NJ, U.S.A.

Z Chen (Z)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY, U.S.A.

L Eckert (L)

Sanofi, Chilly-Mazarin, France.

J Chao (J)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY, U.S.A.

A Korotzer (A)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY, U.S.A.

E Rizova (E)

Sanofi Genzyme, Cambridge, MA, U.S.A.

A B Rossi (AB)

Sanofi Genzyme, Cambridge, MA, U.S.A.

Y Lu (Y)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY, U.S.A.

N M H Graham (NMH)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY, U.S.A.

T Hultsch (T)

Sanofi Genzyme, Cambridge, MA, U.S.A.

G Pirozzi (G)

Sanofi, Bridgewater, NJ, U.S.A.

B Akinlade (B)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY, U.S.A.

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Classifications MeSH