Primary familial brain calcification caused by a novel homozygous MYORG mutation in a consanguineous Italian family.
Homozygous
MYORG
Primary familial brain calcification
Recessive
Journal
Neurogenetics
ISSN: 1364-6753
Titre abrégé: Neurogenetics
Pays: United States
ID NLM: 9709714
Informations de publication
Date de publication:
05 2019
05 2019
Historique:
received:
22
01
2019
accepted:
03
03
2019
pubmed:
22
3
2019
medline:
7
1
2020
entrez:
22
3
2019
Statut:
ppublish
Résumé
Primary familial brain calcification (PFBC) is a rare disorder mostly characterized by calcium deposits in the basal ganglia and a wide spectrum of neurologic and psychiatric symptoms, typically inherited as an autosomal dominant trait. Recently, MYORG was reported as the first autosomal recessive causal gene in PFBC patients of Chinese and Middle Eastern origin. Herein, we describe the first PFBC patient of European descent found to carry a novel homozygous MYORG mutation (p.N511Tfs*243). Interestingly, the patient's father, a heterozygous carrier of the same mutation, showed diffuse bilateral cerebral calcifications with no symptoms other than very mild postural tremor.
Identifiants
pubmed: 30895394
doi: 10.1007/s10048-019-00571-8
pii: 10.1007/s10048-019-00571-8
doi:
Substances chimiques
Glycoside Hydrolases
EC 3.2.1.-
MYORG protein, human
EC 3.2.1.-
Types de publication
Case Reports
Journal Article
Research Support, N.I.H., Extramural
Research Support, Non-U.S. Gov't
Langues
eng
Sous-ensembles de citation
IM
Pagination
99-102Subventions
Organisme : NINDS Informatics Center for Neurogenetics and Neurogenomics
ID : P30 NS062691
Pays : International
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