Antisense oligonucleotides for the treatment of cardiomyopathy in Duchenne muscular dystrophy.
Duchenne muscular dystrophy
antisense therapy
cardiomyopathy
drug delivery
dystrophin
morpholinos
Journal
American journal of translational research
ISSN: 1943-8141
Titre abrégé: Am J Transl Res
Pays: United States
ID NLM: 101493030
Informations de publication
Date de publication:
2019
2019
Historique:
received:
19
09
2018
accepted:
02
01
2019
entrez:
12
4
2019
pubmed:
12
4
2019
medline:
12
4
2019
Statut:
epublish
Résumé
Duchenne muscular dystrophy (DMD) is an X-linked recessive fatal neuromuscular disorder characterized by progressive muscle degeneration which affects one in 3500-5000 males born worldwide. DMD is caused by loss-of-function mutations in the
Types de publication
Journal Article
Review
Langues
eng
Pagination
1202-1218Déclaration de conflit d'intérêts
None.
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