In vivo selective inhibition of TRPC6 by antagonist BI 749327 ameliorates fibrosis and dysfunction in cardiac and renal disease.


Journal

Proceedings of the National Academy of Sciences of the United States of America
ISSN: 1091-6490
Titre abrégé: Proc Natl Acad Sci U S A
Pays: United States
ID NLM: 7505876

Informations de publication

Date de publication:
14 05 2019
Historique:
pubmed: 28 4 2019
medline: 31 3 2020
entrez: 28 4 2019
Statut: ppublish

Résumé

Transient receptor potential canonical type 6 (TRPC6) is a nonselective receptor-operated cation channel that regulates reactive fibrosis and growth signaling. Increased TRPC6 activity from enhanced gene expression or gain-of-function mutations contribute to cardiac and/or renal disease. Despite evidence supporting a pathophysiological role, no orally bioavailable selective TRPC6 inhibitor has yet been developed and tested in vivo in disease models. Here, we report an orally bioavailable TRPC6 antagonist (BI 749327; IC

Identifiants

pubmed: 31028142
pii: 1815354116
doi: 10.1073/pnas.1815354116
pmc: PMC6525474
doi:

Substances chimiques

TRPC6 Cation Channel 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

10156-10161

Subventions

Organisme : NHLBI NIH HHS
ID : R35 HL135827
Pays : United States
Organisme : NHLBI NIH HHS
ID : T32 HL007227
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL119012
Pays : United States

Déclaration de conflit d'intérêts

Conflict of interest statement: D.M., J.F.D., L.P., D.W., G.R., S.M.W., S.Z., H.S.Q, J.J.K, A.S., and S.S.P. are full-time employees of Boehringer Ingelheim Pharmaceuticals, Inc. M.M, M.R.N, A.B., and C.S. were full-time employees of Boehringer Ingelheim Pharmaceuticals, Inc. A.B. and M.R.N. are listed as coinventors on a US provisional patent application filed by Boehringer Ingelheim Pharmaceuticals, Inc. relevant to this work. J.F.D., N.Z., D.d.C., X.Z., N.T.B., J.A.C., D.P.H., and M.M.M. were employees of Hydra Biosciences, and received options. This work was supported in part by Boehringer Ingelheim Pharmaceuticals, Inc.

Références

Circ Res. 2001 Feb 16;88(3):325-32
pubmed: 11179201
Proc Natl Acad Sci U S A. 2002 May 28;99(11):7461-6
pubmed: 12032305
J Biol Chem. 2005 Mar 25;280(12):10997-1006
pubmed: 15647288
Nat Med. 2005 Feb;11(2):214-22
pubmed: 15665834
Science. 2005 Jun 17;308(5729):1801-4
pubmed: 15879175
Nat Genet. 2005 Jul;37(7):739-44
pubmed: 15924139
Mol Cell Biol. 2005 Aug;25(16):6980-9
pubmed: 16055711
Proc Natl Acad Sci U S A. 2006 Oct 31;103(44):16586-91
pubmed: 17056714
EMBO J. 2006 Nov 15;25(22):5305-16
pubmed: 17082763
J Clin Invest. 2006 Dec;116(12):3114-26
pubmed: 17099778
Proc Natl Acad Sci U S A. 2006 Dec 12;103(50):19093-8
pubmed: 17142322
PLoS One. 2009 Nov 10;4(11):e7771
pubmed: 19936226
J Mol Cell Cardiol. 2010 Apr;48(4):713-24
pubmed: 19961855
Proc Natl Acad Sci U S A. 2010 Apr 13;107(15):7000-5
pubmed: 20351294
PLoS One. 2010 Sep 20;5(9):e12859
pubmed: 20877463
J Am Soc Nephrol. 2011 Mar;22(3):526-35
pubmed: 21258036
Respir Res. 2011 Feb 04;12:20
pubmed: 21294865
Clin J Am Soc Nephrol. 2011 Jul;6(7):1626-34
pubmed: 21734084
Biochem J. 1990 Oct 15;271(2):515-22
pubmed: 2173565
Cell Calcium. 2012 Feb;51(2):194-206
pubmed: 22280812
Nat Commun. 2012 Jan 31;3:649
pubmed: 22337127
PLoS One. 2012;7(4):e35393
pubmed: 22530015
Dev Cell. 2012 Oct 16;23(4):705-15
pubmed: 23022034
Nat Commun. 2012;3:1238
pubmed: 23212367
Nephrol Dial Transplant. 2013 Jul;28(7):1830-8
pubmed: 23291369
J Clin Invest. 2013 Dec;123(12):5298-309
pubmed: 24231357
Circ Res. 2014 Feb 28;114(5):823-32
pubmed: 24449818
Proc Natl Acad Sci U S A. 2014 Jan 28;111(4):1551-6
pubmed: 24453217
Handb Exp Pharmacol. 2014;222:157-88
pubmed: 24756706
Circ Res. 2014 Aug 29;115(6):567-580
pubmed: 25047165
Physiology (Bethesda). 2014 Sep;29(5):343-60
pubmed: 25180264
J Clin Invest. 2015 May;125(5):1913-26
pubmed: 25844902
Br J Pharmacol. 2015 Jul;172(14):3650-60
pubmed: 25847402
Mol Pharmacol. 2016 Jan;89(1):197-213
pubmed: 26500253
Biochim Biophys Acta Mol Basis Dis. 2017 Feb;1863(2):560-568
pubmed: 27932059
Kidney Int. 2017 Apr;91(4):830-841
pubmed: 27979597
Proc Natl Acad Sci U S A. 2017 Dec 12;114(50):E10763-E10771
pubmed: 29187535
ChemMedChem. 2018 May 23;13(10):1028-1035
pubmed: 29522264
Cell Res. 2018 Jul;28(7):746-755
pubmed: 29700422
Bioorg Med Chem Lett. 2018 Jul 1;28(12):2222-2227
pubmed: 29752182
Cancer Lett. 2018 Sep 28;432:47-55
pubmed: 29859875

Auteurs

Brian Leei Lin (BL)

Division of Cardiology, Johns Hopkins Medical Institutions, Baltimore, MD 21205.

Damian Matera (D)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Julia F Doerner (JF)

Hydra Biosciences, Cambridge, MA 02138.

Nan Zheng (N)

Hydra Biosciences, Cambridge, MA 02138.

Donato Del Camino (D)

Hydra Biosciences, Cambridge, MA 02138.

Sumita Mishra (S)

Division of Cardiology, Johns Hopkins Medical Institutions, Baltimore, MD 21205.

Hong Bian (H)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Svetlana Zeveleva (S)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Xiaoguang Zhen (X)

Hydra Biosciences, Cambridge, MA 02138.

Nathaniel T Blair (NT)

Hydra Biosciences, Cambridge, MA 02138.

Jayhong A Chong (JA)

Hydra Biosciences, Cambridge, MA 02138.

David P Hessler (DP)

Hydra Biosciences, Cambridge, MA 02138.

Djahida Bedja (D)

Division of Cardiology, Johns Hopkins Medical Institutions, Baltimore, MD 21205.

Guangshuo Zhu (G)

Division of Cardiology, Johns Hopkins Medical Institutions, Baltimore, MD 21205.

Grace K Muller (GK)

Division of Cardiology, Johns Hopkins Medical Institutions, Baltimore, MD 21205.

Mark J Ranek (MJ)

Division of Cardiology, Johns Hopkins Medical Institutions, Baltimore, MD 21205.

Lynn Pantages (L)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Mary McFarland (M)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Matthew R Netherton (MR)

Small Molecule Discovery Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Angela Berry (A)

Small Molecule Discovery Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Diane Wong (D)

Small Molecule Discovery Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Georg Rast (G)

Drug Discovery Sciences, Boehringer Ingelheim GmbH & Co. KG, 88397 Biberach an der Riss, Germany.

Hu Sheng Qian (HS)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Steven M Weldon (SM)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Jay J Kuo (JJ)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Achim Sauer (A)

Drug Discovery Sciences, Boehringer Ingelheim GmbH & Co. KG, 88397 Biberach an der Riss, Germany.

Chris Sarko (C)

Small Molecule Discovery Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877.

Magdalene M Moran (MM)

Hydra Biosciences, Cambridge, MA 02138.

David A Kass (DA)

Division of Cardiology, Johns Hopkins Medical Institutions, Baltimore, MD 21205; dkass@jhmi.edu steven.pullen@boehringer-ingelheim.com.

Steven S Pullen (SS)

Cardiometabolic Diseases Research, Boehringer Ingelheim Pharmaceuticals, Inc., Ridgefield, CT 06877; dkass@jhmi.edu steven.pullen@boehringer-ingelheim.com.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH