Clinical Characteristics, Associated Malignancies and Management of Primary Sclerosing Cholangitis in Inflammatory Bowel Disease Patients: A Multicentre Retrospective Cohort Study.


Journal

Journal of Crohn's & colitis
ISSN: 1876-4479
Titre abrégé: J Crohns Colitis
Pays: England
ID NLM: 101318676

Informations de publication

Date de publication:
10 Dec 2019
Historique:
pubmed: 8 5 2019
medline: 29 5 2020
entrez: 8 5 2019
Statut: ppublish

Résumé

Primary sclerosing cholangitis [PSC] is usually associated with inflammatory bowel disease [IBD]. An increased risk of malignancies, mainly colorectal cancer [CRC] and cholangiocarcinoma [CCA], has been reported in PSC-IBD patients. Our aim was to determine the clinical characteristics and management of PSC in IBD patients, and the factors associated with malignancies. PSC-IBD patients were identified from the Spanish ENEIDA registry of GETECCU. Additional data were collected using the AEG-REDCap electronic data capture tool. In total, 277 PSC-IBD patients were included, with an incidence rate of 61 PSC cases per 100 000 IBD patient-years, 69.7% men, 67.5% ulcerative colitis and mean age at PSC diagnosis of 40 ± 16 years. Most patients [85.2%] were treated with ursodeoxycholic acid. Liver transplantation was required in 35 patients [12.6%] after 79 months (interquartile range [IQR] 50-139). It was more common in intra- and extrahepatic PSC compared with small-duct PSC (16.3% vs 3.3%; odds ratio [OR] 5.7: 95% confidence interval [CI] = 1.7-19.3). The incidence rate of CRC since PSC diagnosis was 3.3 cases per 1000 patient-years [95% CI = 1.9-5.6]. Having symptoms of PSC at PSC diagnosis was the only factor related to an increased risk of CRC after IBD diagnosis [hazard ratio= 3.3: 95% CI = 1.1-9.9]. CCA was detected in seven patients [2.5%] with intra- and extrahepatic PSC, with median age of 42 years [IQR 39-53], and presented a lower life expectancy compared with patients without CCA and patients with or without CRC. PSC-IBD patients with symptoms of PSC at PSC diagnosis have an increased risk of CRC. CCA was only diagnosed in patients with intra- and extrahepatic PSC and was associated with poor survival.

Sections du résumé

BACKGROUND AND AIMS OBJECTIVE
Primary sclerosing cholangitis [PSC] is usually associated with inflammatory bowel disease [IBD]. An increased risk of malignancies, mainly colorectal cancer [CRC] and cholangiocarcinoma [CCA], has been reported in PSC-IBD patients. Our aim was to determine the clinical characteristics and management of PSC in IBD patients, and the factors associated with malignancies.
METHODS METHODS
PSC-IBD patients were identified from the Spanish ENEIDA registry of GETECCU. Additional data were collected using the AEG-REDCap electronic data capture tool.
RESULTS RESULTS
In total, 277 PSC-IBD patients were included, with an incidence rate of 61 PSC cases per 100 000 IBD patient-years, 69.7% men, 67.5% ulcerative colitis and mean age at PSC diagnosis of 40 ± 16 years. Most patients [85.2%] were treated with ursodeoxycholic acid. Liver transplantation was required in 35 patients [12.6%] after 79 months (interquartile range [IQR] 50-139). It was more common in intra- and extrahepatic PSC compared with small-duct PSC (16.3% vs 3.3%; odds ratio [OR] 5.7: 95% confidence interval [CI] = 1.7-19.3). The incidence rate of CRC since PSC diagnosis was 3.3 cases per 1000 patient-years [95% CI = 1.9-5.6]. Having symptoms of PSC at PSC diagnosis was the only factor related to an increased risk of CRC after IBD diagnosis [hazard ratio= 3.3: 95% CI = 1.1-9.9]. CCA was detected in seven patients [2.5%] with intra- and extrahepatic PSC, with median age of 42 years [IQR 39-53], and presented a lower life expectancy compared with patients without CCA and patients with or without CRC.
CONCLUSIONS CONCLUSIONS
PSC-IBD patients with symptoms of PSC at PSC diagnosis have an increased risk of CRC. CCA was only diagnosed in patients with intra- and extrahepatic PSC and was associated with poor survival.

Identifiants

pubmed: 31063540
pii: 5486538
doi: 10.1093/ecco-jcc/jjz094
doi:

Types de publication

Journal Article Multicenter Study Observational Study

Langues

eng

Sous-ensembles de citation

IM

Pagination

1492-1500

Informations de copyright

Copyright © 2019 European Crohn’s and Colitis Organisation (ECCO). Published by Oxford University Press. All rights reserved. For permissions, please email: journals.permissions@oup.com.

Auteurs

Ivan Guerra (I)

Hospital Universitario de Fuenlabrada and Instituto de Investigación del Hospital Universitario La Paz, IdiPaz, Madrid, Spain.

Luis Bujanda (L)

Hospital Donostia/Instituto Biodonostia, Universidad del País Vasco UPV/EHU, Donostia-San Sebastián, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.

Jesús Castro (J)

Hospital Clinic de Barcelona, Barcelona, Spain.

Olga Merino (O)

Hospital Universitario de Cruces, Barakaldo, Vizcaya, Spain.

Joan Tosca (J)

Hospital Universitario Clínico de Valencia, Department of Medicine, University of Valencia, Valencia, Spain.

Blau Camps (B)

Hospital Universitari de Bellvitge, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), l'Hospitalet de Llobregat, Spain.

Ana Gutiérrez (A)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital General Universitario de Alicante, Alicante, Spain.

Jordi Gordillo Ábalos (J)

Hospital de la Santa Creu i Sant Pau, Barcelona, Spain.

Luisa de Castro (L)

Complexo Hospitalario Universitario de Vigo, Instituto de Investigación Biomédica. Estructura Organizativa de Xestión Integrada de Vigo, Vigo, Spain.

Marisa Iborra (M)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital Universitario y Politécnico de La Fe, Valencia, Spain.

Ana Y Carbajo (AY)

Hospital Universitario Rio Hortega, Valladolid.

Carlos Taxonera (C)

Hospital Clínico San Carlos and Instituto de Investigación del Hospital Clínico San Carlos (IdISSC), Madrid, Spain.

Iago Rodríguez-Lago (I)

Hospital de Galdakao, Galdakao, Vizcaya, Spain.

Francisco Mesonero (F)

Hospital Universitario Ramón y Cajal, Madrid, Spain.

Ruth de Francisco (R)

Hospital Universitario Central De Asturias, Instituto de Investigación Sanitaria del Principado de Asturias (ISPA), Oviedo, Spain.

Gonzalo J Gómez-Gómez (GJ)

Hospital 12 de Octubre, Madrid, Spain.

María Chaparro (M)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital Universitario de La Princesa, Instituto de Investigación Sanitaria Princesa (IIS-IP), Universidad Autónoma de Madrid, Madrid, Spain.

Carlos A Tardillo (CA)

Hospital Universitario Nuestra Señora Candelaria, Santa Cruz De Tenerife, Spain.

Montserrat Rivero (M)

Hospital Universitario Marqués de Valdecilla and IDIVAL, Santander, Spain.

Alicia Algaba (A)

Hospital Universitario de Fuenlabrada and Instituto de Investigación del Hospital Universitario La Paz, IdiPaz, Madrid, Spain.

Eduardo Martín Arranz (E)

Hospital Universitario La Paz and Instituto de Investigación del Hospital Universitario La Paz, IdiPaz, Madrid.

Fiorella Cañete (F)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital Universitari Germans Trias i Pujol, Badalona, Spain.

Raquel Vicente (R)

Hospital Universitario Miguel Servet, Zaragoza, Spain.

Beatriz Sicilia (B)

Hospital Universitario de Burgos, Burgos, Spain.

Beatriz Antolín (B)

Hospital Clínico Universitario de Valladolid, Valladolid, Spain.

Vanessa Prieto (V)

Hospital Universitario de Salamanca, Salamanca, Spain.

Lucía Márquez (L)

Parc de Salut Mar, Barcelona, Spain.

José M Benítez (JM)

Hospital Universitario Reina Sofía and Instituto Maimónides de Investigación Biomédica de Córdoba (IMIBIC), Córdoba, Spain.

Patricia Camo (P)

Hospital General San Jorge, Huesca, Spain.

Marta Piqueras (M)

Consorci Sanitari Terrassa, Terrassa, Spain.

Carla J Gargallo (CJ)

Hospital Clínico Universitario "Lozano Blesa" and Aragón Health Research Institute (IIS Aragón), Zaragoza, Spain.

Esther Hinojosa (E)

Hospital de Manises, Valencia, Spain.

José M Huguet (JM)

Hospital General Universitario de Valencia, Valencia, Spain.

José L Pérez Calle (JL)

Hospital Universitario Fundación Alcorcón, Madrid, Spain.

Manuel Van Domselaar (M)

Hospital Universitario de Torrejón and Universidad Francisco de Vitoria, Madrid, Spain.

Cristina Rodriguez (C)

Complejo hospitalario de Navarra, Pamplona, Spain.

Xavier Calvet (X)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Corporació Sanitària Universitària Parc Taulí, Universitat Autònoma de Barcelona, Sabadell, Spain.

Carmen Muñoz-Villafranca (C)

Hospital Universitario de Basurto, Bilbao, Spain.

Mariana F García-Sepulcre (MF)

Hospital General Universitario Elche, Alicante, Spain.

Patricia Munoz-Garrido (P)

Hospital Donostia/Instituto Biodonostia, Universidad del País Vasco UPV/EHU, Donostia-San Sebastián, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.

Agnès Fernández-Clotet (A)

Hospital Clinic de Barcelona, Barcelona, Spain.

Laura Gómez Irwin (L)

Hospital Universitario de Cruces, Barakaldo, Vizcaya, Spain.

Sherly Hernández (S)

Hospital Universitario Clínico de Valencia, Department of Medicine, University of Valencia, Valencia, Spain.

Jordi Guardiola (J)

Hospital Universitari de Bellvitge, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), l'Hospitalet de Llobregat, Spain.
Universitat de Barcelona, Spain.

Laura Sempere (L)

Hospital General Universitario de Alicante, Alicante, Spain.

Carlos González Muñoza (C)

Hospital de la Santa Creu i Sant Pau, Barcelona, Spain.

Vicent Hernández (V)

Complexo Hospitalario Universitario de Vigo, Instituto de Investigación Biomédica. Estructura Organizativa de Xestión Integrada de Vigo, Vigo, Spain.

Belén Beltrán (B)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital Universitario y Politécnico de La Fe, Valencia, Spain.

Jesús Barrio (J)

Hospital Universitario Rio Hortega, Valladolid.

Cristina Alba (C)

Hospital Clínico San Carlos and Instituto de Investigación del Hospital Clínico San Carlos (IdISSC), Madrid, Spain.

Irene Moraleja (I)

Hospital de Galdakao, Galdakao, Vizcaya, Spain.

Antonio López-Sanromán (A)

Hospital Universitario Ramón y Cajal, Madrid, Spain.

Sabino Riestra (S)

Hospital Universitario Central De Asturias, Instituto de Investigación Sanitaria del Principado de Asturias (ISPA), Oviedo, Spain.

Pilar Martínez Montiel (P)

Hospital 12 de Octubre, Madrid, Spain.

Ana Garre (A)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital Universitario de La Princesa, Instituto de Investigación Sanitaria Princesa (IIS-IP), Universidad Autónoma de Madrid, Madrid, Spain.

Laura Arranz (L)

Hospital Universitario Nuestra Señora Candelaria, Santa Cruz De Tenerife, Spain.

María José García (MJ)

Hospital Universitario Marqués de Valdecilla and IDIVAL, Santander, Spain.

María Dolores Martín Arranz (MD)

Hospital Universitario La Paz and Instituto de Investigación del Hospital Universitario La Paz, IdiPaz, Madrid.

Pilar Corsino (P)

Hospital Universitario Miguel Servet, Zaragoza, Spain.

Lara Arias (L)

Hospital Universitario de Burgos, Burgos, Spain.

Luis Fernández-Salazar (L)

Hospital Clínico Universitario de Valladolid, Valladolid, Spain.

Alejandra Fernández-Pordomingo (A)

Hospital Universitario de Salamanca, Salamanca, Spain.

Montserrat Andreu (M)

Parc de Salut Mar, Barcelona, Spain.

Eva Iglesias (E)

Hospital Universitario Reina Sofía and Instituto Maimónides de Investigación Biomédica de Córdoba (IMIBIC), Córdoba, Spain.

Yolanda Ber (Y)

Hospital General San Jorge, Huesca, Spain.

Raquel Mena (R)

Consorci Sanitari Terrassa, Terrassa, Spain.

María Teresa Arroyo Villarino (MT)

Hospital Clínico Universitario "Lozano Blesa" and Aragón Health Research Institute (IIS Aragón), Zaragoza, Spain.

María Mora (M)

Hospital de Manises, Valencia, Spain.

Lucía Ruiz (L)

Hospital General Universitario de Valencia, Valencia, Spain.

Pilar López-Serrano (P)

Hospital Universitario Fundación Alcorcón, Madrid, Spain.

Isabel Blazquez (I)

Hospital Universitario de Torrejón and Universidad Francisco de Vitoria, Madrid, Spain.

Albert Villoria (A)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Complejo hospitalario de Navarra, Pamplona, Spain.

María Fernández (M)

Corporació Sanitària Universitària Parc Taulí, Universitat Autònoma de Barcelona, Sabadell, Spain.

Fernando Bermejo (F)

Hospital Universitario de Fuenlabrada and Instituto de Investigación del Hospital Universitario La Paz, IdiPaz, Madrid, Spain.

Jesus M Banales (JM)

Hospital Donostia/Instituto Biodonostia, Universidad del País Vasco UPV/EHU, Donostia-San Sebastián, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Ikerbasque (Basque Foundation for Sciencies), Bilbao, Spain.

Eugeni Domènech (E)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital Universitari Germans Trias i Pujol, Badalona, Spain.

Javier P Gisbert (JP)

Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBERehd), Spain.
Hospital Universitario de La Princesa, Instituto de Investigación Sanitaria Princesa (IIS-IP), Universidad Autónoma de Madrid, Madrid, Spain.

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