Precision Medicine.
data-driven decision science
dynamic treatment regimes
machine learning
patient heterogeneity
statistical inference
Journal
Annual review of statistics and its application
ISSN: 2326-8298
Titre abrégé: Annu Rev Stat Appl
Pays: United States
ID NLM: 101622422
Informations de publication
Date de publication:
Mar 2019
Mar 2019
Historique:
entrez:
11
5
2019
pubmed:
11
5
2019
medline:
11
5
2019
Statut:
ppublish
Résumé
Precision medicine seeks to maximize the quality of healthcare by individualizing the healthcare process to the uniquely evolving health status of each patient. This endeavor spans a broad range of scientific areas including drug discovery, genetics/genomics, health communication, and causal inference all in support of evidence-based, i.e., data-driven, decision making. Precision medicine is formalized as a treatment regime which comprises a sequence of decision rules, one per decision point, which map up-to-date patient information to a recommended action. The potential actions could be the selection of which drug to use, the selection of dose, timing of administration, specific diet or exercise recommendation, or other aspects of treatment or care. Statistics research in precision medicine is broadly focused on methodological development for estimation of and inference for treatment regimes which maximize some cumulative clinical outcome. In this review, we provide an overview of this vibrant area of research and present important and emerging challenges.
Identifiants
pubmed: 31073534
doi: 10.1146/annurev-statistics-030718-105251
pmc: PMC6502478
mid: NIHMS983058
doi:
Types de publication
Journal Article
Langues
eng
Pagination
263-286Subventions
Organisme : NCI NIH HHS
ID : P01 CA142538
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK108073
Pays : United States
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