Histone Deacetylase Inhibition with Panobinostat Combined with Intensive Induction Chemotherapy in Older Patients with Acute Myeloid Leukemia: Phase I Study Results.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
15 08 2019
Historique:
received: 15 01 2019
revised: 15 04 2019
accepted: 28 05 2019
pubmed: 4 6 2019
medline: 20 8 2020
entrez: 2 6 2019
Statut: ppublish

Résumé

The histone deacetylase (HDAC) inhibitor panobinostat potentiates anthracycline and cytarabine cytotoxicity in acute myeloid leukemia (AML) cells. We hypothesized that panobinostat prior to and during induction chemotherapy would be tolerable and augment response in patients showing increased histone acetylation. Patients received panobinostat 20-60 mg oral daily on days 1, 3, 5, and 8 with daunorubicin 60 mg/m Twenty-five patients ages 60-85 years (median age, 69) were treated. Fifteen patients had Panobinostat with "7+3" for older patients with AML was well tolerated. Panobinostat 50 mg on days 1, 3, 5, and 8 starting 2 days prior to "7+3" is recommended for future studies. Panobinostat-induced increases in histone acetylation in PBMCs predicted CR/CRi.

Identifiants

pubmed: 31152020
pii: 1078-0432.CCR-19-0171
doi: 10.1158/1078-0432.CCR-19-0171
doi:

Substances chimiques

Antineoplastic Agents 0
Histone Deacetylase Inhibitors 0
Histones 0

Types de publication

Clinical Trial, Phase I Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

4917-4923

Informations de copyright

©2019 American Association for Cancer Research.

Auteurs

Matthew J Wieduwilt (MJ)

University of California, San Diego, La Jolla, California. mwieduwilt@ucsd.edu.

Nela Pawlowska (N)

University of California, San Francisco, San Francisco, California.

Scott Thomas (S)

University of California, San Francisco, San Francisco, California.

Rebecca Olin (R)

University of California, San Francisco, San Francisco, California.

Aaron C Logan (AC)

University of California, San Francisco, San Francisco, California.

Lloyd E Damon (LE)

University of California, San Francisco, San Francisco, California.

Thomas Martin (T)

University of California, San Francisco, San Francisco, California.

McNancy Kang (M)

University of California, San Francisco, San Francisco, California.

Peter H Sayre (PH)

University of California, San Francisco, San Francisco, California.

Wanda Boyer (W)

University of California, San Francisco, San Francisco, California.

Karin M L Gaensler (KML)

University of California, San Francisco, San Francisco, California.

Kirsten Anderson (K)

University of California, Los Angeles, Los Angeles, California.

Pamela N Munster (PN)

University of California, San Francisco, San Francisco, California.

Charalambos Andreadis (C)

University of California, San Francisco, San Francisco, California.

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Classifications MeSH