Plasma AR status and cabazitaxel in heavily treated metastatic castration-resistant prostate cancer.


Journal

European journal of cancer (Oxford, England : 1990)
ISSN: 1879-0852
Titre abrégé: Eur J Cancer
Pays: England
ID NLM: 9005373

Informations de publication

Date de publication:
07 2019
Historique:
received: 12 12 2018
revised: 26 04 2019
accepted: 07 05 2019
pubmed: 15 6 2019
medline: 2 6 2020
entrez: 15 6 2019
Statut: ppublish

Résumé

Plasma androgen receptor (AR) copy number status has been identified as a potential biomarker of response in patients with metastatic castration-resistant prostate cancer (mCRPC) receiving docetaxel or the AR-targeted therapies abiraterone or enzalutamide. However, the relevance of plasma AR status in the context of cabazitaxel therapy is unknown. Between September 2011 and January 2018, pretherapy plasma samples were collected from 155 patients treated with second- or third-line cabazitaxel at standard or reduced dose in different biomarker protocols. Droplet digital polymerase chain reaction was used to identify plasma AR gain and normal samples. The primary objective was to evaluate associations of plasma AR status with treatment outcome. In an exploratory analysis, a comparison between plasma AR and treatment type was investigated by incorporating updated data from our prior study of 85 post-docetaxel patients receiving abiraterone or enzalutamide. We observed a shorter median overall survival (OS) and progression-free survival (PFS) in AR-gained compared to AR-normal patients (OS 10.5 versus 14.1 months, hazard ratio (HR) = 1.44, 95% confidence interval [CI] 0.98-2.13, P = 0.064 and PFS 4.0 versus 5.0 months, HR = 1.47, 95% CI 1.05-2.07, P = 0.024). In patients with mCRPC receiving second-line therapies, a significant treatment interaction was observed between plasma AR and cabazitaxel versus AR-directed therapies for OS (P = 0.041) but not PFS (P = 0.244). In an exploratory analysis, AR-gained patients treated with initial reduced dose of cabazitaxel had a significantly shorter median OS (7.3 versus 11.5 months, HR = 1.95, 95% CI 1.13-3.38, P = 0.016) and PFS (2.7 versus 5.0 months, HR = 2.27, 95% CI 1.39-3.71, P = 0.001). Plasma AR status has a potential clinical utility in patients being considered for cabazitaxel. Validation of these findings in prospective trials is warranted.

Sections du résumé

BACKGROUND
Plasma androgen receptor (AR) copy number status has been identified as a potential biomarker of response in patients with metastatic castration-resistant prostate cancer (mCRPC) receiving docetaxel or the AR-targeted therapies abiraterone or enzalutamide. However, the relevance of plasma AR status in the context of cabazitaxel therapy is unknown.
PATIENTS AND METHODS
Between September 2011 and January 2018, pretherapy plasma samples were collected from 155 patients treated with second- or third-line cabazitaxel at standard or reduced dose in different biomarker protocols. Droplet digital polymerase chain reaction was used to identify plasma AR gain and normal samples. The primary objective was to evaluate associations of plasma AR status with treatment outcome. In an exploratory analysis, a comparison between plasma AR and treatment type was investigated by incorporating updated data from our prior study of 85 post-docetaxel patients receiving abiraterone or enzalutamide.
RESULTS
We observed a shorter median overall survival (OS) and progression-free survival (PFS) in AR-gained compared to AR-normal patients (OS 10.5 versus 14.1 months, hazard ratio (HR) = 1.44, 95% confidence interval [CI] 0.98-2.13, P = 0.064 and PFS 4.0 versus 5.0 months, HR = 1.47, 95% CI 1.05-2.07, P = 0.024). In patients with mCRPC receiving second-line therapies, a significant treatment interaction was observed between plasma AR and cabazitaxel versus AR-directed therapies for OS (P = 0.041) but not PFS (P = 0.244). In an exploratory analysis, AR-gained patients treated with initial reduced dose of cabazitaxel had a significantly shorter median OS (7.3 versus 11.5 months, HR = 1.95, 95% CI 1.13-3.38, P = 0.016) and PFS (2.7 versus 5.0 months, HR = 2.27, 95% CI 1.39-3.71, P = 0.001).
CONCLUSION
Plasma AR status has a potential clinical utility in patients being considered for cabazitaxel. Validation of these findings in prospective trials is warranted.

Identifiants

pubmed: 31200322
pii: S0959-8049(19)30310-7
doi: 10.1016/j.ejca.2019.05.007
pii:
doi:

Substances chimiques

AR protein, human 0
Antineoplastic Agents 0
Biomarkers, Tumor 0
Receptors, Androgen 0
Taxoids 0
cabazitaxel 51F690397J

Types de publication

Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

158-168

Subventions

Organisme : Medical Research Council
ID : MR/P002072/1
Pays : United Kingdom
Organisme : Prostate Cancer UK
ID : PG12-49
Pays : United Kingdom

Informations de copyright

Copyright © 2019 Elsevier Ltd. All rights reserved.

Auteurs

Vincenza Conteduca (V)

Istituto Scientifico Romagnolo per Io Studio e La Cura dei Tumori (IRST) IRCCS, Meldola, Italy; University College London Cancer Institute, London, UK. Electronic address: vincenza.conteduca@irst.emr.it.

Elena Castro (E)

Prostate Cancer Research Unit, Spanish National Cancer Research Centre (CNIO), Madrid, Spain; Hospital Universitario Quirón, Madrid, Spain.

Daniel Wetterskog (D)

University College London Cancer Institute, London, UK.

Emanuela Scarpi (E)

Istituto Scientifico Romagnolo per Io Studio e La Cura dei Tumori (IRST) IRCCS, Meldola, Italy.

Anuradha Jayaram (A)

University College London Cancer Institute, London, UK.

Nuria Romero-Laorden (N)

Prostate Cancer Research Unit, Spanish National Cancer Research Centre (CNIO), Madrid, Spain; Medical Oncology Department, Hospital Universitario La Princesa, Madrid, Spain.

David Olmos (D)

Prostate Cancer Research Unit, Spanish National Cancer Research Centre (CNIO), Madrid, Spain; CNIO-IBIMA Genitourinary Cancer Unit, Hospitales Universitarios Virgen de Ia Victoria y Regional de Málaga, Instituto de Investigación Biomédica de Málaga, Spain.

Giorgia Gurioli (G)

Istituto Scientifico Romagnolo per Io Studio e La Cura dei Tumori (IRST) IRCCS, Meldola, Italy.

Cristian Lolli (C)

Istituto Scientifico Romagnolo per Io Studio e La Cura dei Tumori (IRST) IRCCS, Meldola, Italy.

Maria Isabel Sáez (MI)

CNIO-IBIMA Genitourinary Cancer Unit, Hospitales Universitarios Virgen de Ia Victoria y Regional de Málaga, Instituto de Investigación Biomédica de Málaga, Spain.

Javier Puente (J)

Medical Oncology Department, Hospital Clínico San Carlos, Instituto de Investigación Sanitaria del Hospital Clínico San Carlos (IdISSC), CIBERONC, Madrid, Spain.

Giuseppe Schepisi (G)

Istituto Scientifico Romagnolo per Io Studio e La Cura dei Tumori (IRST) IRCCS, Meldola, Italy.

Samanta Salvi (S)

Istituto Scientifico Romagnolo per Io Studio e La Cura dei Tumori (IRST) IRCCS, Meldola, Italy.

Anna Wingate (A)

University College London Cancer Institute, London, UK.

Ana Medina (A)

Medical Oncology Department, Centro Oncológico de Galicia, A Coruña, Spain.

Rosa Querol-Niñerola (R)

Hospital de Mataró, Mataró, Spain.

Mercedes Marin-Aguilera (M)

Medical Oncology Department, IDIBAPS, Hospital Clínico y Provincial, Barcelona, Spain.

Jose Angel Arranz (JA)

Medical Oncology Department, Gregorio Marañón University Hospital, Madrid, Spain.

Giuseppe Fornarini (G)

Medical Oncology Unit, Ospedale Policlinico San Martino, Genoa, Italy.

Umberto Basso (U)

Medical Oncology Unit 1, Istituto Oncologico Veneto IOV IRCCS, Padua, Italy.

Begoña Mellado (B)

Medical Oncology Department, IDIBAPS, Hospital Clínico y Provincial, Barcelona, Spain.

Enrique Gonzalez-Billalabeitia (E)

Department of Hematology & Medical Oncology, Hospital Universitario Morales Meseguer, IMIB-Universidad de Murcia, Murcia, Spain; Universidad Católica San Antonio de Murcia-UCAM, Murcia, Spain.

Gerhardt Attard (G)

University College London Cancer Institute, London, UK. Electronic address: g.attard@ucl.ac.uk.

Ugo De Giorgi (U)

Istituto Scientifico Romagnolo per Io Studio e La Cura dei Tumori (IRST) IRCCS, Meldola, Italy.

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Classifications MeSH