Tisagenlecleucel CAR T-cell therapy in secondary CNS lymphoma.


Journal

Blood
ISSN: 1528-0020
Titre abrégé: Blood
Pays: United States
ID NLM: 7603509

Informations de publication

Date de publication:
12 09 2019
Historique:
received: 21 05 2019
accepted: 10 07 2019
pubmed: 20 7 2019
medline: 24 1 2020
entrez: 20 7 2019
Statut: ppublish

Résumé

Chimeric antigen receptor (CAR) T cells targeting CD19 have emerged as a leading engineered T-cell therapy for relapsed/refractory B-cell non-Hodgkin lymphoma. The phase 1/2 clinical trials that led to US Food and Drug Administration approval excluded patients with central nervous system (CNS) involvement, due to strict eligibility criteria. Here, we report on our institutional experience with 8 secondary CNS lymphoma patients treated with commercial tisagenlecleucel. No patient experienced greater than grade 1 neurotoxicity, and no patient required tocilizumab or steroids for CAR T-cell-mediated toxicities. Biomarker analysis suggested CAR T-cell expansion, despite the absence of systemic disease, and early response assessments demonstrated activity of IV infused CAR T cells within the CNS space.

Identifiants

pubmed: 31320380
pii: S0006-4971(20)30006-9
doi: 10.1182/blood.2019001694
pmc: PMC7022436
doi:

Substances chimiques

Receptors, Antigen, T-Cell 0
tisagenlecleucel Q6C9WHR03O

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

860-866

Commentaires et corrections

Type : CommentIn

Informations de copyright

© 2019 by The American Society of Hematology.

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Auteurs

Matthew J Frigault (MJ)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.
Blood and Marrow Transplant Program, Massachusetts General Hospital.

Jorg Dietrich (J)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.
Division of Neuro-Oncology, Department of Neurology, Massachusetts General Hospital Cancer Center.

Maria Martinez-Lage (M)

Department of Pathology, Massachusetts General Hospital.

Mark Leick (M)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.

Bryan D Choi (BD)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.
Department of Neurosurgery, Massachusetts General Hospital and Harvard Medical School, and.

Zachariah DeFilipp (Z)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.
Blood and Marrow Transplant Program, Massachusetts General Hospital.

Yi-Bin Chen (YB)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.
Blood and Marrow Transplant Program, Massachusetts General Hospital.

Jeremy Abramson (J)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.
Center for Lymphoma, Massachusetts General Hospital Cancer Center, Harvard Medical School, Boston, MA; and.

Jennifer Crombie (J)

Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA.

Philippe Armand (P)

Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA.

Lakshmi Nayak (L)

Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA.

Chris Panzini (C)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.

Lauren S Riley (LS)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.

Kathleen Gallagher (K)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.

Marcela V Maus (MV)

Cellular Immunotherapy Program, Massachusetts General Hospital Cancer Center.
Blood and Marrow Transplant Program, Massachusetts General Hospital.

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Classifications MeSH