Pulmonary Hypertension and Hereditary Hemorrhagic Telangiectasia Related to an ACVRL1 Mutation.


Journal

Internal medicine (Tokyo, Japan)
ISSN: 1349-7235
Titre abrégé: Intern Med
Pays: Japan
ID NLM: 9204241

Informations de publication

Date de publication:
15 Jan 2020
Historique:
pubmed: 13 9 2019
medline: 9 6 2020
entrez: 13 9 2019
Statut: ppublish

Résumé

Pulmonary hypertension and hereditary hemorrhagic telangiectasia (HHT) have an association mediated by activin A receptor type II-like 1 (ACVRL1) gene pathogenic variants. A 30-year-old woman was previously admitted to a hospital due to lung hemorrhage, and was diagnosed with pulmonary hypertension, but stopped follow-up visits. At 48 years of age, she was admitted to our hospital and was diagnosed with HHT. Genetic testing revealed an ACVRL1 pathogenic variant. After the initiation of pulmonary vasodilator treatment, the patient's mean pulmonary artery pressure started to decrease from 43 mmHg, declining to 37 mmHg when she was 58 years of age. This is the first report describing the 28-year follow-up of an HHT and pulmonary hypertension patient with an ACVRL1 mutation.

Identifiants

pubmed: 31511490
doi: 10.2169/internalmedicine.3625-19
pmc: PMC7008044
doi:

Substances chimiques

ACVRL1 protein, human EC 2.7.11.30
Activin Receptors, Type II EC 2.7.11.30

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

221-227

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Auteurs

Tetsuro Yokokawa (T)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.
Department of Pulmonary Hypertension, Fukushima Medical University, Japan.

Koichi Sugimoto (K)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.
Department of Pulmonary Hypertension, Fukushima Medical University, Japan.

Yusuke Kimishima (Y)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.

Tomofumi Misaka (T)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.
Department of Advanced Cardiac Therapeutics, Fukushima Medical University, Japan.

Akiomi Yoshihisa (A)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.
Department of Advanced Cardiac Therapeutics, Fukushima Medical University, Japan.

Hiroko Morisaki (H)

Department of Medical Genetics, Sakakibara Heart Institute, Japan.

Osamu Yamada (O)

Department of Pathology, National Cerebral and Cardiovascular Center, Japan.

Kazuhiko Nakazato (K)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.

Takafumi Ishida (T)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.

Yasuchika Takeishi (Y)

Department of Cardiovascular Medicine, Fukushima Medical University, Japan.

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