Results from a multicenter, noninterventional registry study for multiple myeloma patients who received stem cell mobilization regimens with and without plerixafor.


Journal

Bone marrow transplantation
ISSN: 1476-5365
Titre abrégé: Bone Marrow Transplant
Pays: England
ID NLM: 8702459

Informations de publication

Date de publication:
02 2020
Historique:
received: 14 02 2019
accepted: 15 07 2019
revised: 03 07 2019
pubmed: 20 9 2019
medline: 22 6 2021
entrez: 20 9 2019
Statut: ppublish

Résumé

Plerixafor plus granulocyte-colony stimulating factor (G-CSF) enhances the mobilization of hematopoietic stem cells (HSCs) for collection and subsequent autologous hematopoietic stem cell transplantation (HSCT) in patients with multiple myeloma (MM). This international, multicenter, noninterventional registry study (NCT01362972), evaluated long-term outcomes for MM patients who received plerixafor versus other mobilization regimens. The comparisons were: G-CSF + plerixafor (G-CSF + P) versus G-CSF-; G-CSF + P versus G-CSF + chemotherapy (G-CSF + C); and G-CSF + P + C versus G-CSF + C. Propensity score matching was used to balance groups. Primary outcome measures were progression free survival (PFS), overall survival (OS), and cumulative incidence of relapse (CIR) after transplantation. After propensity matching, 77 versus 41 patients in the G-CSF + P versus G-CSF cohorts, 129 versus 129 in the G-CSF + P versus G-CSF + C cohorts, and 117 versus 117 in the G-CSF + P + C versus G-CSF + C cohorts were matched, respectively. Propensity score matching resulted in a smaller sample size and imbalances were not completely overcome. For both PFS and OS, the upper limits of the hazard ratio 95% confidence intervals exceeded prespecified boundaries; noninferiority was not demonstrated. CIR rates were higher in the plerixafor cohorts. G-CSF + P remains an option for the mobilization of HSCs in poor mobilizers with MM with no substantial differences in PFS, OS, and CIR in comparison with other regimens.

Identifiants

pubmed: 31534192
doi: 10.1038/s41409-019-0676-0
pii: 10.1038/s41409-019-0676-0
pmc: PMC6995780
doi:

Substances chimiques

Benzylamines 0
Cyclams 0
Heterocyclic Compounds 0
plerixafor S915P5499N

Banques de données

ClinicalTrials.gov
['NCT01362972']

Types de publication

Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

356-366

Références

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Auteurs

Curly Morris (C)

Queens University, Belfast, UK. curlymorris_cliff@yahoo.com.

Christian Chabannon (C)

Institut Paoli-Calmettes, Marseille, France.

Tamas Masszi (T)

Semmelweis University, Budapest, Hungary.

Nigel Russell (N)

Nottingham University, Nottingham, UK.

Hareth Nahi (H)

Karolinska University Hospital, Stockholm, Sweden.

Guido Kobbe (G)

University Hospital of Dusseldorf, Dusseldorf, Germany.

Marta Krejci (M)

Department of Internal Medicine, Hematology and Oncology, University Hospital Brno and Faculty of Medicine, Masaryk University, Brno, Czech Republic.

Holger W Auner (HW)

Imperial College London, London, UK.

David Pohlreich (D)

Charles University Hospital, Prague, Czech Republic.

Patrick Hayden (P)

St. James Hospital, Dublin, Ireland.

Grzegorz W Basak (GW)

Medical University of Warsaw, Warsaw, Poland.

Stig Lenhoff (S)

Skanes University Hospital, Lund, Sweden.

Nicolaas Schaap (N)

Radboud University Medical Centre, Nijmegen, The Netherlands.

Anja van Biezen (A)

European Society for Blood and Marrow Transplantation, Leiden, The Netherlands.

Cora Knol (C)

European Society for Blood and Marrow Transplantation, Leiden, The Netherlands.

Simona Iacobelli (S)

University Tor Vergata, Rome, Italy.

Qianying Liu (Q)

Sanofi, Cambridge, MA, USA.

Marina Celanovic (M)

Sanofi, Cambridge, MA, USA.

Laurent Garderet (L)

Hospital Saint Antoine, Paris, France.

Nicolaus Kröger (N)

University Hospital, Hamburg, Germany.

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