Genotypic Categorization of Loeys-Dietz Syndrome Based on 24 Novel Families and Literature Data.


Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
28 09 2019
Historique:
received: 27 08 2019
revised: 17 09 2019
accepted: 21 09 2019
entrez: 2 10 2019
pubmed: 2 10 2019
medline: 23 2 2020
Statut: epublish

Résumé

Loeys-Dietz syndrome (LDS) is a connective tissue disorder first described in 2005 featuring aortic/arterial aneurysms, dissections, and tortuosity associated with craniofacial, osteoarticular, musculoskeletal, and cutaneous manifestations. Heterozygous mutations in 6 genes (

Identifiants

pubmed: 31569402
pii: genes10100764
doi: 10.3390/genes10100764
pmc: PMC6826414
pii:
doi:

Substances chimiques

SMAD3 protein, human 0
Smad3 Protein 0
TGFB2 protein, human 0
Transforming Growth Factor beta2 0
Receptor, Transforming Growth Factor-beta Type I EC 2.7.11.30
Receptor, Transforming Growth Factor-beta Type II EC 2.7.11.30
TGFBR1 protein, human EC 2.7.11.30
TGFBR2 protein, human EC 2.7.11.30

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't Review

Langues

eng

Sous-ensembles de citation

IM

Déclaration de conflit d'intérêts

All authors declare that there is no conflict of interest concerning this work.

Références

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pubmed: 29392890
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pubmed: 24577266

Auteurs

Letizia Camerota (L)

Human Genetics Institute, Department of Life, Health, and Environmental Sciences, University of L'Aquila, 67100 L'Aquila, Italy. letizia.camerota@guest.univaq.it.

Marco Ritelli (M)

Division of Biology and Genetics, Department of Molecular and Translational Medicine, University of Brescia, 25123 Brescia, Italy. marco.ritelli@unibs.it.

Anita Wischmeijer (A)

Clinical Genetics Unit, Department of Pediatrics, Regional Hospital of Bolzano, 39100 Bolzano, Italy. rosanna.monetta@graduate.univaq.it.

Silvia Majore (S)

Medical Genetics Laboratory, Department of Molecular Medicine, Sapienza University, 00185 Rome, Italy. valeria.cinquina1@unibs.it.
San Camillo-Forlanini Hospital, 00152 Rome, Italy. valeria.cinquina1@unibs.it.

Valeria Cinquina (V)

Division of Biology and Genetics, Department of Molecular and Translational Medicine, University of Brescia, 25123 Brescia, Italy. titiaanita.wischmeijer@sabes.it.

Paola Fortugno (P)

Laboratory of Molecular and Cell Biology, Istituto Dermopatico dell'Immacolata, IDI-IRCCS, 00167 Rome, Italy. smajore@scamilloforlanini.rm.it.

Rosanna Monetta (R)

Human Genetics Institute, Department of Life, Health, and Environmental Sciences, University of L'Aquila, 67100 L'Aquila, Italy. p.fortugno@idi.it.
Laboratory of Molecular and Cell Biology, Istituto Dermopatico dell'Immacolata, IDI-IRCCS, 00167 Rome, Italy. p.fortugno@idi.it.

Laura Gigante (L)

Department of Biomedicine and Prevention, Tor Vergata University, 00133 Rome, Italy. laura.gigante84@gmail.com.
Medical Genetics Unit, Policlinico Tor Vergata University Hospital, 00133 Rome, Italy. laura.gigante84@gmail.com.
Human Genetics Institute, Department of Life, Health, and Environmental Sciences, University of L'Aquila, 67100 L'Aquila, Italy. sangiuolo@med.uniroma2.it.

Federica Carla Sangiuolo (FC)

Department of Biomedicine and Prevention, Tor Vergata University, 00133 Rome, Italy. novelli@med.uniroma2.it.
Medical Genetics Unit, Policlinico Tor Vergata University Hospital, 00133 Rome, Italy. novelli@med.uniroma2.it.

Giuseppe Novelli (G)

Department of Biomedicine and Prevention, Tor Vergata University, 00133 Rome, Italy.
Medical Genetics Unit, Policlinico Tor Vergata University Hospital, 00133 Rome, Italy.
IRCCS Neuromed Institute, 86077 Pozzilli, Italy.

Marina Colombi (M)

Division of Biology and Genetics, Department of Molecular and Translational Medicine, University of Brescia, 25123 Brescia, Italy. francesco.brancati@univaq.it.

Francesco Brancati (F)

Human Genetics Institute, Department of Life, Health, and Environmental Sciences, University of L'Aquila, 67100 L'Aquila, Italy. marina.colombi@unibs.it.
Laboratory of Molecular and Cell Biology, Istituto Dermopatico dell'Immacolata, IDI-IRCCS, 00167 Rome, Italy. marina.colombi@unibs.it.

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Classifications MeSH