Discovery of a Novel Cabazitaxel Nanoparticle-Drug Conjugate (CRLX522) with Improved Pharmacokinetic Properties and Anticancer Effects Using a β-Cyclodextrin-PEG Copolymer Based Delivery Platform.


Journal

Journal of medicinal chemistry
ISSN: 1520-4804
Titre abrégé: J Med Chem
Pays: United States
ID NLM: 9716531

Informations de publication

Date de publication:
14 11 2019
Historique:
pubmed: 9 10 2019
medline: 17 6 2020
entrez: 9 10 2019
Statut: ppublish

Résumé

Novel nanoparticle-drug conjugates (NDCs) containing diverse, clinically relevant anticancer drug payloads (docetaxel, cabazitaxel, and gemcitabine) were successfully generated and tested in drug discovery studies. The NDCs utilized structurally varied linkers that attached the drug payloads to a β-cyclodextrin-PEG copolymer to form self-assembled nanoparticles. In vitro release studies revealed a diversity of release rates driven by linker structure-activity relationships (SARs). Improved in vivo pharmacokinetics (PK) for the cabazitaxel (CBTX) NDCs with glycinate-containing (

Identifiants

pubmed: 31593466
doi: 10.1021/acs.jmedchem.9b00892
doi:

Substances chimiques

Antineoplastic Agents 0
Drug Carriers 0
Taxoids 0
beta-Cyclodextrins 0
Polyethylene Glycols 3WJQ0SDW1A
cabazitaxel 51F690397J

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

9541-9559

Auteurs

Chester A Metcalf (CA)

Novartis Institutes for BioMedical Research Inc. , 181 Massachusetts Avenue , Cambridge , Massachusetts 02139 , United States.

Sonke Svenson (S)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Jungyeon Hwang (J)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Snehlata Tripathi (S)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Geeti Gangal (G)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Sujan Kabir (S)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Douglas Lazarus (D)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Roderic Cole (R)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Beata Sweryda-Krawiec (B)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Pochi Shum (P)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Donna Brown (D)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Roy I Case (RI)

Novartis Institutes for BioMedical Research Inc. , 181 Massachusetts Avenue , Cambridge , Massachusetts 02139 , United States.

Derek van der Poll (D)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Ellen Rohde (E)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

Stephanie Harlfinger (S)

Novartis Institutes for BioMedical Research Inc. , 181 Massachusetts Avenue , Cambridge , Massachusetts 02139 , United States.

Chi-Hse Teng (CH)

Novartis Institutes for BioMedical Research Inc. , 181 Massachusetts Avenue , Cambridge , Massachusetts 02139 , United States.

Scott Eliasof (S)

Cerulean Pharma Inc. , 35 Gatehouse Drive , Waltham , Massachusetts 02451 , United States.

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Classifications MeSH