Severe Peripheral Joint Laxity is a Distinctive Clinical Feature of Spondylodysplastic-Ehlers-Danlos Syndrome (EDS)-

Ehlers–Danlos syndrome (EDS) SEMDJL-Beighton type) beta-1,3-galactosyltransferase 6 (B3GALT6) beta-1,4-galactosyltransferase 7 (B4GALT7) doughy skin on the hands and feet extreme laxity of distal joints soft spEDS-B3GALT6 spEDS-B4GALT7 spondylodysplastic Ehlers–Danlos syndrome (spEDS) spondyloepimetaphyseal dysplasia with joint laxity (SEMDJL1

Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
12 10 2019
Historique:
received: 30 08 2019
revised: 25 09 2019
accepted: 11 10 2019
entrez: 17 10 2019
pubmed: 17 10 2019
medline: 27 2 2020
Statut: epublish

Résumé

Variations in genes encoding for the enzymes responsible for synthesizing the linker region of proteoglycans may result in recessive conditions known as "linkeropathies". The two phenotypes related to mutations in genes

Identifiants

pubmed: 31614862
pii: genes10100799
doi: 10.3390/genes10100799
pmc: PMC6826576
pii:
doi:

Substances chimiques

B3GALT6 protein, human EC 2.4.1.-
Galactosyltransferases EC 2.4.1.-
xylosylprotein 4-beta-galactosyltransferase EC 2.4.1.133

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Déclaration de conflit d'intérêts

All authors declare that there are no conflicts of interest concerning this work.

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Auteurs

Stefano Giuseppe Caraffi (SG)

Medical Genetics Unit, Maternal and Child Health Department, Azienda USL-IRCCS of Reggio Emilia, 42122 Reggio Emilia, Italy. stefanogiuseppe.caraffi@ausl.re.it.

Ilenia Maini (I)

Medical Genetics Unit, Maternal and Child Health Department, Azienda USL-IRCCS of Reggio Emilia, 42122 Reggio Emilia, Italy. imaini@ausl.pr.it.
Child Neuropsychiatry Unit, Azienda USL of Parma, 43125 Parma, Italy. imaini@ausl.pr.it.

Ivan Ivanovski (I)

Medical Genetics Unit, Maternal and Child Health Department, Azienda USL-IRCCS of Reggio Emilia, 42122 Reggio Emilia, Italy. ivan.ivanovski@ausl.re.it.
Department of Surgical, Medical, Dental and Morphological Sciences with interest in Transplant, Oncology and Regenerative Medicine, University of Modena and Reggio Emilia, 42121 Reggio Emilia, Italy. ivan.ivanovski@ausl.re.it.

Marzia Pollazzon (M)

Medical Genetics Unit, Maternal and Child Health Department, Azienda USL-IRCCS of Reggio Emilia, 42122 Reggio Emilia, Italy. marzia.pollazzon@ausl.re.it.

Sara Giangiobbe (S)

Medical Genetics Unit, Maternal and Child Health Department, Azienda USL-IRCCS of Reggio Emilia, 42122 Reggio Emilia, Italy. sara.giangiobbe@ausl.re.it.

Maurizia Valli (M)

Department of Molecular Medicine, Unit of Biochemistry, University of Pavia, 27100 Pavia, Italy. zuffardi@unipv.it.

Antonio Rossi (A)

Department of Molecular Medicine, Unit of Biochemistry, University of Pavia, 27100 Pavia, Italy. antonio.rossi@unipv.it.

Silvia Sassi (S)

Rehabilitation Pediatric Unit, Azienda USL-IRCCS of Reggio Emilia, Reggio Emilia, 42122 Reggio Emilia, Italy. silvia.sassi@ausl.re.it.

Silvia Faccioli (S)

Rehabilitation Pediatric Unit, Azienda USL-IRCCS of Reggio Emilia, Reggio Emilia, 42122 Reggio Emilia, Italy. silvia.faccioli@ausl.re.it.

Maja Di Rocco (MD)

Department of Pediatrics, Unit of Rare Diseases, IRCCS Istituto Giannina Gaslini, 16147 Genoa, Italy. majadirocco@gaslini.org.

Cinzia Magnani (C)

Neonatology and Neonatal Intensive Care Unit, Maternal and Child Department, University of Parma, 43121 Parma, Italy. cinzia.magnani@unipr.it.

Belinda Campos-Xavier (B)

Division of Genetic Medicine, Centre Hospitalier Universitaire Vaudois (CHUV), University of Lausanne, 1011 Lausanne, Switzerland. belinda.xavier@chuv.ch.

Sheila Unger (S)

Division of Genetic Medicine, Centre Hospitalier Universitaire Vaudois (CHUV), University of Lausanne, 1011 Lausanne, Switzerland. sheila.unger@chuv.ch.

Andrea Superti-Furga (A)

Division of Genetic Medicine, Centre Hospitalier Universitaire Vaudois (CHUV), University of Lausanne, 1011 Lausanne, Switzerland. asuperti@unil.ch.

Livia Garavelli (L)

Medical Genetics Unit, Maternal and Child Health Department, Azienda USL-IRCCS of Reggio Emilia, 42122 Reggio Emilia, Italy. livia.garavelli@ausl.re.it.

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