Positive Impact of Expert Reference Center Validation on Performance of Next-Generation Sequencing for Genetic Diagnosis of Autoinflammatory Diseases.

autoinflammatory diseases multidisciplinary consultation next-generation sequencing

Journal

Journal of clinical medicine
ISSN: 2077-0383
Titre abrégé: J Clin Med
Pays: Switzerland
ID NLM: 101606588

Informations de publication

Date de publication:
18 10 2019
Historique:
received: 21 08 2019
revised: 10 10 2019
accepted: 15 10 2019
entrez: 23 10 2019
pubmed: 23 10 2019
medline: 23 10 2019
Statut: epublish

Résumé

Monogenic autoinflammatory diseases (AIDs) are caused by variants in genes that regulate innate immunity. The current diagnostic performance of targeted next-generation sequencing (NGS) for AIDs is low. We assessed whether pre-analytic advice from expert clinicians could help improve NGS performance from our 4 years of experience with the sequencing of a panel of 55 AIDs genes. The study included all patients who underwent routine NGS testing between September 2014 and January 2019 at the laboratory of autoinflammatory diseases (Montpellier, France). Before March 2018, all medical requests for testing were accepted. After this time, we required validation by a reference center before NGS: the positive advice could be obtained after a face-to-face consultation with the patient or presentation of the patient's case at a multidisciplinary staff meeting. Targeted NGS resulted in an overall 7% genetic confirmation, which is consistent with recent reports. The diagnostic performance before and after implementation of the new pre-requisite increased from 6% to 10% (

Identifiants

pubmed: 31635385
pii: jcm8101729
doi: 10.3390/jcm8101729
pmc: PMC6832712
pii:
doi:

Types de publication

Journal Article

Langues

eng

Subventions

Organisme : Ministère des Affaires Sociales et de la Santé
ID : No grant. Funding as National Reference Center.
Pays : International

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Auteurs

Guilaine Boursier (G)

Department of Medical Genetics, Rare Diseases and Personalized Medicine, CHU Montpellier, Rare and Autoinflammatory diseases unit, Univ Montpellier, 34295 Montpellier, France. g-boursier@chu-montpellier.fr.

Cécile Rittore (C)

Department of Medical Genetics, Rare Diseases and Personalized Medicine, CHU Montpellier, Rare and Autoinflammatory diseases unit, Univ Montpellier, 34295 Montpellier, France. cecile.rittore@inserm.fr.

Sophie Georgin-Lavialle (S)

Department of Internal Medicine, CEREMAIA, Tenon Hospital, AP-HP, University of Pierre et Marie Curie, 75970 Paris, France. sophie.georgin-lavialle@aphp.fr.

Alexandre Belot (A)

Paediatric Nephrology, Rheumatology, Dermatology Unit, RAISE, HFME, HCL, Univ Lyon, 69677 Bron, France. alexandre.belot@chu-lyon.fr.

Caroline Galeotti (C)

Department of Paediatric Rheumatology, CEREMAIA, Bicêtre Hospital, AP-HP, 94275 Le Kremlin-Bicêtre, France. caroline.galeotti@aphp.fr.

Eric Hachulla (E)

Department of Internal Medicine and Clinical Immunology, CHU Lille, University of Lille, 59037 Lille, France. Eric.HACHULLA@chru-lille.fr.

Véronique Hentgen (V)

Department of General Pediatrics, CEREMAIA, CH Versailles, 78157 Le Chesnay, France. vhentgen@ch-versailles.fr.

Linda Rossi-Semerano (L)

Department of Paediatric Rheumatology, CEREMAIA, Bicêtre Hospital, AP-HP, 94275 Le Kremlin-Bicêtre, France. linda.rossi@aphp.fr.

Guillaume Sarrabay (G)

Cellules souches, plasticité cellulaire, médecine régénératrice et immunothérapies, INSERM, University Montpellier, Department of Medical Genetics, Rare Diseases and Personalized Medicine, CEREMAIA, CHU Montpellier, 34295 Montpellier, France. guillaume.sarrabay@inserm.fr.

Isabelle Touitou (I)

Cellules souches, plasticité cellulaire, médecine régénératrice et immunothérapies, INSERM, University Montpellier, Department of Medical Genetics, Rare Diseases and Personalized Medicine, CEREMAIA, CHU Montpellier, 34295 Montpellier, France. isabelle.touitou@inserm.fr.

Classifications MeSH