First-in-human phase I clinical trial of a combined immune modulatory approach using TetMYB vaccine and Anti-PD-1 antibody in patients with advanced solid cancer including colorectal or adenoid cystic carcinoma: The MYPHISMO study protocol (NCT03287427).

Adenoid cystic carcinoma Cancer vaccine Colorectal neoplasms Glandular and epithelial neoplasms Immune checkpoint therapy Immunotherapy

Journal

Contemporary clinical trials communications
ISSN: 2451-8654
Titre abrégé: Contemp Clin Trials Commun
Pays: Netherlands
ID NLM: 101671157

Informations de publication

Date de publication:
Dec 2019
Historique:
received: 07 01 2019
revised: 30 06 2019
accepted: 09 07 2019
entrez: 26 10 2019
pubmed: 28 10 2019
medline: 28 10 2019
Statut: epublish

Résumé

MYB is a transcription factor that is overexpressed in colorectal cancer (CRC) and also a driver mutation in adenoid cystic carcinoma (AdCC). Therefore, the MYB protein is an ideal target to vaccinate against to aid recruitment of tumour infiltrating lymphocytes (TILs) against these tumours. The Peter MacCallum Cancer Centre (Melbourne, Australia) has engineered a DNA vaccine, TetMYB, based on the pVAX1 plasmid vector carrying a fusion construct consisting of the universal tetanus toxin T-cell epitopes flanking an inactivated This prospective first-in-human phase I single-arm multi-centre clinical trial involves patients with metastatic CRC or AdCC. Stage 1 will evaluate the safety profile of escalating doses of TetMYB vaccine, given sequentially and in combination with an anti-PD-1 inhibitory antibody, to determine the maximum tolerated dose (MTD). Stage 2 will assess the MTD in an expanded cohort. The calculated sample size is 32 patients: 12 in Stage 1 and 20 in Stage 2. The expected total duration of the trial is 3 years with 15 months of recruitment followed by a minimum of 18 months follow-up. MYB transcription factor is aberrantly overexpressed in a range of epithelial cancers, not limited to the above tumour types. Based on promising pre-clinical data of vaccine-induced tumour clearance and establishment of anti-tumour memory, we are embarking on this first-in-human trial. If successful, the results from this trial will allow progression to a Phase II trial and validation of this breakthrough immunotherapeutic approach, not only in CRC and AdCC, but other MYB over-expressing cancers. ClinicalTrials.gov ID: NCT03287427. Registered: September 19, 2017.

Sections du résumé

BACKGROUND BACKGROUND
MYB is a transcription factor that is overexpressed in colorectal cancer (CRC) and also a driver mutation in adenoid cystic carcinoma (AdCC). Therefore, the MYB protein is an ideal target to vaccinate against to aid recruitment of tumour infiltrating lymphocytes (TILs) against these tumours. The Peter MacCallum Cancer Centre (Melbourne, Australia) has engineered a DNA vaccine, TetMYB, based on the pVAX1 plasmid vector carrying a fusion construct consisting of the universal tetanus toxin T-cell epitopes flanking an inactivated
METHODS METHODS
This prospective first-in-human phase I single-arm multi-centre clinical trial involves patients with metastatic CRC or AdCC. Stage 1 will evaluate the safety profile of escalating doses of TetMYB vaccine, given sequentially and in combination with an anti-PD-1 inhibitory antibody, to determine the maximum tolerated dose (MTD). Stage 2 will assess the MTD in an expanded cohort. The calculated sample size is 32 patients: 12 in Stage 1 and 20 in Stage 2. The expected total duration of the trial is 3 years with 15 months of recruitment followed by a minimum of 18 months follow-up.
DISCUSSION CONCLUSIONS
MYB transcription factor is aberrantly overexpressed in a range of epithelial cancers, not limited to the above tumour types. Based on promising pre-clinical data of vaccine-induced tumour clearance and establishment of anti-tumour memory, we are embarking on this first-in-human trial. If successful, the results from this trial will allow progression to a Phase II trial and validation of this breakthrough immunotherapeutic approach, not only in CRC and AdCC, but other MYB over-expressing cancers.
TRIAL REGISTRATION BACKGROUND
ClinicalTrials.gov ID: NCT03287427. Registered: September 19, 2017.

Identifiants

pubmed: 31650066
doi: 10.1016/j.conctc.2019.100409
pii: S2451-8654(19)30007-9
pii: 100409
pmc: PMC6804811
doi:

Banques de données

ClinicalTrials.gov
['NCT03287427']

Types de publication

Journal Article

Langues

eng

Pagination

100409

Informations de copyright

© 2019 Published by Elsevier Inc.

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Auteurs

Toan Pham (T)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.
Division of Cancer Surgery, Peter MacCallum Cancer Centre, Melbourne, Australia.
Sir Peter MacCallum Department of Oncology, University of Melbourne, Melbourne, Australia.
Department of Surgery, University of Melbourne, Melbourne, Australia.

Lloyd Pereira (L)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.

Sara Roth (S)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.

Laura Galletta (L)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.

Emma Link (E)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.

Tim Akhurst (T)

Division of Medical Imaging, Peter MacCallum Cancer Centre, Melbourne, Australia.

Ben Solomon (B)

Sir Peter MacCallum Department of Oncology, University of Melbourne, Melbourne, Australia.
Division of Medical Oncology, Peter MacCallum Cancer Centre, Melbourne, Australia.

Michael Michael (M)

Sir Peter MacCallum Department of Oncology, University of Melbourne, Melbourne, Australia.
Division of Medical Oncology, Peter MacCallum Cancer Centre, Melbourne, Australia.

Phillip Darcy (P)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.

Shienny Sampurno (S)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.

Alexander Heriot (A)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.
Division of Cancer Surgery, Peter MacCallum Cancer Centre, Melbourne, Australia.
Sir Peter MacCallum Department of Oncology, University of Melbourne, Melbourne, Australia.
Department of Surgery, University of Melbourne, Melbourne, Australia.

Robert Ramsay (R)

Division of Cancer Research, Peter MacCallum Cancer Centre, Melbourne, Australia.
Sir Peter MacCallum Department of Oncology, University of Melbourne, Melbourne, Australia.
Department of Pathology, University of Melbourne, Melbourne, Australia.

Jayesh Desai (J)

Sir Peter MacCallum Department of Oncology, University of Melbourne, Melbourne, Australia.
Division of Medical Oncology, Peter MacCallum Cancer Centre, Melbourne, Australia.

Classifications MeSH