Improved Androgen Receptor Splice Variant 7 Detection Using a Highly Sensitive Assay to Predict Resistance to Abiraterone or Enzalutamide in Metastatic Prostate Cancer Patients.

Androgen receptor signaling inhibitors Androgen receptor splice variant 7 (AR-V7) Circulating tumor cells Highly sensitive AR-V7 assay Liquid profiling Metastatic castration-resistant prostate cancer

Journal

European urology oncology
ISSN: 2588-9311
Titre abrégé: Eur Urol Oncol
Pays: Netherlands
ID NLM: 101724904

Informations de publication

Date de publication:
08 2021
Historique:
received: 02 05 2019
revised: 04 07 2019
accepted: 15 08 2019
pubmed: 5 11 2019
medline: 2 2 2022
entrez: 3 11 2019
Statut: ppublish

Résumé

In metastatic castration-resistant prostate cancer (mCRPC), androgen receptor splice variant 7 (AR-V7) expression is associated with a low response to androgen receptor signaling (ARS) inhibitors such as abiraterone or enzalutamide. To perform a highly sensitive assay for detecting AR-V7 (hsAR-V7) in circulating tumor cells (CTCs) and evaluate its ability to predict response to ARS inhibitors. From 41 mCRPC patients, CTCs were prospectively enriched using AdnaTest platform and analyzed for AR-V7 with and without the highly sensitive assay. The first objective of the study was to compare AR-V7 detection rates with and without the highly sensitive assay. Next, we investigated how AR-V7 (detected without the highly sensitive assay) and hsAR-V7 status influenced prostate-specific antigen (PSA) response and long-term clinical outcomes (PSA progression-free survival [PFS] and radiological PFS) after ARS-inhibitor treatment. Finally, discriminatory abilities of the assays were assessed by C-index to compare their impact on long-term clinical outcomes. AR-V7 detection rates increased from 22% to 56% when the highly sensitive assay was used. The discriminatory abilities of hsAR-V7 for PSA PFS (C-index, 0.74; 95% confidence interval [CI], 0.60-0.88) and radiological PFS (0.70; 95% CI, 0.55-0.85) were higher than those of AR-V7 detected without the highly sensitive assay (0.60, 0.51-0.72, and 0.56, 0.44-0.67, respectively). After ARS-inhibitor treatment, PSA response was lower in hsAR-V7 The hsAR-V7 assay achieved the highest AR-V7 detection rates among those reported in mCRPC. Discriminatory abilities for long-term clinical outcomes were better with hsAR-V7 assay. We prospectively analyzed circulating tumor cells from men with metastatic castration-resistant prostate cancer for androgen receptor splice variant 7 (AR-V7) status using a highly sensitive assay. It yielded higher AR-V7 detection rates and predicted resistance to androgen receptor signaling inhibitors with better discriminatory abilities for long-term clinical outcomes.

Sections du résumé

BACKGROUND
In metastatic castration-resistant prostate cancer (mCRPC), androgen receptor splice variant 7 (AR-V7) expression is associated with a low response to androgen receptor signaling (ARS) inhibitors such as abiraterone or enzalutamide.
OBJECTIVE
To perform a highly sensitive assay for detecting AR-V7 (hsAR-V7) in circulating tumor cells (CTCs) and evaluate its ability to predict response to ARS inhibitors.
DESIGN, SETTING, AND PARTICIPANTS
From 41 mCRPC patients, CTCs were prospectively enriched using AdnaTest platform and analyzed for AR-V7 with and without the highly sensitive assay.
OUTCOME MEASUREMENTS AND STATISTICAL ANALYSIS
The first objective of the study was to compare AR-V7 detection rates with and without the highly sensitive assay. Next, we investigated how AR-V7 (detected without the highly sensitive assay) and hsAR-V7 status influenced prostate-specific antigen (PSA) response and long-term clinical outcomes (PSA progression-free survival [PFS] and radiological PFS) after ARS-inhibitor treatment. Finally, discriminatory abilities of the assays were assessed by C-index to compare their impact on long-term clinical outcomes.
RESULTS AND LIMITATIONS
AR-V7 detection rates increased from 22% to 56% when the highly sensitive assay was used. The discriminatory abilities of hsAR-V7 for PSA PFS (C-index, 0.74; 95% confidence interval [CI], 0.60-0.88) and radiological PFS (0.70; 95% CI, 0.55-0.85) were higher than those of AR-V7 detected without the highly sensitive assay (0.60, 0.51-0.72, and 0.56, 0.44-0.67, respectively). After ARS-inhibitor treatment, PSA response was lower in hsAR-V7
CONCLUSIONS
The hsAR-V7 assay achieved the highest AR-V7 detection rates among those reported in mCRPC. Discriminatory abilities for long-term clinical outcomes were better with hsAR-V7 assay.
PATIENT SUMMARY
We prospectively analyzed circulating tumor cells from men with metastatic castration-resistant prostate cancer for androgen receptor splice variant 7 (AR-V7) status using a highly sensitive assay. It yielded higher AR-V7 detection rates and predicted resistance to androgen receptor signaling inhibitors with better discriminatory abilities for long-term clinical outcomes.

Identifiants

pubmed: 31676281
pii: S2588-9311(19)30136-1
doi: 10.1016/j.euo.2019.08.010
pii:
doi:

Substances chimiques

Androstenes 0
Benzamides 0
Nitriles 0
Receptors, Androgen 0
Phenylthiohydantoin 2010-15-3
enzalutamide 93T0T9GKNU
abiraterone G819A456D0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

609-617

Informations de copyright

Copyright © 2019 European Association of Urology. Published by Elsevier B.V. All rights reserved.

Auteurs

Denis Maillet (D)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Centre de Recherche en Cancérologie de Lyon, INSERM 1052 CNRS UMR 5286, Centre Léon Berard, Université Claude Bernard Lyon 1, Lyon, France; Centre d'études, de Recherche et de Valorisation en Oncologie (CERVO), Faculté de Médecine et de Maïeutique Lyon Sud-Charles Mérieux, Pierre-Bénite, France. Electronic address: denis.maillet@chu-lyon.fr.

Nathalie Allioli (N)

Centre de Recherche en Cancérologie de Lyon, INSERM 1052 CNRS UMR 5286, Centre Léon Berard, Université Claude Bernard Lyon 1, Lyon, France; Centre d'études, de Recherche et de Valorisation en Oncologie (CERVO), Faculté de Médecine et de Maïeutique Lyon Sud-Charles Mérieux, Pierre-Bénite, France; Institut des Sciences Pharmaceutiques et Biologiques, Faculté de Pharmacie, Université Claude Bernard Lyon 1, Lyon, France.

Julien Peron (J)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Service de Biostatistique et Bioinformatique, Hospices Civils de Lyon, Lyon, France; Laboratoire de Biométrie et Biologie Evolutive, Equipe Biostatistique-Santé, CNRS UMR 5558, Université Claude Bernard Lyon 1, Villeurbanne, France.

Adriana Plesa (A)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Service d'Hématologie Biologique, Centre Hospitalier Lyon Sud, Pierre-Bénite, France.

Myriam Decaussin-Petrucci (M)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Centre de Recherche en Cancérologie de Lyon, INSERM 1052 CNRS UMR 5286, Centre Léon Berard, Université Claude Bernard Lyon 1, Lyon, France; Faculté de Médecine et de Maïeutique Lyon-Sud-Charles Mérieux, Université Claude Bernard Lyon 1, Pierre-Bénite, France; Service d'Anatomie et de Cytologie Pathologiques, Centre Hospitalier Lyon Sud, Hospices Civils de Lyon, Pierre-Bénite, France.

Sophie Tartas (S)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France.

Alain Ruffion (A)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Centre de Recherche en Cancérologie de Lyon, INSERM 1052 CNRS UMR 5286, Centre Léon Berard, Université Claude Bernard Lyon 1, Lyon, France; Centre d'études, de Recherche et de Valorisation en Oncologie (CERVO), Faculté de Médecine et de Maïeutique Lyon Sud-Charles Mérieux, Pierre-Bénite, France; Faculté de Médecine et de Maïeutique Lyon-Sud-Charles Mérieux, Université Claude Bernard Lyon 1, Pierre-Bénite, France; Service d'Urologie, Centre Hospitalier Lyon Sud, Hospices Civils de Lyon, Pierre-Bénite, France.

Sébatien Crouzet (S)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Service d'Urologie, Hôpital Edouard Herriot, Hospices Civils de Lyon, Lyon, France; Faculté de Médecine Lyon Est, Université Claude Bernard Lyon 1, Lyon, France.

Ruth Rimokh (R)

Centre de Recherche en Cancérologie de Lyon, INSERM 1052 CNRS UMR 5286, Centre Léon Berard, Université Claude Bernard Lyon 1, Lyon, France.

Pierre-Germain Gillet (PG)

Centre de Recherche en Cancérologie de Lyon, INSERM 1052 CNRS UMR 5286, Centre Léon Berard, Université Claude Bernard Lyon 1, Lyon, France; Centre d'études, de Recherche et de Valorisation en Oncologie (CERVO), Faculté de Médecine et de Maïeutique Lyon Sud-Charles Mérieux, Pierre-Bénite, France; Faculté de Médecine et de Maïeutique Lyon-Sud-Charles Mérieux, Université Claude Bernard Lyon 1, Pierre-Bénite, France; Service d'Anatomie et de Cytologie Pathologiques, Centre Hospitalier Lyon Sud, Hospices Civils de Lyon, Pierre-Bénite, France.

Gilles Freyer (G)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Faculté de Médecine et de Maïeutique Lyon-Sud-Charles Mérieux, Université Claude Bernard Lyon 1, Pierre-Bénite, France.

Virginie Vlaeminck-Guillem (V)

Institut de Cancérologie des Hospices Civils de Lyon, Lyon, France; Centre de Recherche en Cancérologie de Lyon, INSERM 1052 CNRS UMR 5286, Centre Léon Berard, Université Claude Bernard Lyon 1, Lyon, France; Centre d'études, de Recherche et de Valorisation en Oncologie (CERVO), Faculté de Médecine et de Maïeutique Lyon Sud-Charles Mérieux, Pierre-Bénite, France; Faculté de Médecine Lyon Est, Université Claude Bernard Lyon 1, Lyon, France; Service de Biochimie Biologie Moléculaire Sud, Centre Hospitalier Lyon Sud, Hospices Civils de Lyon, Pierre-Bénite, France. Electronic address: virginie.vlaeminck-guillem@univ-lyon1.fr.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH