Safety and Efficacy of Rituximab and Cyclophosphamide in a Case of Resistant Acquired Hemophilia A in Course of Chronic Lymphocytic Leukemia.

acquired hemophilia cyclophosphamide factor viii inhibitor immunosuppressive treatment rituximab steroids

Journal

Cureus
ISSN: 2168-8184
Titre abrégé: Cureus
Pays: United States
ID NLM: 101596737

Informations de publication

Date de publication:
12 Sep 2019
Historique:
entrez: 9 11 2019
pubmed: 9 11 2019
medline: 9 11 2019
Statut: epublish

Résumé

Acquired Hemophilia A (AHA) is a rare disease caused by anti-factor VIII autoantibodies. It is usually characterized by clinically significant bleeding at the onset and requires prompt hemostatic and immunosuppressive therapies. Due to its rarity and the lack of randomized trials, its treatment is a great challenge, especially in the relapse/refractory setting. This report presents the case of a patient diagnosed with chronic lymphocytic leukemia who developed a steroid-resistant AHA, successfully managed with aggressive immunosuppressive therapy.

Identifiants

pubmed: 31700733
doi: 10.7759/cureus.5630
pmc: PMC6822901
doi:

Types de publication

Case Reports

Langues

eng

Pagination

e5630

Informations de copyright

Copyright © 2019, Mazziotta et al.

Déclaration de conflit d'intérêts

The authors have declared that no competing interests exist.

Références

Hematology Am Soc Hematol Educ Program. 2006;:432-7
pubmed: 17124095
BJOG. 2012 Nov;119(12):1529-37
pubmed: 22901076
Am J Hematol. 2017 Sep;92(9):946-965
pubmed: 28782884
Leukemia. 1999 Aug;13(8):1294
pubmed: 10450761
J Thromb Haemost. 2012 Apr;10(4):622-31
pubmed: 22321904
Blood Coagul Fibrinolysis. 2015 Dec;26(8):967-71
pubmed: 26517066
Am J Hematol. 1995 Oct;50(2):149-50
pubmed: 7573000
Environ Health Perspect. 1999 Oct;107 Suppl 5:811-3
pubmed: 10502548
Blood Transfus. 2015 Jul;13(3):498-513
pubmed: 26192778
Semin Oncol. 2006 Apr;33(2):230-9
pubmed: 16616070
Am J Hematol. 2017 Jul;92(7):695-705
pubmed: 28470674
Haematologica. 2007 Jan;92(1):66-71
pubmed: 17229637
Haematologica. 2008 Mar;93(3):447-50
pubmed: 18287133
Clin Exp Immunol. 2009 Jan;155(1):1-15
pubmed: 19076824
Br J Haematol. 2010 Jan;148(2):183-94
pubmed: 19814739
Blood. 2012 Jul 5;120(1):39-46
pubmed: 22618709
Blood. 2008 Jul 15;112(2):250-5
pubmed: 18463353
Blood. 2012 Jul 5;120(1):47-55
pubmed: 22517903
Leukemia. 2011 Mar;25(3):473-8
pubmed: 21127498
Crit Rev Oncol Hematol. 2007 Jul;63(1):47-52
pubmed: 17236786

Auteurs

Francesco Mazziotta (F)

Genomec School of Doctorate, University of Siena, Siena, ITA.

Nadia Cecconi (N)

Clinical and Experimental Medicine, University of Pisa, Pisa, ITA.

Lorenzo Iovino (L)

Clinical and Experimental Medicine, University of Pisa, Pisa, ITA.

Giulia Cervetti (G)

Clinical and Experimental Medicine, University of Pisa, Pisa, ITA.

Mario Petrini (M)

Clinical and Experimental Medicine, University of Pisa, Pisa, ITA.

Classifications MeSH