Comprehensive clinical, biochemical and genetic screening reveals four distinct

GBA Gaucher disease Genotype-phenotype correlation

Journal

Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422

Informations de publication

Date de publication:
Dec 2019
Historique:
received: 24 07 2019
revised: 07 10 2019
accepted: 08 10 2019
entrez: 12 11 2019
pubmed: 12 11 2019
medline: 12 11 2019
Statut: epublish

Résumé

Gaucher disease (GD) is a lysosomal storage disorder that is associated with bi-allelic pathogenic variants in

Identifiants

pubmed: 31709146
doi: 10.1016/j.ymgmr.2019.100532
pii: S2214-4269(19)30117-X
pii: 100532
pmc: PMC6831897
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100532

Informations de copyright

© 2019 The Authors.

Références

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Auteurs

P Cullufi (P)

Pediatric Department, University Hospital "Mother Teresa", Tirana, Albania.

M Tabaku (M)

Pediatric Department, University Hospital "Mother Teresa", Tirana, Albania.

C Beetz (C)

CENTOGENE AG, Rostock, Germany.

S Tomori (S)

Pediatric Department, University Hospital "Mother Teresa", Tirana, Albania.

V Velmishi (V)

Pediatric Department, University Hospital "Mother Teresa", Tirana, Albania.

A Gjikopulli (A)

Pediatric Department, University Hospital "Mother Teresa", Tirana, Albania.

P Bauer (P)

CENTOGENE AG, Rostock, Germany.

S Wirth (S)

Department of Pediatrics, HELIOS University Hospital Wuppertal, Centre for Clinical and Translational Research, Wuppertal, Germany.

A Rolfs (A)

CENTOGENE AG, Rostock, Germany.
University of Rostock, Medical Faculty, Rostock, Germany.

Classifications MeSH