Splanchnic vein thromboses associated with myeloproliferative neoplasms: An international, retrospective study on 518 cases.


Journal

American journal of hematology
ISSN: 1096-8652
Titre abrégé: Am J Hematol
Pays: United States
ID NLM: 7610369

Informations de publication

Date de publication:
02 2020
Historique:
received: 05 10 2019
revised: 01 11 2019
accepted: 05 11 2019
pubmed: 14 11 2019
medline: 6 5 2020
entrez: 14 11 2019
Statut: ppublish

Résumé

Myeloproliferative Neoplasms (MPN) course can be complicated by thrombosis involving unusual sites as the splanchnic veins (SVT). Their management is challenging, given their composite vascular risk. We performed a retrospective, cohort study in the framework of the International Working Group for MPN Research and Treatment (IWG-MRT), and AIRC-Gruppo Italiano Malattie Mieloproliferative (AGIMM). A total of 518 MPN-SVT cases were collected and compared with 1628 unselected, control MPN population, matched for disease subtype. Those with MPN-SVT were younger (median 44 years) and enriched in females compared to controls; PV (37.1%) and ET (34.4%) were the most frequent diagnoses. JAK2V617F mutation was highly prevalent (90.2%), and 38.6% of cases had an additional hypercoagulable disorder. SVT recurrence rate was 1.6 per 100 patient-years. Vitamin K-antagonists (VKA) halved the incidence of recurrence (OR 0.48), unlike cytoreduction (OR 0.96), and were not associated with overall or gastrointestinal bleeding in multivariable analysis. Esophageal varices were the only independent predictor for major bleeding (OR 17.4). Among MPN-SVT, risk of subsequent vascular events was skewed towards venous thromboses compared to controls. However, MPN-SVT clinical course was overall benign: SVT were enriched in PMF with lower IPSS, resulting in significantly longer survival than controls; survival was not affected in PV and slightly reduced in ET. MPN-U with SVT (n = 55) showed a particularly indolent phenotype, with no signs of disease evolution. In the to-date largest, contemporary cohort of MPN-SVT, VKA were confirmed effective in preventing recurrence, unlike cytoreduction, and safe; the major risk factor for bleeding was esophageal varices that therefore represent a major therapeutic target.

Identifiants

pubmed: 31721282
doi: 10.1002/ajh.25677
doi:

Substances chimiques

Anticoagulants 0

Types de publication

Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

156-166

Subventions

Organisme : Associazione Italiana per la Ricerca sul Cancro
Pays : International
Organisme : AIRC
Pays : International

Informations de copyright

© 2019 Wiley Periodicals, Inc.

Références

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Auteurs

Emanuela Sant'Antonio (E)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.
Medical Genetics, University of Siena, Siena, Italy.

Paola Guglielmelli (P)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.

Lisa Pieri (L)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.

Massimo Primignani (M)

CRC "A. M. e A. Migliavacca" Center for Liver Disease, Division of Gastroenterology and Hepatology, Foundation IRCCS Cà Granda Maggiore Policlinico Hospital, University of Milan, Milan, Italy.

Maria Luigia Randi (ML)

Department of Medicine - DIMED, University of Padova Medical School, Padova, Italy.

Claudia Santarossa (C)

Department of Medicine - DIMED, University of Padova Medical School, Padova, Italy.

Elisa Rumi (E)

Department of Hematology Oncology, IRCCS Policlinico S. Matteo Foundation and University of Pavia, Pavia, Italy.

Francisco Cervantes (F)

Hematology Department, Hospital Clinic, IDIBAPS, Barcelona, Spain.

Federica Delaini (F)

Hematology and Bone Marrow Transplant Unit, Azienda Ospedaliera Papa Giovanni XXIII, Bergamo, Italy.

Alessandra Carobbio (A)

Hematology and Bone Marrow Transplant Unit, Azienda Ospedaliera Papa Giovanni XXIII, Bergamo, Italy.

Silvia Betti (S)

Institute of Hematology, Catholic University, Fondazione Policlinico A. Gemelli IRCCS, Rome, Italy.

Elena Rossi (E)

Institute of Hematology, Catholic University, Fondazione Policlinico A. Gemelli IRCCS, Rome, Italy.

Noa Lavi (N)

Department of Hematology and Bone Marrow Transplantation, Rambam Health Care Campus, Haifa, Israel.

Claire N Harrison (CN)

Department of Haematology, Guy's and St. Thomas NHS Foundation Trust, London, UK.

Natalia Curto-Garcia (N)

Department of Haematology, Guy's and St. Thomas NHS Foundation Trust, London, UK.

Heinz Gisslinger (H)

Department of Internal Medicine I, Division of Hematology and Blood Coagulation, Medical University of Vienna, Vienna, Austria.

Bettina Gisslinger (B)

Department of Internal Medicine I, Division of Hematology and Blood Coagulation, Medical University of Vienna, Vienna, Austria.

Giorgina Specchia (G)

Department of Emergency and Organ Transplantation, Section of Hematology with Transplantation, Medical School, University of Bari, Bari, Italy.

Alessandra Ricco (A)

Department of Emergency and Organ Transplantation, Section of Hematology with Transplantation, Medical School, University of Bari, Bari, Italy.

Nicola Vianelli (N)

Department of Hematology and Clinical Oncology "L. and A. Seràgnoli" S. Orsola-Malpighi Hospital, Bologna, Italy.

Nicola Polverelli (N)

Department of Hematology and Clinical Oncology "L. and A. Seràgnoli" S. Orsola-Malpighi Hospital, Bologna, Italy.

Maya Koren-Michowitz (M)

Department of Hematology, Shamir Medical Center (Assaf Harofeh), Zerifin, Israel and Sackler school of Medicine, Tel Aviv University, Tel Aviv, Israel.

Marco Ruggeri (M)

Hematology, San Bortolo Hospital, Vicenza, Italy.

Francois Girodon (F)

CHU Dijon, Laboratoire d'Hematologie, Dijon, France.

Martin Ellis (M)

The Hematology Institute and Blood Bank and Translational Hemato-Oncology, Meir Hospital, Kfar-Saba, Israel.

Alessandra Iurlo (A)

Hematology Division, Foundation IRCCS Ca' Granda-Ospedale Maggiore Policlinico, Milan, Italy.

Francesco Mannelli (F)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.

Lara Mannelli (L)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.
Medical Genetics, University of Siena, Siena, Italy.

Benedetta Sordi (B)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.

Giuseppe Gaetano Loscocco (GG)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.

Mario Cazzola (M)

Department of Hematology Oncology, IRCCS Policlinico S. Matteo Foundation and University of Pavia, Pavia, Italy.

Valerio De Stefano (V)

Institute of Hematology, Catholic University, Fondazione Policlinico A. Gemelli IRCCS, Rome, Italy.

Tiziano Barbui (T)

Research Foundation, Azienda Ospedaliera Papa Giovanni XXIII, Bergamo, Italy.

Ayalew Tefferi (A)

Division of Hematology, Mayo Clinic, Rochester, Minnesota.

Alessandro Maria Vannucchi (AM)

CRIMM, Centro di Ricerca e Innovazione per le Malattie Mieloproliferative, Azienda Ospedaliera Universitaria Careggi, Florence, Italy.
Dipartimento di Medicina Sperimentale e Clinica, Università degli Studi, Firenze, DENOTHE Excellence Center, Florence, Italy.

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