A Single Synonymous Variant (c.354G>A [p.P118P]) in

ADAMTS13 codon usage post-translational modifications ribosome profiling specific activity synonymous variant translation

Journal

International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791

Informations de publication

Date de publication:
15 Nov 2019
Historique:
received: 08 10 2019
revised: 09 11 2019
accepted: 13 11 2019
entrez: 17 11 2019
pubmed: 17 11 2019
medline: 9 4 2020
Statut: epublish

Résumé

Synonymous variants within coding regions may influence protein expression and function. We have previously reported increased protein expression levels ex vivo (~120% in comparison to wild-type) from a synonymous polymorphism variant, c.354G>A [p.P118P], of the

Identifiants

pubmed: 31731663
pii: ijms20225734
doi: 10.3390/ijms20225734
pmc: PMC6888508
pii:
doi:

Substances chimiques

ADAMTS13 Protein EC 3.4.24.87
ADAMTS13 protein, human EC 3.4.24.87

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : The American Heart Association
ID : 13GRNT17070025
Organisme : NHLBI NIH HHS
ID : R01 HL128119
Pays : United States
Organisme : NIH HHS
ID : 1R15HL121779-01A1
Pays : United States
Organisme : Department of Energy
ID : Not Applicable
Organisme : NHLBI NIH HHS
ID : R15 HL121779
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK058702
Pays : United States
Organisme : U.S. Food and Drug Administration
ID : MODSCI

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Auteurs

Ryan Hunt (R)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Gaya Hettiarachchi (G)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Upendra Katneni (U)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Nancy Hernandez (N)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

David Holcomb (D)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Jacob Kames (J)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Redab Alnifaidy (R)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Brian Lin (B)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Nobuko Hamasaki-Katagiri (N)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Aaron Wesley (A)

Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
Present Address: Department of Emergency Medicine, Banner University Medical Center, The University of Arizona, Tucson, AZ 85724, USA.

Tal Kafri (T)

Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.

Christina Morris (C)

BioPharmaSpec Ltd., St. Saviour JE2 7LA, UK.

Laura Bouché (L)

Department of Life Sciences, Imperial College London, South Kensington Campus, London SW7 2AZ, UK.
Present Address: Antikor Biopharma Ltd., Stevenage Bioscience Catalyst, Gunnels Wood Road, Stevenage SG1 2FX, UK.

Maria Panico (M)

BioPharmaSpec Ltd., St. Saviour JE2 7LA, UK.
Department of Life Sciences, Imperial College London, South Kensington Campus, London SW7 2AZ, UK.

Tal Schiller (T)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

Juan Ibla (J)

Departments of Cardiac Surgery and Anesthesiology, Perioperative and Pain Medicine, Boston Children's Hospital and Harvard Medical School, Boston, MA 02115, USA.

Haim Bar (H)

Department of Statistics, University of Connecticut, Storrs, CT 06269, USA.

Amra Ismail (A)

Center for Gene Regulation in Health and Disease, Department of Biological, Geological & Environmental Sciences, Cleveland State University, Cleveland, OH 44115, USA.

Howard Morris (H)

BioPharmaSpec Ltd., St. Saviour JE2 7LA, UK.
Department of Life Sciences, Imperial College London, South Kensington Campus, London SW7 2AZ, UK.

Anton Komar (A)

Center for Gene Regulation in Health and Disease, Department of Biological, Geological & Environmental Sciences, Cleveland State University, Cleveland, OH 44115, USA.

Chava Kimchi-Sarfaty (C)

Hemostasis Branch, Division of Plasma Protein Therapeutics, Office of Tissues and Advanced Therapies, Center for Biologics Evaluation & Research, US FDA, Silver Spring, MD 20993, USA.

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