Studying Brugada Syndrome With an SCN1B Variants in Human-Induced Pluripotent Stem Cell-Derived Cardiomyocytes.

Brugada channelopathy genetic sodium channel sudden cardiac death

Journal

Frontiers in cell and developmental biology
ISSN: 2296-634X
Titre abrégé: Front Cell Dev Biol
Pays: Switzerland
ID NLM: 101630250

Informations de publication

Date de publication:
2019
Historique:
received: 24 08 2019
accepted: 17 10 2019
entrez: 19 11 2019
pubmed: 19 11 2019
medline: 19 11 2019
Statut: epublish

Résumé

Among rare channelopathies BrS patients are at high risk of sudden cardiac death (SCD). SCN5A mutations are found in a quarter of patients. Other rare gene mutations including SCN1B have been implicated to BrS. Studying the human cellular phenotype of BrS associated with rare gene mutation remains lacking. We sought to study the cellular phenotype of BrS with the SCN1B gene variants using human-induced pluripotent stem cell (hiPSCs)-derived cardiomyocytes (hiPSC-CMs). A BrS patient suffering from recurrent syncope harboring a two variants (c.629T > C and c.637C > A) in SCN1B, which encodes the function-modifying sodium channel beta1 subunit, and three independent healthy subjects were recruited and their skin biopsies were used to generate hiPSCs, which were differentiated into cardiomyocytes (hiPSC-CMs) for studying the cellular electrophysiology. A significantly reduced peak and late sodium channel current (I Our hiPSC-CMs from a BrS-patient with two variants in SCN1B recapitulated some key phenotypic features of BrS and can provide a platform for studies on BrS with SCN1B variants.

Sections du résumé

BACKGROUND BACKGROUND
Among rare channelopathies BrS patients are at high risk of sudden cardiac death (SCD). SCN5A mutations are found in a quarter of patients. Other rare gene mutations including SCN1B have been implicated to BrS. Studying the human cellular phenotype of BrS associated with rare gene mutation remains lacking.
OBJECTIVES OBJECTIVE
We sought to study the cellular phenotype of BrS with the SCN1B gene variants using human-induced pluripotent stem cell (hiPSCs)-derived cardiomyocytes (hiPSC-CMs).
METHODS AND RESULTS RESULTS
A BrS patient suffering from recurrent syncope harboring a two variants (c.629T > C and c.637C > A) in SCN1B, which encodes the function-modifying sodium channel beta1 subunit, and three independent healthy subjects were recruited and their skin biopsies were used to generate hiPSCs, which were differentiated into cardiomyocytes (hiPSC-CMs) for studying the cellular electrophysiology. A significantly reduced peak and late sodium channel current (I
CONCLUSION CONCLUSIONS
Our hiPSC-CMs from a BrS-patient with two variants in SCN1B recapitulated some key phenotypic features of BrS and can provide a platform for studies on BrS with SCN1B variants.

Identifiants

pubmed: 31737628
doi: 10.3389/fcell.2019.00261
pmc: PMC6839339
doi:

Types de publication

Journal Article

Langues

eng

Pagination

261

Informations de copyright

Copyright © 2019 El-Battrawy, Müller, Zhao, Cyganek, Zhong, Zhang, Kleinsorge, Lan, Li, Xu, Huang, Liao, Moscu-Gregor, Albers, Dinkel, Lang, Diecke, Zimmermann, Utikal, Wieland, Borggrefe, Zhou and Akin.

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Auteurs

Ibrahim El-Battrawy (I)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.

Jonas Müller (J)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.

Zhihan Zhao (Z)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.

Lukas Cyganek (L)

DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.
Stem Cell Unit, Clinic for Cardiology and Pneumology, University Medical Center Göttingen, Göttingen, Germany.

Rujia Zhong (R)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.

Feng Zhang (F)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.

Mandy Kleinsorge (M)

DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.
Stem Cell Unit, Clinic for Cardiology and Pneumology, University Medical Center Göttingen, Göttingen, Germany.

Huan Lan (H)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.
Key Laboratory of Medical Electrophysiology of Ministry of Education and Medical Electrophysiological, Key Laboratory of Sichuan Province, Institute of Cardiovascular Research, Southwest Medical University, Luzhou, China.

Xin Li (X)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.

Qiang Xu (Q)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.

Mengying Huang (M)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.

Zhenxing Liao (Z)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.

Alexander Moscu-Gregor (A)

Center for Human Genetics and Laboratory Medicine, Martinsried, Germany.

Sebastian Albers (S)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.

Hendrik Dinkel (H)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.

Siegfried Lang (S)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.

Sebastian Diecke (S)

Max Delbrück Center for Molecular Medicine, Berlin, Germany.

Wolfram-Hubertus Zimmermann (WH)

DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.
Institute of Pharmacology and Toxicology, University of Göttingen, Göttingen, Germany.

Jochen Utikal (J)

DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.
Skin Cancer Unit, German Cancer Research Center (DKFZ), Heidelberg and Department of Dermatology, Venereology and Allergology, University Medical Center Mannheim, University of Heidelberg, Mannheim, Germany.

Thomas Wieland (T)

DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.
Institute of Experimental and Clinical Pharmacology and Toxicology, Medical Faculty Mannheim, University of Heidelberg, Mannheim, Germany.

Martin Borggrefe (M)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.

Xiaobo Zhou (X)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.
Key Laboratory of Medical Electrophysiology of Ministry of Education and Medical Electrophysiological, Key Laboratory of Sichuan Province, Institute of Cardiovascular Research, Southwest Medical University, Luzhou, China.

Ibrahim Akin (I)

First Department of Medicine, University Medical Centre Mannheim (UMM), Mannheim, Germany.
DZHK (German Center for Cardiovascular Research), Partner Sites Heidelberg-Mannheim and Göttingen, Mannheim, Germany.

Classifications MeSH