The NLRP3 p.A441V Mutation in

IL‐1β NLRP3 NLRP3‐AID cryopyrin‐associated periodic syndromes inflammasome variation

Journal

ACR open rheumatology
ISSN: 2578-5745
Titre abrégé: ACR Open Rheumatol
Pays: United States
ID NLM: 101740025

Informations de publication

Date de publication:
Jun 2019
Historique:
entrez: 29 11 2019
pubmed: 30 11 2019
medline: 30 11 2019
Statut: epublish

Résumé

To determine the molecular and cellular bases of autoinflammatory syndromes in a multigenerational French family with Muckle-Wells syndrome and in a patient originating from Portugal with familial cold autoinflammatory syndrome. Sequencing of The same heterozygous mutation (c.1322C>T, p.A441V) located in the NACHT domain, segregating with the disease within the first family, was identified in the two families. This mutation was found to be associated with different core haplotypes. NLRP3-A441V led to increased ASC speck formation and high levels of secreted IL-1β. Monocyte inflammasome-related gene expression and cytokine secretion, which were within the normal range in patients out of crisis, were found to be differentially regulated between the two probands, correlating with their phenotypic status. These molecular and cellular findings, which indicate a recurrent mutational event, clearly demonstrate the pathogenicity of the p.A441V missense mutation in

Identifiants

pubmed: 31777803
doi: 10.1002/acr2.1039
pii: ACR21039
pmc: PMC6857991
doi:

Types de publication

Journal Article

Langues

eng

Pagination

267-276

Informations de copyright

© 2019 The Authors. ACR Open Rheumatology published by Wiley Periodicals, Inc. on behalf of American College of Rheumatology.

Références

Expert Rev Clin Immunol. 2014 Jan;10(1):7-18
pubmed: 24308832
Cell. 2010 Mar 19;140(6):821-32
pubmed: 20303873
Proc Natl Acad Sci U S A. 2007 May 8;104(19):8041-6
pubmed: 17483456
PLoS One. 2013 Oct 21;8(10):e78045
pubmed: 24205083
Annu Rev Immunol. 2009;27:229-65
pubmed: 19302040
Arthritis Rheum. 2010 Apr;62(4):1176-85
pubmed: 20131254
Am J Hum Genet. 2002 Jun;70(6):1498-506
pubmed: 11992256
J Rheumatol. 2016 Jun;43(6):1101-6
pubmed: 27134254
Arthritis Rheum. 2006 Feb;54(2):508-14
pubmed: 16447225
Exp Ther Med. 2016 Jan;11(1):297-302
pubmed: 26889257
Experientia. 1991 Jan 15;47(1):22-31
pubmed: 1999239
Nat Rev Mol Cell Biol. 2003 Feb;4(2):95-104
pubmed: 12563287
Nat Genet. 2002 Jan;30(1):97-101
pubmed: 11731797
J Immunol. 2003 Dec 15;171(12):6329-33
pubmed: 14662828
J Immunol Methods. 1989 Sep 1;122(2):211-8
pubmed: 2507640
Nat Genet. 2001 Nov;29(3):301-5
pubmed: 11687797
Immunity. 2004 Mar;20(3):319-25
pubmed: 15030775
Sci China Life Sci. 2015 Dec;58(12):1282-7
pubmed: 26582014
Semin Immunopathol. 2015 Jul;37(4):377-85
pubmed: 25963520
Am J Hum Genet. 2002 Jul;71(1):198-203
pubmed: 12032915
Immunol Rev. 2015 May;265(1):6-21
pubmed: 25879280
J Leukoc Biol. 2008 Mar;83(3):507-11
pubmed: 17982111
Methods Mol Biol. 2018;1682:135-147
pubmed: 29039099
Mediators Inflamm. 2013;2013:697972
pubmed: 23818743
J Rheumatol. 2005 Apr;32(4):747-51
pubmed: 15801036
Ann Rheum Dis. 2018 Nov;77(11):1558-1565
pubmed: 30100561
Sensors (Basel). 2010;10(1):97-111
pubmed: 22315529
Nat Rev Immunol. 2017 Mar;17(3):208-214
pubmed: 28163301
PLoS One. 2017 Apr 12;12(4):e0175336
pubmed: 28403163
Cell Death Differ. 2006 Feb;13(2):236-49
pubmed: 16037825

Auteurs

Fawaz Awad (F)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Eman Assrawi (E)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Claire Jumeau (C)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Sylvie Odent (S)

Centre Hospitalier Universitaire de Rennes 35203 Rennes France.

Veronique Despert (V)

Centre Hospitalier Universitaire de Rennes 35203 Rennes France.

Gérard Cam (G)

Centre Hospitalier de Saint-Malo 35400 Saint-Malo France.

Aleth Perdriger (A)

Centre Hospitalier Universitaire de Rennes 35203 Rennes France.

Camille Louvrier (C)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Laetitia Cobret (L)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Bruno Copin (B)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Sandra Chantot-Bastaraud (S)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Philippe Duquesnoy (P)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

William Piterboth (W)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Claire Le Jeunne (C)

Assistance Publique-Hôpitaux de Paris Hôpital Cochin Paris France.

Genevieve Quenum-Miraillet (G)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Jean Pierre Siffroi (JP)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Sophie Georgin-Lavialle (S)

Sorbonne Université INSERM, Hôpital Trousseau and Assistance Publique-Hôpitaux de Paris Hôpital Tenon Paris France.

Gilles Grateau (G)

Sorbonne Université INSERM, Hôpital Trousseau and Assistance Publique-Hôpitaux de Paris Hôpital Tenon Paris France.

Marie Legendre (M)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Irina Giurgea (I)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Sonia-Athina Karabina (SA)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Serge Amselem (S)

Sorbonne Université INSERM, Hôpital Trousseau Paris France.

Classifications MeSH