Severe type I interferonopathy and unrestrained interferon signaling due to a homozygous germline mutation in


Journal

Science immunology
ISSN: 2470-9468
Titre abrégé: Sci Immunol
Pays: United States
ID NLM: 101688624

Informations de publication

Date de publication:
13 12 2019
Historique:
received: 16 10 2018
revised: 29 07 2019
accepted: 14 11 2019
entrez: 15 12 2019
pubmed: 15 12 2019
medline: 4 7 2020
Statut: ppublish

Résumé

Excessive type I interferon (IFNα/β) activity is implicated in a spectrum of human disease, yet its direct role remains to be conclusively proven. We investigated two siblings with severe early-onset autoinflammatory disease and an elevated IFN signature. Whole-exome sequencing revealed a shared homozygous missense Arg148Trp variant in

Identifiants

pubmed: 31836668
pii: 4/42/eaav7501
doi: 10.1126/sciimmunol.aav7501
pmc: PMC7115903
mid: EMS86640
pii:
doi:

Substances chimiques

Interferon Type I 0
STAT2 Transcription Factor 0
STAT2 protein, human 0

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Department of Health
ID : TRF-2016-09-002
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 101788
Pays : United Kingdom
Organisme : Medical Research Council
ID : MC_PC_16054
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 101788/Z/13/Z
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 211153/Z/18/Z
Pays : United Kingdom
Organisme : Wellcome Trust
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 207556
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/N013840/1
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 211153
Pays : United Kingdom
Organisme : MRF
ID : MRF_MRF-159-0002-ELP-BRIGG
Pays : United Kingdom
Organisme : European Research Council
ID : 309449
Pays : International
Organisme : Wellcome Trust
ID : 207556/Z/17/Z
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/R000913/1
Pays : United Kingdom

Informations de copyright

Copyright © 2019 The Authors, some rights reserved; exclusive licensee American Association for the Advancement of Science. No claim to original U.S. Government Works.

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Auteurs

Christopher J A Duncan (CJA)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK. christopher.duncan@ncl.ac.uk tracy.briggs@manchester.ac.uk sophie.hambleton@ncl.ac.uk.
Department of Infection and Tropical Medicine, Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne, UK.

Benjamin J Thompson (BJ)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Rui Chen (R)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Gillian I Rice (GI)

Division of Evolution and Genomic Sciences, School of Biological Sciences, University of Manchester, Manchester, UK.

Florian Gothe (F)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.
Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig-Maximilians-Universität Munich, Munich, Germany.

Dan F Young (DF)

School of Biology, University of St. Andrews, St. Andrews, UK.

Simon C Lovell (SC)

Division of Evolution and Genomic Sciences, School of Biological Sciences, University of Manchester, Manchester, UK.

Victoria G Shuttleworth (VG)

Complement Therapeutics Research Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Vicky Brocklebank (V)

Complement Therapeutics Research Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Bronte Corner (B)

Complement Therapeutics Research Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Andrew J Skelton (AJ)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Vincent Bondet (V)

Immunobiology of Dendritic Cells, Institut Pasteur, Paris, France.

Jonathan Coxhead (J)

Genomics Core Facility, Biosciences Institute, Newcastle University, UK.

Darragh Duffy (D)

Immunobiology of Dendritic Cells, Institut Pasteur, Paris, France.

Cecile Fourrage (C)

Plateforme Bioinformatique, Institut Imagine, Paris, France.

John H Livingston (JH)

Department of Paediatric Neurology, Leeds General Infirmary, Leeds, UK.

Julija Pavaine (J)

Academic Unit of Paediatric Radiology, Royal Manchester Children's Hospital, Central Manchester University Hospitals NHS Foundation Trust, Manchester, UK.
Division of Informatics, Imaging and Data Sciences, School of Health Sciences, Faculty of Biology, Medicine and Health, University of Manchester, Manchester, UK.

Edmund Cheesman (E)

Department of Paediatric Histopathology, Central Manchester University Foundation NHS Trust, Manchester, UK.

Stephania Bitetti (S)

Department of Paediatric Histopathology, Central Manchester University Foundation NHS Trust, Manchester, UK.

Angela Grainger (A)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Meghan Acres (M)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Barbara A Innes (BA)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Aneta Mikulasova (A)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Ruyue Sun (R)

Complement Therapeutics Research Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Rafiqul Hussain (R)

Immunobiology of Dendritic Cells, Institut Pasteur, Paris, France.

Ronnie Wright (R)

Division of Evolution and Genomic Sciences, School of Biological Sciences, University of Manchester, Manchester, UK.
Manchester Centre for Genomic Medicine, St Mary's Hospital, Manchester University Hospitals NHS Foundation Trust, Manchester, UK.

Robert Wynn (R)

Department of Paediatric Blood and Marrow Transplant, Royal Manchester Children's Hospital, Oxford Rd., Manchester, UK.

Mohammed Zarhrate (M)

Genomics Core Facility, Institut Imagine, Paris, France.

Leo A H Zeef (LAH)

Bioinformatics Core Facility, Faculty of Biology, Medicine and Health, University of Manchester, Manchester, UK.

Katrina Wood (K)

Department of Pathology, Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne, UK.

Stephen M Hughes (SM)

Immunology Department, Royal Manchester Children's Hospital, Manchester University Hospitals NHS Foundation Trust, Manchester, UK.

Claire L Harris (CL)

Complement Therapeutics Research Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Karin R Engelhardt (KR)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.

Yanick J Crow (YJ)

MRC Institute of Genetics and Molecular Medicine, Centre for Genomic and Experimental Medicine, The University of Edinburgh, Edinburgh, UK.
Laboratory of Neurogenetics and Neuroinflammation, Institut Imagine, Paris, France.
Paris Descartes University, Sorbonne-Paris-Cité, Paris, France.

Richard E Randall (RE)

School of Biology, University of St. Andrews, St. Andrews, UK.

David Kavanagh (D)

Complement Therapeutics Research Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK.
National Renal Complement Therapeutics Centre, Royal Victoria Infirmary, Newcastle upon Tyne Hosptials NHS Foundation Trust, Newcastle upon Tyne, UK.

Sophie Hambleton (S)

Primary Immunodeficiency Group, Immunity and Inflammation Theme, Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK. christopher.duncan@ncl.ac.uk tracy.briggs@manchester.ac.uk sophie.hambleton@ncl.ac.uk.
Children's Immunology Service, Great North Children's Hospital, Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne, UK.

Tracy A Briggs (TA)

Division of Evolution and Genomic Sciences, School of Biological Sciences, University of Manchester, Manchester, UK. christopher.duncan@ncl.ac.uk tracy.briggs@manchester.ac.uk sophie.hambleton@ncl.ac.uk.
Manchester Centre for Genomic Medicine, St Mary's Hospital, Manchester University Hospitals NHS Foundation Trust, Manchester, UK.

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Classifications MeSH