Journal

Journal of medical genetics
ISSN: 1468-6244
Titre abrégé: J Med Genet
Pays: England
ID NLM: 2985087R

Informations de publication

Date de publication:
04 2020
Historique:
received: 04 07 2019
revised: 13 10 2019
accepted: 22 12 2019
pubmed: 12 1 2020
medline: 5 2 2021
entrez: 12 1 2020
Statut: ppublish

Résumé

Arrhythmogenic right ventricular cardiomyopathy (ARVC) is a heart muscle disease that affects predominantly the right ventricle and is part of the spectrum of arrythmogenic cardiomyopathies (ACMs). ARVC is a genetic condition; however, a pathogenic gene variant is found in only half of patients. Filamin C gene truncations ( One hundred fifty-six patients meeting 2010 ARVC Task Force Criteria and lacking variants in known ARVC genes were evaluated for We identified two unique The identification of

Sections du résumé

BACKGROUND
Arrhythmogenic right ventricular cardiomyopathy (ARVC) is a heart muscle disease that affects predominantly the right ventricle and is part of the spectrum of arrythmogenic cardiomyopathies (ACMs). ARVC is a genetic condition; however, a pathogenic gene variant is found in only half of patients.
OBJECTIVE
Filamin C gene truncations (
METHODS
One hundred fifty-six patients meeting 2010 ARVC Task Force Criteria and lacking variants in known ARVC genes were evaluated for
RESULTS
We identified two unique
CONCLUSION
The identification of

Identifiants

pubmed: 31924696
pii: jmedgenet-2019-106394
doi: 10.1136/jmedgenet-2019-106394
pmc: PMC7539291
mid: NIHMS1633225
doi:

Substances chimiques

FLNC protein, human 0
Filamins 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

254-257

Subventions

Organisme : NHLBI NIH HHS
ID : R01 HL147064
Pays : United States
Organisme : American Heart Association-American Stroke Association
ID : 17GRNT33670495
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR002535
Pays : United States
Organisme : NHGRI NIH HHS
ID : UM1 HG006542
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL069071
Pays : United States
Organisme : NCRR NIH HHS
ID : M01 RR000051
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR001082
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL116906
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL109209
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR001079
Pays : United States

Informations de copyright

© Author(s) (or their employer(s)) 2020. No commercial re-use. See rights and permissions. Published by BMJ.

Déclaration de conflit d'intérêts

Competing interests: None declared.

Références

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Auteurs

Francesca Brun (F)

Cardiovascular Department and Department of Medical Surgical and Health Sciences, University of Trieste, Trieste, Friuli-Venezia Giulia, Italy.

Marta Gigli (M)

Cardiovascular Department and Department of Medical Surgical and Health Sciences, University of Trieste, Trieste, Friuli-Venezia Giulia, Italy.

Sharon L Graw (SL)

Cardiovascular Institute, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Daniel P Judge (DP)

Division of Cardiology, Medical University of South Carolina, Charleston, South Carolina, USA.

Marco Merlo (M)

Cardiovascular Department and Department of Medical Surgical and Health Sciences, University of Trieste, Trieste, Friuli-Venezia Giulia, Italy.

Brittney Murray (B)

Division of Cardiology, Johns Hopkins, Baltimore, Maryland, USA.

Hugh Calkins (H)

Division of Cardiology, Johns Hopkins, Baltimore, Maryland, USA.

Gianfranco Sinagra (G)

Cardiovascular Department and Department of Medical Surgical and Health Sciences, University of Trieste, Trieste, Friuli-Venezia Giulia, Italy.

Matthew Rg Taylor (MR)

Cardiovascular Institute, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.
Adult Medical Genetics Program, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Luisa Mestroni (L)

Cardiovascular Institute, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA luisa.mestroni@CUAnschutz.edu.

Cynthia A James (CA)

Division of Cardiology, Johns Hopkins, Baltimore, Maryland, USA.

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Classifications MeSH