Genomic Profiling of Metastatic Uveal Melanoma and Clinical Results of a Phase I Study of the Protein Kinase C Inhibitor AEB071.


Journal

Molecular cancer therapeutics
ISSN: 1538-8514
Titre abrégé: Mol Cancer Ther
Pays: United States
ID NLM: 101132535

Informations de publication

Date de publication:
04 2020
Historique:
received: 28 01 2019
revised: 24 04 2019
accepted: 23 01 2020
pubmed: 8 2 2020
medline: 7 4 2021
entrez: 8 2 2020
Statut: ppublish

Résumé

Up to 50% of patients with uveal melanoma (UM) develop metastatic disease, for which there is no effective systemic treatment. This study aimed to evaluate the safety and efficacy of the orally available protein kinase C inhibitor, AEB071, in patients with metastatic UM, and to perform genomic profiling of metastatic tumor samples, with the aim to propose combination therapies. Patients with metastatic UM (

Identifiants

pubmed: 32029634
pii: 1535-7163.MCT-19-0098
doi: 10.1158/1535-7163.MCT-19-0098
doi:

Substances chimiques

Biomarkers, Tumor 0
Pyrroles 0
Quinazolines 0
sotrastaurin 7I279E1NZ8
Protein Kinase C EC 2.7.11.13

Types de publication

Clinical Trial, Phase I Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1031-1039

Subventions

Organisme : Department of Health
Pays : United Kingdom

Informations de copyright

©2020 American Association for Cancer Research.

Auteurs

Sophie Piperno-Neumann (S)

Institut Curie, Paris, France. sophie.piperno-neumann@curie.fr.

James Larkin (J)

Royal Marsden NHS Foundation Trust, London, United Kingdom.

Richard D Carvajal (RD)

Memorial Sloan Kettering Cancer Center, New York, New York.

Jason J Luke (JJ)

Dana-Farber Cancer Institute, Boston, Massachusetts.

Gary K Schwartz (GK)

Memorial Sloan Kettering Cancer Center, New York, New York.

F Stephen Hodi (FS)

Dana-Farber Cancer Institute, Boston, Massachusetts.

Marie-Paule Sablin (MP)

Institut Curie, Paris, France.

Alexander N Shoushtari (AN)

Memorial Sloan Kettering Cancer Center, New York, New York.

Sebastian Szpakowski (S)

Novartis Institutes for BioMedical Research, Cambridge, Massachusetts.

Niladri Roy Chowdhury (NR)

Novartis Institutes for BioMedical Research, Cambridge, Massachusetts.

A Rose Brannon (AR)

Novartis Institutes for BioMedical Research, Cambridge, Massachusetts.

Thiruvamoor Ramkumar (T)

Novartis Institutes for BioMedical Research, Cambridge, Massachusetts.

Leanne de Koning (L)

Institut Curie, Paris, France.

Adnan Derti (A)

Novartis Institutes for BioMedical Research, Cambridge, Massachusetts.

Caroline Emery (C)

Novartis Institutes for BioMedical Research, Cambridge, Massachusetts.

Padmaja Yerramilli-Rao (P)

Novartis Institutes for BioMedical Research, Cambridge, Massachusetts.

Ellen Kapiteijn (E)

Leiden University Medical Centre, Department of Medical Oncology, Leiden, the Netherlands.

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Classifications MeSH