Cord blood transplantation for bone marrow failure syndromes: state of art.
Cord blood transplantation (CBT)
Fanconi anemia (FA)
bone marrow failure (BMF)
severe aplastic anemia (SAA)
Journal
Stem cell investigation
ISSN: 2306-9759
Titre abrégé: Stem Cell Investig
Pays: China
ID NLM: 101672113
Informations de publication
Date de publication:
2019
2019
Historique:
received:
19
09
2019
accepted:
16
10
2019
entrez:
11
2
2020
pubmed:
11
2
2020
medline:
11
2
2020
Statut:
epublish
Résumé
Hematopoietic stem cell transplantation (HSCT) and immunosuppressive therapy (IST) represent the milestones of the treatment algorithm for idiopathic and inherited bone marrow failure (BMF) disorders. However, patients lacking a suitable donor or failing IST still have a poor prognosis. Cord blood transplantation (CBT) has extended the possibility of HSCT for many patients in case of the absence of an eligible donor, and although in the last years, this procedure is less used in several hematological diseases, it remains an option for the treatment of patients with BMF syndromes. Nevertheless, optimization of conditioning regimen and cord blood unit selection is warranted to reduce the risk of graft failure and transplant-related mortality. This review summarizes the state of art of CBT in the field of BMF diseases, focusing on historical and recent issues in idiopathic aplastic anemia and inherited disorders.
Identifiants
pubmed: 32039261
doi: 10.21037/sci.2019.10.04
pii: sci-06-2019.10.04
pmc: PMC6987328
doi:
Types de publication
Journal Article
Review
Langues
eng
Pagination
39Informations de copyright
2019 Stem Cell Investigation. All rights reserved.
Déclaration de conflit d'intérêts
Conflicts of Interest: The authors have no conflicts of interest to declare.
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