Study 275: Updated Expanded Access Program for Remestemcel-L in Steroid-Refractory Acute Graft-versus-Host Disease in Children.

Acute graft-versus-host disease Allogeneic hematopoietic cell transplantation Compassionate use Mesenchymal stromal cell Remestemcel-L Steroid

Journal

Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
ISSN: 1523-6536
Titre abrégé: Biol Blood Marrow Transplant
Pays: United States
ID NLM: 9600628

Informations de publication

Date de publication:
05 2020
Historique:
received: 20 11 2019
revised: 30 01 2020
accepted: 31 01 2020
pubmed: 12 2 2020
medline: 24 6 2021
entrez: 12 2 2020
Statut: ppublish

Résumé

Clinical outcomes in children with steroid-refractory acute graft-versus-host disease (SR-aGVHD) are generally poor, with a high mortality rate and limited therapeutic options. Here we report our updated investigational experience with mesenchymal stromal cell (MSC) therapy with remestemcel-L in a multicenter expanded access protocol (ClinicalTrials.gov identifier NCT00759018) in 241 children with aGVHD who failed to respond to steroids with or without other secondary and tertiary immunosuppressive therapies. A total of 241 children with grade B-D SR-aGVHD were enrolled at 50 sites in 8 countries and received 8 biweekly i.v. infusions of human MSCs, 2 × 10

Identifiants

pubmed: 32044400
pii: S1083-8791(20)30059-8
doi: 10.1016/j.bbmt.2020.01.026
pmc: PMC8292970
mid: NIHMS1721330
pii:
doi:

Substances chimiques

Steroids 0

Banques de données

ClinicalTrials.gov
['NCT00759018']

Types de publication

Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

855-864

Subventions

Organisme : NCI NIH HHS
ID : P30 CA008748
Pays : United States

Informations de copyright

Copyright © 2020 American Society for Transplantation and Cellular Therapy. Published by Elsevier Inc. All rights reserved.

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Auteurs

Joanne Kurtzberg (J)

Duke University Medical Center, Durham, North Carolina. Electronic address: joanne.kurtzberg@duke.edu.

Susan Prockop (S)

MSK Kids Memorial Sloan Kettering Cancer Center, New York, New York.

Sonali Chaudhury (S)

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois.

Biljana Horn (B)

University of Florida, Gainesville, Florida.

Eneida Nemecek (E)

Doernbecher Children's Hospital, Oregon Health & Science University, Portland, Oregon.

Vinod Prasad (V)

Duke University Medical Center, Durham, North Carolina.

Prakash Satwani (P)

Columbia University Medical Center, New York, New York.

Pierre Teira (P)

CHU Sainte Justine, Montreal, QC, Canada.

Jack Hayes (J)

Mesoblast Inc, New York, New York.

Elizabeth Burke (E)

Mesoblast Inc, New York, New York.

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Classifications MeSH