Structural Variants May Be a Source of Missing Heritability in sALS.

amyotrophic lateral sclerosis clinical trial stratification genetic marker missing heritability structural variant

Journal

Frontiers in neuroscience
ISSN: 1662-4548
Titre abrégé: Front Neurosci
Pays: Switzerland
ID NLM: 101478481

Informations de publication

Date de publication:
2020
Historique:
received: 21 10 2019
accepted: 13 01 2020
entrez: 22 2 2020
pubmed: 23 2 2020
medline: 23 2 2020
Statut: epublish

Résumé

The underlying genetic and molecular mechanisms that drive amyotrophic lateral sclerosis (ALS) remain poorly understood. Structural variants within the genome can play a significant role in neurodegenerative disease risk, such as the repeat expansion in

Identifiants

pubmed: 32082115
doi: 10.3389/fnins.2020.00047
pmc: PMC7005198
doi:

Types de publication

Journal Article

Langues

eng

Pagination

47

Informations de copyright

Copyright © 2020 Theunissen, Flynn, Anderton, Mastaglia, Pytte, Jiang, Hodgetts, Burns, Saunders, Fletcher, Wilton and Akkari.

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Auteurs

Frances Theunissen (F)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
School of Human Sciences, University of Western Australia, Nedlands, WA, Australia.

Loren L Flynn (LL)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
Centre for Neuromuscular and Neurological Disorders, University of Western Australia, Nedlands, WA, Australia.
Centre for Molecular Medicine and Innovative Therapeutics, Murdoch University, Perth, WA, Australia.

Ryan S Anderton (RS)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
Centre for Neuromuscular and Neurological Disorders, University of Western Australia, Nedlands, WA, Australia.
School of Health Sciences, Institute for Health Research, University of Notre Dame Australia, Fremantle, WA, Australia.

Frank Mastaglia (F)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
Centre for Neuromuscular and Neurological Disorders, University of Western Australia, Nedlands, WA, Australia.

Julia Pytte (J)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
School of Human Sciences, University of Western Australia, Nedlands, WA, Australia.

Leanne Jiang (L)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
School of Biological Sciences, University of Western Australia, Nedlands, WA, Australia.

Stuart Hodgetts (S)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
School of Human Sciences, University of Western Australia, Nedlands, WA, Australia.

Daniel K Burns (DK)

Zinfandel Pharmaceuticals, Chapel Hill, NC, United States.

Ann Saunders (A)

Zinfandel Pharmaceuticals, Chapel Hill, NC, United States.

Sue Fletcher (S)

Centre for Neuromuscular and Neurological Disorders, University of Western Australia, Nedlands, WA, Australia.
Centre for Molecular Medicine and Innovative Therapeutics, Murdoch University, Perth, WA, Australia.

Steve D Wilton (SD)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
Centre for Neuromuscular and Neurological Disorders, University of Western Australia, Nedlands, WA, Australia.
Centre for Molecular Medicine and Innovative Therapeutics, Murdoch University, Perth, WA, Australia.

Patrick Anthony Akkari (PA)

Perron Institute for Neurological and Translational Science, Nedlands, WA, Australia.
Centre for Neuromuscular and Neurological Disorders, University of Western Australia, Nedlands, WA, Australia.
Centre for Molecular Medicine and Innovative Therapeutics, Murdoch University, Perth, WA, Australia.

Classifications MeSH