Endocytosis Inhibition in Humans to Improve Responses to ADCC-Mediating Antibodies.


Journal

Cell
ISSN: 1097-4172
Titre abrégé: Cell
Pays: United States
ID NLM: 0413066

Informations de publication

Date de publication:
05 03 2020
Historique:
received: 03 09 2019
revised: 19 01 2020
accepted: 07 02 2020
entrez: 7 3 2020
pubmed: 7 3 2020
medline: 18 8 2020
Statut: ppublish

Résumé

A safe and controlled manipulation of endocytosis in vivo may have disruptive therapeutic potential. Here, we demonstrate that the anti-emetic/anti-psychotic prochlorperazine can be repurposed to reversibly inhibit the in vivo endocytosis of membrane proteins targeted by therapeutic monoclonal antibodies, as directly demonstrated by our human tumor ex vivo assay. Temporary endocytosis inhibition results in enhanced target availability and improved efficiency of natural killer cell-mediated antibody-dependent cellular cytotoxicity (ADCC), a mediator of clinical responses induced by IgG1 antibodies, demonstrated here for cetuximab, trastuzumab, and avelumab. Extensive analysis of downstream signaling pathways ruled out on-target toxicities. By overcoming the heterogeneity of drug target availability that frequently characterizes poorly responsive or resistant tumors, clinical application of reversible endocytosis inhibition may considerably improve the clinical benefit of ADCC-mediating therapeutic antibodies.

Identifiants

pubmed: 32142680
pii: S0092-8674(20)30163-X
doi: 10.1016/j.cell.2020.02.019
pii:
doi:

Substances chimiques

Antibodies, Monoclonal 0
Antibodies, Monoclonal, Humanized 0
Immunoglobulin G 0
Membrane Proteins 0
avelumab KXG2PJ551I
Trastuzumab P188ANX8CK
Cetuximab PQX0D8J21J
Prochlorperazine YHP6YLT61T

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

895-914.e27

Commentaires et corrections

Type : CommentIn
Type : CommentIn

Informations de copyright

Copyright © 2020 Elsevier Inc. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of interests The authors declare no competing interests other than the following: The avelumab work was conducted under investigator-initiated contract with Merck KGaA. The costs of the experiments were paid for by Merck KGaA and avelumab supplied by Merck. This work utilizes technology subject to the following patents: 2015 WO2014063206-A1 “classifying epidermal growth factor receptor positive tumor into subtype eg epidermal growth factor receptor antagonist sensitive subtype, involves analyzing ligand-induced epidermal growth factor receptor internalization status of tumor.” Simpson, F., Saunders, N.A.; 2015 WO2014063205-A1 “composition useful in kit for treating tumor, preferably cell surface antigen positive tumor eg cancerous tumors, comprises antibody that binds to cell surface antigen of tumor and inhibitor of receptor mediated endocytosis” Simpson, F., Saunders, N.A.

Auteurs

Hui Yi Chew (HY)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Priscila O De Lima (PO)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Jazmina L Gonzalez Cruz (JL)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Blerida Banushi (B)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Godwins Echejoh (G)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Lingbo Hu (L)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Shannon R Joseph (SR)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Benedict Lum (B)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

James Rae (J)

Cell Biology and Molecular Medicine Division, Institute for Molecular Bioscience, University of Queensland, St Lucia QLD 4072, Australia; Australia Centre for Microscopy and Microanalysis, University of Queensland, St Lucia QLD 4072, Australia.

Jake S O'Donnell (JS)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Lilia Merida de Long (L)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Satomi Okano (S)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Brigid King (B)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Rachael Barry (R)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Davide Moi (D)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Roberta Mazzieri (R)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Ranjeny Thomas (R)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Fernando Souza-Fonseca-Guimaraes (F)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Matthew Foote (M)

Princess Alexandra Hospital, Brisbane QLD 4102, Australia.

Adam McCluskey (A)

Centre for Chemistry, Biology and Clinical Pharmacology, The University of Newcastle, Callaghan NSW 2308, Australia.

Phillip J Robinson (PJ)

Cell Signaling Unit, Children's Medical Research Institute, The University of Sydney, Sydney NSW 2145, Australia.

Ian H Frazer (IH)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Nicholas A Saunders (NA)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Robert G Parton (RG)

Cell Biology and Molecular Medicine Division, Institute for Molecular Bioscience, University of Queensland, St Lucia QLD 4072, Australia; Australia Centre for Microscopy and Microanalysis, University of Queensland, St Lucia QLD 4072, Australia.

Riccardo Dolcetti (R)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Katharine Cuff (K)

Princess Alexandra Hospital, Brisbane QLD 4102, Australia; Faculty of Medicine, University of Queensland, Woolloongabba QLD 4102, Australia.

Jennifer H Martin (JH)

Princess Alexandra Hospital, Brisbane QLD 4102, Australia; Centre for Chemistry, Biology and Clinical Pharmacology, The University of Newcastle, Callaghan NSW 2308, Australia.

Benedict Panizza (B)

Princess Alexandra Hospital, Brisbane QLD 4102, Australia; Faculty of Medicine, University of Queensland, Woolloongabba QLD 4102, Australia.

Euan Walpole (E)

Princess Alexandra Hospital, Brisbane QLD 4102, Australia; Faculty of Medicine, University of Queensland, Woolloongabba QLD 4102, Australia.

James W Wells (JW)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia.

Fiona Simpson (F)

The University of Queensland Diamantina Institute, University of Queensland, Woolloongabba QLD 4102, Australia. Electronic address: f.simpson@uq.edu.au.

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Classifications MeSH