Safety and efficacy of talacotuzumab plus decitabine or decitabine alone in patients with acute myeloid leukemia not eligible for chemotherapy: results from a multicenter, randomized, phase 2/3 study.


Journal

Leukemia
ISSN: 1476-5551
Titre abrégé: Leukemia
Pays: England
ID NLM: 8704895

Informations de publication

Date de publication:
01 2021
Historique:
received: 24 07 2019
accepted: 13 02 2020
revised: 11 12 2019
pubmed: 24 3 2020
medline: 14 1 2021
entrez: 24 3 2020
Statut: ppublish

Résumé

Talacotuzumab, a humanized anti-CD123 monoclonal antibody, was evaluated in combination with decitabine in elderly patients with acute myeloid leukemia (AML) not eligible for intensive chemotherapy. A multicenter, phase 2/3 study was initiated to determine the recommended phase 2 dose (RP2D) of talacotuzumab (Part A) followed by an open-label, randomized comparison of talacotuzumab in combination with decitabine versus decitabine alone to assess achievement of complete response (CR) and overall survival (OS) in Part B. Ten patients were enrolled in Part A and 316 in Part B; the results presented here are based on a database lock on January 25, 2018. Part A confirmed the RP2D of talacotuzumab to be 9 mg/kg. In Part B, CR was achieved in 12/80 (15%) patients receiving combination therapy and in 9/82 (11%) patients receiving decitabine alone (odds ratio: 1.4; 95% confidence interval [CI]: 0.6-3.6; p = 0.44). Median (95% CI) OS was 5.36 (4.27-7.95) months for combination therapy versus 7.26 (6.47-8.64) months for decitabine alone (hazard ratio: 1.04; 95% CI: 0.79-1.37; p = 0.78). Combination therapy showed no improvement in efficacy versus decitabine alone, resulting in the Independent Data Monitoring Committee's recommendation of early termination of enrollment and discontinuation of talacotuzumab treatment.

Identifiants

pubmed: 32203138
doi: 10.1038/s41375-020-0773-5
pii: 10.1038/s41375-020-0773-5
pmc: PMC7787975
doi:

Substances chimiques

Antibodies, Monoclonal, Humanized 0
Antineoplastic Agents, Immunological 0
Decitabine 776B62CQ27

Types de publication

Clinical Trial, Phase II Clinical Trial, Phase III Journal Article Multicenter Study Randomized Controlled Trial Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

62-74

Subventions

Organisme : NCI NIH HHS
ID : P30 CA008748
Pays : United States

Références

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Auteurs

Pau Montesinos (P)

Hematology Department, Hospital Universitari i Politècnic La Fe, València, Spain. montesinos_pau@gva.es.
CIBERONC, Instituto Carlos III, Madrid, Spain. montesinos_pau@gva.es.

Gail J Roboz (GJ)

Division of Hematology and Oncology, Department of Medicine, Weill Cornell Medicine and The New York Presbyterian Hospital, New York, NY, USA.

Claude-Eric Bulabois (CE)

CHU Grenoble, Service d'hématologie Clinique, Grenoble, France.

Marion Subklewe (M)

Department of Medicine III, University Hospital Ludwig-Maximillians-Universität München, Munich, Germany.

Uwe Platzbecker (U)

Medical Clinic and Policlinic I, Hematology and Cellular Therapy, Leipzig University Hospital, Leipzig, Germany.

Yishai Ofran (Y)

Department of Hematology and Bone Marrow Transplantation, Rambam Health Care Campus and Technion Faculty of Medicine, Haifa, Israel.

Cristina Papayannidis (C)

Department of Experimental, Diagnostic and Specialty Medicine, Institute of Hematology and Medical Oncology "L. and A. Seragnoli", University of Bologna, Bologna, Italy.

Agnieszka Wierzbowska (A)

Department of Hematology, Medical University of Lodz, Lodz, Poland.

Ho Jin Shin (HJ)

Division of Hematology-Oncology, Department of Internal Medicine, School of Medicine, Medical Research Institute, Pusan National University Hospital, Pusan, Republic of Korea.

Vadim Doronin (V)

Department of Hematology and Chemotherapy, City Clinical Hospital No. 40, Moscow, Russian Federation.

Stefan Deneberg (S)

Department of Hematology, Karolinska University Hospital, Stockholm, Sweden.

Su-Peng Yeh (SP)

Division of Hematology-Oncology, China Medical University Hospital, Taichung, Taiwan.

Mehmet Ali Ozcan (MA)

Department of Hematology, Faculty of Medicine, Dokuz Eylul Universıty, Izmir, Turkey.

Steven Knapper (S)

Cardiff University School of Medicine, Cardiff, UK.

Jorge Cortes (J)

Department of Leukemia, MD Anderson Cancer Center, Houston, TX, USA.

Daniel A Pollyea (DA)

Division of Hematology, School of Medicine, University of Colorado, Aurora, CO, USA.

Gert Ossenkoppele (G)

Department of Hematology, Amsterdam University Medical Center, VUMC, Amsterdam, The Netherlands.

Sergio Giralt (S)

Division of Hematologic Oncology, Memorial Sloan Kettering Cancer Center, New York, NY, USA.

Hartmut Döhner (H)

Department of Internal Medicine III, University Hospital of Ulm, Ulm, Germany.

Michael Heuser (M)

Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany.

Liang Xiu (L)

Janssen Research and Development, Raritan, NJ, USA.

Indrajeet Singh (I)

Janssen Research and Development, Spring House, PA, USA.

Fei Huang (F)

Janssen Research and Development, Spring House, PA, USA.

Julie S Larsen (JS)

Janssen Research and Development, Los Angeles, CA, USA.

Andrew H Wei (AH)

Department of Haematology, The Alfred Hospital and Monash University, Melbourne, VIC, Australia.

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