Resveratrol corrects aberrant splicing of

CUG-BP1 MBNL1 alternative splicing calcium homeostasis foci myotonic dystrophy type 1 myotubes resveratrol

Journal

Neural regeneration research
ISSN: 1673-5374
Titre abrégé: Neural Regen Res
Pays: India
ID NLM: 101316351

Informations de publication

Date de publication:
Sep 2020
Historique:
entrez: 27 3 2020
pubmed: 27 3 2020
medline: 27 3 2020
Statut: ppublish

Résumé

Myotonic dystrophy type 1 (DM1) is a spliceopathy related to the mis-splicing of several genes caused by sequestration of nuclear transcriptional RNA-binding factors from non-coding CUG repeats of DMPK pre-mRNAs. Dysregulation of ryanodine receptor 1 (RYR1), sarcoplasmatic/endoplasmatic Ca

Identifiants

pubmed: 32209783
pii: NeuralRegenRes_2020_15_9_1757_276336
doi: 10.4103/1673-5374.276336
pmc: PMC7437583
doi:

Types de publication

Journal Article

Langues

eng

Pagination

1757-1766

Déclaration de conflit d'intérêts

None

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Auteurs

Massimo Santoro (M)

IRCCS Fondazione Don Carlo Gnocchi, Milan, Italy.

Roberto Piacentini (R)

Department of Neuroscience, Università Cattolica del Sacro Cuore; Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.

Alessia Perna (A)

Department of Neuroscience, Università Cattolica del Sacro Cuore, Rome, Italy.

Eugenia Pisano (E)

Department of Cardiovascular and Thoracic Sciences, Università Cattolica del Sacro Cuore; Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.

Anna Severino (A)

Department of Cardiovascular and Thoracic Sciences, Università Cattolica del Sacro Cuore, Rome, Italy.

Anna Modoni (A)

Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.

Claudio Grassi (C)

Department of Neuroscience, Università Cattolica del Sacro Cuore; Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.

Gabriella Silvestri (G)

Department of Neuroscience, Università Cattolica del Sacro Cuore; Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.

Classifications MeSH