Infant High-Grade Gliomas Comprise Multiple Subgroups Characterized by Novel Targetable Gene Fusions and Favorable Outcomes.


Journal

Cancer discovery
ISSN: 2159-8290
Titre abrégé: Cancer Discov
Pays: United States
ID NLM: 101561693

Informations de publication

Date de publication:
07 2020
Historique:
received: 04 09 2019
revised: 03 03 2020
accepted: 20 03 2020
pubmed: 3 4 2020
medline: 20 11 2021
entrez: 3 4 2020
Statut: ppublish

Résumé

Infant high-grade gliomas appear clinically distinct from their counterparts in older children, indicating that histopathologic grading may not accurately reflect the biology of these tumors. We have collected 241 cases under 4 years of age, and carried out histologic review, methylation profiling, and custom panel, genome, or exome sequencing. After excluding tumors representing other established entities or subgroups, we identified 130 cases to be part of an "intrinsic" spectrum of disease specific to the infant population. These included those with targetable MAPK alterations, and a large proportion of remaining cases harboring gene fusions targeting

Identifiants

pubmed: 32238360
pii: 2159-8290.CD-19-1030
doi: 10.1158/2159-8290.CD-19-1030
pmc: PMC8313225
mid: NIHMS1721217
doi:

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

942-963

Subventions

Organisme : Cancer Research UK
ID : A23536
Pays : United Kingdom
Organisme : Medical Research Council
ID : G0701018
Pays : United Kingdom
Organisme : Medical Research Council
ID : G1100578
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/N004272/1
Pays : United Kingdom
Organisme : NCI NIH HHS
ID : P30 CA008748
Pays : United States
Organisme : NCI NIH HHS
ID : P30 CA021765
Pays : United States
Organisme : NCI NIH HHS
ID : P01 CA096832
Pays : United States

Commentaires et corrections

Type : CommentIn

Informations de copyright

©2020 American Association for Cancer Research.

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Auteurs

Matthew Clarke (M)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Alan Mackay (A)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Britta Ismer (B)

German Cancer Research Center (DKFZ), Heidelberg, Germany.
Faculty of Biosciences, Heidelberg University, Heidelberg, Germany.
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.

Jessica C Pickles (JC)

UCL Great Ormond Street Institute of Child Health, London, United Kingdom.

Ruth G Tatevossian (RG)

Department of Neuropathology, St. Jude Children's Research Hospital, Memphis, Tennessee.

Scott Newman (S)

Department of Computational Biology, St. Jude Children's Research Hospital, Memphis, Tennessee.

Tejus A Bale (TA)

Department of Neuropathology, Memorial Sloan-Kettering Cancer Center, New York, New York.

Iris Stoler (I)

Charité Universitätsmedizin Berlin, corporate member of Freie Universität Berlin, Humboldt-Universität zu Berlin, and Berlin Institute of Health, Department of Neuropathology, Berlin, Germany.

Elisa Izquierdo (E)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Sara Temelso (S)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Diana M Carvalho (DM)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Valeria Molinari (V)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Anna Burford (A)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Louise Howell (L)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.

Alex Virasami (A)

UCL Great Ormond Street Institute of Child Health, London, United Kingdom.

Amy R Fairchild (AR)

UCL Great Ormond Street Institute of Child Health, London, United Kingdom.

Aimee Avery (A)

UCL Great Ormond Street Institute of Child Health, London, United Kingdom.

Jane Chalker (J)

UCL Great Ormond Street Institute of Child Health, London, United Kingdom.

Mark Kristiansen (M)

UCL Great Ormond Street Institute of Child Health, London, United Kingdom.

Kelly Haupfear (K)

Department of Neuropathology, St. Jude Children's Research Hospital, Memphis, Tennessee.

James D Dalton (JD)

Department of Neuropathology, St. Jude Children's Research Hospital, Memphis, Tennessee.

Wilda Orisme (W)

Department of Neuropathology, St. Jude Children's Research Hospital, Memphis, Tennessee.

Ji Wen (J)

Department of Neuropathology, St. Jude Children's Research Hospital, Memphis, Tennessee.

Michael Hubank (M)

Molecular Diagnostics, Royal Marsden Hospital NHS Trust, Sutton, United Kingdom.

Kathreena M Kurian (KM)

Brain Tumour Research Centre, University of Bristol, Bristol, United Kingdom.

Catherine Rowe (C)

Brain Tumour Research Centre, University of Bristol, Bristol, United Kingdom.

Mellissa Maybury (M)

The University of Queensland Diamantina Institute, The University of Queensland, Woolloongabba, Australia.
Oncology Service, Queensland Children's Hospital, Brisbane, Australia.
Child Health Research Centre, The University of Queensland, South Brisbane, Australia.

Stephen Crosier (S)

Newcastle Hospitals NHS Foundation Trust, Newcastle, United Kingdom.

Jeffrey Knipstein (J)

Division of Pediatric Hematology/Oncology/BMT, Medical College of Wisconsin, Milwaukee, Wisconsin.

Ulrich Schüller (U)

Department of Neuropathology, University Hospital Hamburg-Eppendorf, and Research Institute Children's Cancer Center, Hamburg, Germany.
Pediatric Hematology and Oncology, University Hospital Hamburg-Eppendorf, Hamburg, Germany.

Uwe Kordes (U)

Pediatric Hematology and Oncology, University Hospital Hamburg-Eppendorf, Hamburg, Germany.

David E Kram (DE)

Section of Pediatric Hematology-Oncology, Wake Forest School of Medicine, Winston-Salem, North Carolina.

Matija Snuderl (M)

Department of Neuropathology, NYU Langone Health, New York, New York.

Leslie Bridges (L)

Department of Neuropathology, St George's Hospital NHS Trust, London, United Kingdom.

Andrew J Martin (AJ)

Department of Neurosurgery, St George's Hospital NHS Trust, London, United Kingdom.

Lawrence J Doey (LJ)

Department of Clinical Neuropathology, Kings College Hospital NHS Trust, London, United Kingdom.

Safa Al-Sarraj (S)

Department of Clinical Neuropathology, Kings College Hospital NHS Trust, London, United Kingdom.

Christopher Chandler (C)

Department of Neurosurgery, Kings College Hospital NHS Trust, London, United Kingdom.

Bassel Zebian (B)

Department of Neurosurgery, Kings College Hospital NHS Trust, London, United Kingdom.

Claire Cairns (C)

Department of Neurosurgery, Kings College Hospital NHS Trust, London, United Kingdom.

Rachael Natrajan (R)

The Breast Cancer Now Toby Robins Research Centre, The Institute of Cancer Research, London, United Kingdom.

Jessica K R Boult (JKR)

Division of Radiotherapy and Imaging, The Institute of Cancer Research, London, United Kingdom.

Simon P Robinson (SP)

Division of Radiotherapy and Imaging, The Institute of Cancer Research, London, United Kingdom.

Martin Sill (M)

German Cancer Research Center (DKFZ), Heidelberg, Germany.

Ira J Dunkel (IJ)

Department of Pediatrics, Memorial Sloan-Kettering Cancer Center, New York, New York.

Stephen W Gilheeney (SW)

Department of Pediatrics, Memorial Sloan-Kettering Cancer Center, New York, New York.

Marc K Rosenblum (MK)

Department of Neuropathology, Memorial Sloan-Kettering Cancer Center, New York, New York.

Debbie Hughes (D)

Molecular Diagnostics, Royal Marsden Hospital NHS Trust, Sutton, United Kingdom.

Paula Z Proszek (PZ)

Molecular Diagnostics, Royal Marsden Hospital NHS Trust, Sutton, United Kingdom.

Tobey J Macdonald (TJ)

Aflac Cancer and Blood Disorders Center, Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia.

Matthias Preusser (M)

Comprehensive Cancer Center, Medical University of Vienna, Vienna, Austria.

Christine Haberler (C)

Comprehensive Cancer Center, Medical University of Vienna, Vienna, Austria.
Institute of Neurology, Medical University of Vienna, Vienna, Austria.

Irene Slavc (I)

Department of Pediatrics and Adolescent Medicine, Medical University of Vienna, Vienna, Austria.

Roger Packer (R)

Center for Neuroscience and Behavioural Medicine, Children's National Medical Center, Washington, DC.

Ho-Keung Ng (HK)

Department of Anatomical and Cellular Pathology, The Chinese University of Hong Kong, China.

Shani Caspi (S)

Cancer Research Center, Sheba Medical Center, Tel Aviv, Israel.

Mara Popović (M)

Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.

Barbara Faganel Kotnik (B)

Department of Hematology and Oncology, University Children's Hospital, Ljubljana, Slovenia.

Matthew D Wood (MD)

Department of Pathology, Oregon Health & Science University, Portland, Oregon.

Lissa Baird (L)

Department of Neurosurgery, Oregon Health & Science University, Portland, Oregon.

Monika Ashok Davare (MA)

Department of Pediatrics, Oregon Health & Science University, Portland, Oregon.

David A Solomon (DA)

Department of Pathology, University of California, San Francisco, California.
Clinical Cancer Genomics Laboratory, University of California, San Francisco, California.

Thale Kristin Olsen (TK)

Department of Women's and Children's Health, Karolinska Institute, Stockholm, Sweden.

Petter Brandal (P)

Department of Oncology, Oslo University Hospital, Oslo, Norway.

Michael Farrell (M)

Department of Histopathology, Beaumont Hospital, Dublin, Ireland.

Jane B Cryan (JB)

Department of Histopathology, Beaumont Hospital, Dublin, Ireland.

Michael Capra (M)

Paediatric Oncology, Our Lady's Children's Hospital, Dublin, Ireland.

Michael Karremann (M)

Department of Pediatrics, University Medical Center Mannheim, Medical Faculty Mannheim, Heidelberg University, Mannheim, Germany.

Jens Schittenhelm (J)

Institute of Pathology and Neuropathology, University Hospital Tübingen, Germany.

Martin U Schuhmann (MU)

Department of Neurosurgery, University Hospital Tübingen, Germany.

Martin Ebinger (M)

Department of Pediatric Hematology and Oncology, University Hospital Tübingen, Germany.

Winand N M Dinjens (WNM)

Department of Pathology, Erasmus Medical Center, Rotterdam, the Netherlands.

Kornelius Kerl (K)

Department of Pediatric Hematology and Oncology, University Hospital Muenster, Germany.

Simone Hettmer (S)

Department of Pediatric Hematology and Oncology, University Hospital Freiburg, Germany.

Torsten Pietsch (T)

Institute of Neuropathology, DGNN Brain Tumor Reference Center, University of Bonn Medical Center, Bonn, Germany.

Felipe Andreiuolo (F)

Institute of Neuropathology, DGNN Brain Tumor Reference Center, University of Bonn Medical Center, Bonn, Germany.

Pablo Hernáiz Driever (PH)

Department of Paediatric Haematology/Oncology Charité Universitätsmedizin, Berlin, Germany.

Andrey Korshunov (A)

Department of Neuropathology, University Hospital Heidelberg, Germany.

Lotte Hiddingh (L)

German Cancer Research Center (DKFZ), Heidelberg, Germany.

Barbara C Worst (BC)

German Cancer Research Center (DKFZ), Heidelberg, Germany.
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.
Department of Pediatric Oncology, Hematology, Immunology and Pulmonology, Heidelberg University Hospital, Heidelberg, Germany.

Dominik Sturm (D)

German Cancer Research Center (DKFZ), Heidelberg, Germany.
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.
Department of Pediatric Oncology, Hematology, Immunology and Pulmonology, Heidelberg University Hospital, Heidelberg, Germany.

Marc Zuckermann (M)

German Cancer Research Center (DKFZ), Heidelberg, Germany.
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.

Olaf Witt (O)

German Cancer Research Center (DKFZ), Heidelberg, Germany.
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.
Department of Pediatric Oncology, Hematology, Immunology and Pulmonology, Heidelberg University Hospital, Heidelberg, Germany.

Tabitha Bloom (T)

BRAIN UK, University of Southampton, Southampton, United Kingdom.

Clare Mitchell (C)

BRAIN UK, University of Southampton, Southampton, United Kingdom.

Evelina Miele (E)

Department of Onco-haematology, Cell and Gene Therapy, Bambino Gesù Children's Hospital-IRCCS, Rome, Italy.

Giovanna Stefania Colafati (GS)

Oncological Neuroradiology Unit, Department of Diagnostic Imaging, Bambino Gesù Children's Hospital-IRCCS, Rome, Italy.

Francesca Diomedi-Camassei (F)

Department of Laboratories - Pathology Unit, Bambino Gesù Children's Hospital-IRCCS, Rome, Italy.

Simon Bailey (S)

Newcastle Hospitals NHS Foundation Trust, Newcastle, United Kingdom.

Andrew S Moore (AS)

The University of Queensland Diamantina Institute, The University of Queensland, Woolloongabba, Australia.
Oncology Service, Queensland Children's Hospital, Brisbane, Australia.
Child Health Research Centre, The University of Queensland, South Brisbane, Australia.

Timothy E G Hassall (TEG)

Oncology Service, Queensland Children's Hospital, Brisbane, Australia.
Institute for Molecular Bioscience, The University of Queensland, St Lucia, Australia.
School of Biomedical Sciences, Faculty of Health, Queensland University of Technology, Brisbane, Australia.

Stephen P Lowis (SP)

Brain Tumour Research Centre, University of Bristol, Bristol, United Kingdom.

Maria Tsoli (M)

Children's Cancer Institute, University of New South Wales, Sydney, Australia.
Kids Cancer Centre, Sydney Children's Hospital, Randwick, Australia.

Mark J Cowley (MJ)

Children's Cancer Institute, University of New South Wales, Sydney, Australia.
Kids Cancer Centre, Sydney Children's Hospital, Randwick, Australia.

David S Ziegler (DS)

Children's Cancer Institute, University of New South Wales, Sydney, Australia.
Kids Cancer Centre, Sydney Children's Hospital, Randwick, Australia.

Matthias A Karajannis (MA)

Department of Pediatrics, Memorial Sloan-Kettering Cancer Center, New York, New York.

Kristian Aquilina (K)

Department of Neurosurgery, Great Ormond Street Hospital NHS Foundation Trust, London, United Kingdom.

Darren R Hargrave (DR)

Department of Paediatric Oncology, Great Ormond Street Hospital NHS Foundation Trust, London, United Kingdom.

Fernando Carceller (F)

Division of Clinical Studies, The Institute of Cancer Research, London, United Kingdom.
Children & Young People's Unit, Royal Marsden Hospital NHS Trust, Sutton, United Kingdom.

Lynley V Marshall (LV)

Division of Clinical Studies, The Institute of Cancer Research, London, United Kingdom.
Children & Young People's Unit, Royal Marsden Hospital NHS Trust, Sutton, United Kingdom.

Andreas von Deimling (A)

Department of Neuropathology, University Hospital Heidelberg, Germany.
Clinical Cooperation Unit Neuropathology, German Cancer Consortium (DKTK), German Cancer Research Center (DKFZ), Heidelberg, Germany.

Christof M Kramm (CM)

Division of Pediatric Hematology and Oncology, University Medical Centre Göttingen, Germany.

Stefan M Pfister (SM)

German Cancer Research Center (DKFZ), Heidelberg, Germany.
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.
Department of Pediatric Oncology, Hematology, Immunology and Pulmonology, Heidelberg University Hospital, Heidelberg, Germany.

Felix Sahm (F)

Department of Paediatric Haematology/Oncology Charité Universitätsmedizin, Berlin, Germany.
Clinical Cooperation Unit Neuropathology, German Cancer Consortium (DKTK), German Cancer Research Center (DKFZ), Heidelberg, Germany.

Suzanne J Baker (SJ)

Department of Neurobiology, St. Jude Children's Research Hospital, Memphis, Tennessee.

Angela Mastronuzzi (A)

Neuro-oncology Unit, Department of Onco-haematology, Cell and Gene Therapy, Bambino Gesù Children's Hospital-IRCCS, Rome, Italy.

Andrea Carai (A)

Oncological Neurosurgery Unit, Department of Neuroscience and Neurorehabilitation, Bambino Gesù Children's Hospital-IRCCS, Rome, Italy.

Maria Vinci (M)

Department of Onco-haematology, Cell and Gene Therapy, Bambino Gesù Children's Hospital-IRCCS, Rome, Italy.

David Capper (D)

Charité Universitätsmedizin Berlin, corporate member of Freie Universität Berlin, Humboldt-Universität zu Berlin, and Berlin Institute of Health, Department of Neuropathology, Berlin, Germany.
German Cancer Consortium (DKTK), Partner Site Berlin, German Cancer Research Center (DKFZ), Heidelberg, Germany.

Sergey Popov (S)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom.
Department of Pathology, University of Wales Hospital NHS Trust, Cardiff, United Kingdom.

David W Ellison (DW)

Department of Neuropathology, St. Jude Children's Research Hospital, Memphis, Tennessee. chris.jones@icr.ac.uk david.jones@kitz-heidelberg.de t.jacques@ucl.ac.uk david.ellison@stjude.org.

Thomas S Jacques (TS)

UCL Great Ormond Street Institute of Child Health, London, United Kingdom. chris.jones@icr.ac.uk david.jones@kitz-heidelberg.de t.jacques@ucl.ac.uk david.ellison@stjude.org.

David T W Jones (DTW)

German Cancer Research Center (DKFZ), Heidelberg, Germany. chris.jones@icr.ac.uk david.jones@kitz-heidelberg.de t.jacques@ucl.ac.uk david.ellison@stjude.org.
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.

Chris Jones (C)

Division of Molecular Pathology, Institute of Cancer Research, London, United Kingdom. chris.jones@icr.ac.uk david.jones@kitz-heidelberg.de t.jacques@ucl.ac.uk david.ellison@stjude.org.

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