Development of an
adeno-associated virus
biopotency
coagulation factor IX
gene therapy
Journal
Molecular therapy. Methods & clinical development
ISSN: 2329-0501
Titre abrégé: Mol Ther Methods Clin Dev
Pays: United States
ID NLM: 101624857
Informations de publication
Date de publication:
12 Jun 2020
12 Jun 2020
Historique:
received:
19
02
2020
accepted:
12
03
2020
entrez:
14
4
2020
pubmed:
14
4
2020
medline:
14
4
2020
Statut:
epublish
Résumé
Gene therapy product release requires reliable and consistent demonstration of biopotency. In hemophilia B vectors, this is usually determined
Identifiants
pubmed: 32280725
doi: 10.1016/j.omtm.2020.03.013
pii: S2329-0501(20)30043-7
pmc: PMC7139127
doi:
Types de publication
Journal Article
Langues
eng
Pagination
581-588Informations de copyright
© 2020 Shire International GmbH, now part of Takeda, Zurich, Switzerland.
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