Complement Receptor Targeted Liposomes Encapsulating the Liver X Receptor Agonist GW3965 Accumulate in and Stabilize Atherosclerotic Plaques.


Journal

Advanced healthcare materials
ISSN: 2192-2659
Titre abrégé: Adv Healthc Mater
Pays: Germany
ID NLM: 101581613

Informations de publication

Date de publication:
05 2020
Historique:
received: 08 01 2020
revised: 20 02 2020
pubmed: 25 4 2020
medline: 15 5 2021
entrez: 25 4 2020
Statut: ppublish

Résumé

Atherosclerosis is characterized by the retention of lipids in foam cells in the arterial intima. The liver X receptor (LXR) agonist GW3965 is a promising therapeutic compound, since it induces reverse cholesterol transport in foam cells. However, hepatic LXR activation increases plasma and liver lipid levels, inhibiting its clinical development. Herein, a formulation that specifically enhances GW3965 deposition in the atherosclerotic lesion is aimed to be developed. GW3965 is encapsulated in liposomes functionalized with the cyclic peptide Lyp-1 (CGNKRTRGC), which binds the p32 receptor expressed on foam cells. These liposomes show preferential uptake by foam cells in vitro and higher accumulation in atherosclerotic plaques in mice compared to non-targeted liposomes as determined by in vivo imaging. Flow cytometry analysis of plaques reveals increased retention of Lyp-1 liposomes in atherosclerotic plaque macrophages compared to controls (p < 0.05). Long term treatment of established plaques in LDLR -/- mice with GW3965-containing Lyp-1 liposomes significantly reduces plaque macrophage content by 50% (p < 0.01). Importantly, GW3965-containing Lyp-1 liposomes do not increase plasma or hepatic lipid content. Thus, GW3965-containing Lyp-1 liposomes successfully target the atherosclerotic macrophages allowing plaque stabilization without commonly observed side effects of LXR agonists.

Identifiants

pubmed: 32329226
doi: 10.1002/adhm.202000043
doi:

Substances chimiques

Benzoates 0
Benzylamines 0
GW 3965 0
Liposomes 0
Liver X Receptors 0
Receptors, Complement 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

e2000043

Informations de copyright

© 2020 The Authors. Published by WILEY-VCH Verlag GmbH & Co. KGaA, Weinheim.

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Auteurs

Naomi Benne (N)

Division BioTherapeutics, Leiden Academic Centre for Drug Research, Leiden University, Leiden, 2333CC, The Netherlands.

Renata Martins Cardoso (R)

Division BioTherapeutics, Leiden Academic Centre for Drug Research, Leiden University, Leiden, 2333CC, The Netherlands.

Aimee L Boyle (AL)

Department of Supramolecular and Biomaterials Chemistry, Leiden Institute of Chemistry, Leiden University, Leiden, 2333CC, The Netherlands.

Alexander Kros (A)

Department of Supramolecular and Biomaterials Chemistry, Leiden Institute of Chemistry, Leiden University, Leiden, 2333CC, The Netherlands.

Wim Jiskoot (W)

Division BioTherapeutics, Leiden Academic Centre for Drug Research, Leiden University, Leiden, 2333CC, The Netherlands.

Johan Kuiper (J)

Division BioTherapeutics, Leiden Academic Centre for Drug Research, Leiden University, Leiden, 2333CC, The Netherlands.

Joke Bouwstra (J)

Division BioTherapeutics, Leiden Academic Centre for Drug Research, Leiden University, Leiden, 2333CC, The Netherlands.

Miranda Van Eck (M)

Division BioTherapeutics, Leiden Academic Centre for Drug Research, Leiden University, Leiden, 2333CC, The Netherlands.

Bram Slütter (B)

Division BioTherapeutics, Leiden Academic Centre for Drug Research, Leiden University, Leiden, 2333CC, The Netherlands.

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