Modeling Hypoxia-Induced Neuropathies Using a Fast and Scalable Human Motor Neuron Differentiation System.


Journal

Stem cell reports
ISSN: 2213-6711
Titre abrégé: Stem Cell Reports
Pays: United States
ID NLM: 101611300

Informations de publication

Date de publication:
09 06 2020
Historique:
received: 21 10 2019
revised: 07 04 2020
accepted: 08 04 2020
pubmed: 11 5 2020
medline: 20 4 2021
entrez: 11 5 2020
Statut: ppublish

Résumé

Human motor neuron (MN) diseases encompass a spectrum of disorders. A critical barrier to dissecting disease mechanisms is the lack of appropriate human MN models. Here, we describe a scalable, suspension-based differentiation system to generate functional human MN diseases in 3 weeks. Using this model, we translated recent findings that mRNA mis-localization plays a role in disease development to the human context by establishing a membrane-based system that allows efficient fractionation of MN cell soma and neurites. In response to hypoxia, used to mimic diabetic neuropathies, MNs upregulated mitochondrial transcripts in neurites; however, mitochondria were decreased. These data suggest that hypoxia may disrupt translation of mitochondrial mRNA, potentially leading to neurite damage and development of neuropathies. We report the development of a novel human MN model system to investigate mechanisms of disease affecting soma and/or neurites that facilitates the rapid generation and testing of patient-specific MN diseases.

Identifiants

pubmed: 32386561
pii: S2213-6711(20)30143-0
doi: 10.1016/j.stemcr.2020.04.003
pmc: PMC7355142
pii:
doi:

Substances chimiques

Mitochondrial Proteins 0
RNA, Messenger 0
Oxygen S88TT14065

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1033-1043

Subventions

Organisme : NIGMS NIH HHS
ID : R35 GM133385
Pays : United States
Organisme : NIDDK NIH HHS
ID : K12 DK094712
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK120444
Pays : United States
Organisme : NIAID NIH HHS
ID : R21 AI140044
Pays : United States
Organisme : NIDDK NIH HHS
ID : F32 DK118803
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR002535
Pays : United States

Commentaires et corrections

Type : ErratumIn

Informations de copyright

Copyright © 2020 The Authors. Published by Elsevier Inc. All rights reserved.

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Auteurs

Laura I Hudish (LI)

Barbara Davis Center for Diabetes, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

Andrew Bubak (A)

Department of Neurology, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

Taylor M Triolo (TM)

Barbara Davis Center for Diabetes, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

Christy S Niemeyer (CS)

Department of Neurology, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

David S Lorberbaum (DS)

Barbara Davis Center for Diabetes, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

Lori Sussel (L)

Barbara Davis Center for Diabetes, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

Maria Nagel (M)

Department of Neurology, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

J Matthew Taliaferro (JM)

Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA; RNA Bioscience Initiative, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA.

Holger A Russ (HA)

Barbara Davis Center for Diabetes, University of Colorado Anschutz Medical Campus, Aurora, CO 80045, USA. Electronic address: holger.russ@cuanschutz.edu.

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Classifications MeSH