Not Described Variant of Notch3 Gen for Cadasil Disease.


Journal

Journal of stroke and cerebrovascular diseases : the official journal of National Stroke Association
ISSN: 1532-8511
Titre abrégé: J Stroke Cerebrovasc Dis
Pays: United States
ID NLM: 9111633

Informations de publication

Date de publication:
Jul 2020
Historique:
received: 24 08 2019
revised: 09 02 2020
accepted: 02 03 2020
pubmed: 11 5 2020
medline: 6 10 2020
entrez: 11 5 2020
Statut: ppublish

Résumé

Autosomal dominant cerebral arteriopathy with subcortical infarctions and leukoencephalopathy (CADASIL), is a genetic disease caused by mutations in the Notch3 gene. More than 170 monogenic mutations leading to the development of CADASIL have been reported. We describe a case of a patient and her family with compatible symptoms of CADASIL disease, in which a variable not yet described in the Notch3 gene was detected, that generates a probably pathogenic change in the protein.

Identifiants

pubmed: 32387185
pii: S1052-3057(20)30187-7
doi: 10.1016/j.jstrokecerebrovasdis.2020.104803
pii:
doi:

Substances chimiques

NOTCH3 protein, human 0
Receptor, Notch3 0

Types de publication

Case Reports

Langues

eng

Sous-ensembles de citation

IM

Pagination

104803

Informations de copyright

Copyright © 2020 Elsevier Inc. All rights reserved.

Auteurs

Surai Mellinger (S)

Neurology Service, Hospital Señor del Milagro, Salta Capital, Argentina. Electronic address: suri_mellinger@hotmail.com.

D Romero (D)

Neurosurgery Service, Hospital San Bernardo, Salta Capital, Argentina.

A Visich (A)

Biogen Foundation, Salta Capital, Argentina.

S Chanampa (S)

Neurology Service, Hospital San Bernardo, Salta Capital, Argentina.

G Ivetich (G)

Neurology Service, Hospital San Bernardo, Salta Capital, Argentina.

M Burgos (M)

Neurology Service, Hospital San Bernardo, Salta Capital, Argentina.

G Orzuza (G)

Neurology Service, Hospital San Bernardo, Salta Capital, Argentina.

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Classifications MeSH