Two cases of a non-progressive hepatic form of glycogen storage disease type IV with atypical liver pathology.

ALT, alanine aminotransferase AST, aspartate transaminase Andersen disease COI, cut-off index GBE, glycogen-branching enzyme GBE1 GSD IV GSD IV, Glycogen storage disease type IV M2BPGi M2BPGi, Mac-2 binding protein glycosylation isomer Nutrition therapy PAS, periodic acid-Schiff PAS-D, periodic acid-Schiff-diastase SD, standard deviation γ-GTP, gamma-glutamyltransferase

Journal

Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422

Informations de publication

Date de publication:
Sep 2020
Historique:
received: 21 03 2020
revised: 02 05 2020
accepted: 02 05 2020
entrez: 27 5 2020
pubmed: 27 5 2020
medline: 27 5 2020
Statut: epublish

Résumé

Glycogen storage disease type IV (GSD IV) is a rare inborn metabolic disorder characterized by the accumulation of amylopectin-like glycogen in the liver or other organs. The hepatic subtype may appear normal at birth but rapidly develops to liver cirrhosis in infancy. Liver pathological findings help diagnose the hepatic form of the disease, supported by analyses of enzyme activity and

Identifiants

pubmed: 32455116
doi: 10.1016/j.ymgmr.2020.100601
pii: S2214-4269(20)30047-1
pii: 100601
pmc: PMC7235638
doi:

Types de publication

Case Reports

Langues

eng

Pagination

100601

Informations de copyright

© 2020 The Authors.

Déclaration de conflit d'intérêts

All the authors declare that they have no conflicts of interest to disclose.

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Auteurs

Keiko Ichimoto (K)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Tomoo Fujisawa (T)

Department of Pediatric Hepatology and Gastroenterology, Saiseikai Yokohama-shi Tobu Hospital, 3-6-1 Shimosueyoshi, Tsurumi-ku, Yokohama 230-8765, Japan.

Masaru Shimura (M)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Takuya Fushimi (T)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Makiko Tajika (M)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Ayako Matsunaga (A)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Minako Ogawa-Tominaga (M)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Nana Akiyama (N)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Yuki Naruke (Y)

Department of Pathology, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Hiroshi Horie (H)

Department of Pathology, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Tokiko Fukuda (T)

Department of Pediatrics, Hamamatsu University School of Medicine, 1-20-1 Handayama, Higashi-ku, Hamamatsu 431-3192, Japan.

Hideo Sugie (H)

Faculty of Health and Medical Sciences, Tokoha University, 1230 Miyakodachou, Kita-ku, Hamamatsu 431-2102, Japan.

Ayano Inui (A)

Department of Pediatric Hepatology and Gastroenterology, Saiseikai Yokohama-shi Tobu Hospital, 3-6-1 Shimosueyoshi, Tsurumi-ku, Yokohama 230-8765, Japan.

Kei Murayama (K)

Center for Medical Genetics, Department of Metabolism, Chiba Children's Hospital, 579-1 Heta-cho, Midori-ku, Chiba 266-0007, Japan.

Classifications MeSH