Significance of NT-proBNP and High-sensitivity Troponin in Friedreich Ataxia.

Friedreich ataxia NT-proBNP cardiomyopathy hs troponin

Journal

Journal of clinical medicine
ISSN: 2077-0383
Titre abrégé: J Clin Med
Pays: Switzerland
ID NLM: 101606588

Informations de publication

Date de publication:
28 May 2020
Historique:
received: 29 04 2020
revised: 22 05 2020
accepted: 22 05 2020
entrez: 3 6 2020
pubmed: 3 6 2020
medline: 3 6 2020
Statut: epublish

Résumé

Friedreich's ataxia (FA) is a rare autosomal recessive mitochondrial disease resulting of a triplet repeat expansion guanine-adenine-adenine (GAA) in the frataxin (FXN) gene, exhibiting progressive cerebellar ataxia, diabetes and cardiomyopathy. We aimed to determine the relationship between cardiac biomarkers, serum N-terminal pro-brain natriuretic peptide (NT-proBNP), and serum cardiac high-sensitivity troponin (hsTnT) concentrations, and the extent of genetic abnormality and cardiac parameters. Between 2013 and 2015, 85 consecutive genetically confirmed FA adult patients were prospectively evaluated by measuring plasma hsTnT and NT-proBNP concentrations, electrocardiogram, and echocardiography. The 85 FA patients (49% women) with a mean age of 39 ± 12 years, a mean disease onset of 17 ± 11 years had a mean SARA (Scale for the Assessment and Rating of Ataxia) score of 26 ± 10. The median hsTnT concentration was 10 ng/L (3 to 85 ng/L) and 34% had a significant elevated hsTnT ≥ 14 ng/L. Increased septal wall thickness was associated with increased hsTnT plasma levels ( hsTnT was increased in 1/3 of the adult FA and associated with increased septal wall thickness. Increased NT-proBNP remained a marker of increased left ventricular filling pressure. This could be used to identify patients that should undergo a closer cardiac surveillance.

Sections du résumé

BACKGROUND BACKGROUND
Friedreich's ataxia (FA) is a rare autosomal recessive mitochondrial disease resulting of a triplet repeat expansion guanine-adenine-adenine (GAA) in the frataxin (FXN) gene, exhibiting progressive cerebellar ataxia, diabetes and cardiomyopathy. We aimed to determine the relationship between cardiac biomarkers, serum N-terminal pro-brain natriuretic peptide (NT-proBNP), and serum cardiac high-sensitivity troponin (hsTnT) concentrations, and the extent of genetic abnormality and cardiac parameters.
METHODS METHODS
Between 2013 and 2015, 85 consecutive genetically confirmed FA adult patients were prospectively evaluated by measuring plasma hsTnT and NT-proBNP concentrations, electrocardiogram, and echocardiography.
RESULTS RESULTS
The 85 FA patients (49% women) with a mean age of 39 ± 12 years, a mean disease onset of 17 ± 11 years had a mean SARA (Scale for the Assessment and Rating of Ataxia) score of 26 ± 10. The median hsTnT concentration was 10 ng/L (3 to 85 ng/L) and 34% had a significant elevated hsTnT ≥ 14 ng/L. Increased septal wall thickness was associated with increased hsTnT plasma levels (
CONCLUSION CONCLUSIONS
hsTnT was increased in 1/3 of the adult FA and associated with increased septal wall thickness. Increased NT-proBNP remained a marker of increased left ventricular filling pressure. This could be used to identify patients that should undergo a closer cardiac surveillance.

Identifiants

pubmed: 32481586
pii: jcm9061630
doi: 10.3390/jcm9061630
pmc: PMC7356582
pii:
doi:

Types de publication

Journal Article

Langues

eng

Subventions

Organisme : Seventh Framework Programme
ID : HEALTH-F22010-242193

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Auteurs

Lise Legrand (L)

Cardiology Department, AP-HP, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.
ICAN (Institute for Cardiometabolism and Nutrition), Pitié-Salpêtrière University Hospital, 75651 Paris, France.
ACTION (Allies in Cardiovascular Trials Initiatives and Organized Networks) Group, URC Lariboisière University Hospital, 75475 Paris, France.

Carole Maupain (C)

Cardiology Department, AP-HP, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.
ICAN (Institute for Cardiometabolism and Nutrition), Pitié-Salpêtrière University Hospital, 75651 Paris, France.
ACTION (Allies in Cardiovascular Trials Initiatives and Organized Networks) Group, URC Lariboisière University Hospital, 75475 Paris, France.

Marie-Lorraine Monin (ML)

Institut du Cerveau et de la Moelle épinière (ICM), AP-HP, INSERM, CNRS, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.

Claire Ewenczyk (C)

Institut du Cerveau et de la Moelle épinière (ICM), AP-HP, INSERM, CNRS, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.

Richard Isnard (R)

Cardiology Department, AP-HP, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.
ICAN (Institute for Cardiometabolism and Nutrition), Pitié-Salpêtrière University Hospital, 75651 Paris, France.
ACTION (Allies in Cardiovascular Trials Initiatives and Organized Networks) Group, URC Lariboisière University Hospital, 75475 Paris, France.

Rana Alkouri (R)

Metabolic Biochemistry Department, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.

Alexandra Durr (A)

Institut du Cerveau et de la Moelle épinière (ICM), AP-HP, INSERM, CNRS, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.

Francoise Pousset (F)

Cardiology Department, AP-HP, Sorbonne Université, Pitié-Salpêtrière University Hospital, 75013 Paris, France.
ICAN (Institute for Cardiometabolism and Nutrition), Pitié-Salpêtrière University Hospital, 75651 Paris, France.
ACTION (Allies in Cardiovascular Trials Initiatives and Organized Networks) Group, URC Lariboisière University Hospital, 75475 Paris, France.

Classifications MeSH