Testis formation in XX individuals resulting from novel pathogenic variants in Wilms' tumor 1 (


Journal

Proceedings of the National Academy of Sciences of the United States of America
ISSN: 1091-6490
Titre abrégé: Proc Natl Acad Sci U S A
Pays: United States
ID NLM: 7505876

Informations de publication

Date de publication:
16 06 2020
Historique:
pubmed: 5 6 2020
medline: 15 9 2020
entrez: 5 6 2020
Statut: ppublish

Résumé

Sex determination in mammals is governed by antagonistic interactions of two genetic pathways, imbalance in which may lead to disorders/differences of sex development (DSD) in human. Among 46,XX individuals with testicular DSD (TDSD) or ovotesticular DSD (OTDSD), testicular tissue is present in the gonad. Although the testis-determining gene

Identifiants

pubmed: 32493750
pii: 1921676117
doi: 10.1073/pnas.1921676117
pmc: PMC7306989
doi:

Substances chimiques

WT1 Proteins 0
WT1 protein, human 0
WT1 protein, mouse 0
beta Catenin 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

13680-13688

Subventions

Organisme : Cancer Research UK
ID : FC001107
Pays : United Kingdom
Organisme : Wellcome Trust
ID : FC001107
Pays : United Kingdom
Organisme : NICHD NIH HHS
ID : R21 HD074278
Pays : United States
Organisme : NICHD NIH HHS
ID : R01 HD070647
Pays : United States
Organisme : NIGMS NIH HHS
ID : R01 GM116889
Pays : United States
Organisme : Wellcome Trust
Pays : United Kingdom
Organisme : Medical Research Council
ID : U117512772
Pays : United Kingdom
Organisme : Medical Research Council
ID : FC001107
Pays : United Kingdom

Informations de copyright

Copyright © 2020 the Author(s). Published by PNAS.

Déclaration de conflit d'intérêts

The authors declare no competing interest.

Références

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Auteurs

Caroline Eozenou (C)

Human Developmental Genetics Unit, Institut Pasteur, 75724 Paris, France.

Nitzan Gonen (N)

Laboratory of Stem Cell Biology and Developmental Genetics, The Francis Crick Institute, NW1 1AT London, United Kingdom.
The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, 5290002 Ramat Gan, Israel.

Maria Sol Touzon (MS)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Anne Jorgensen (A)

Department of Growth and Reproduction, Copenhagen University Hospital (Rigshospitalet), 2100 Copenhagen, Denmark.

Svetlana A Yatsenko (SA)

Department of Obstetrics, Gynecology & Reproductive Sciences, Magee-Womens Research Institute, University of Pittsburgh, Pittsburgh, PA 15213.
Department of Pathology, Magee-Womens Research Institute, University of Pittsburgh, Pittsburgh, PA 15213.
Department of Human Genetics, Magee-Womens Research Institute, University of Pittsburgh, Pittsburgh, PA 15213.

Leila Fusee (L)

Human Developmental Genetics Unit, Institut Pasteur, 75724 Paris, France.

Alaa K Kamel (AK)

Division of Human Genetics and Genome Research, National Research Centre, Dokki, Cairo, 12622, Egypt.

Balazs Gellen (B)

Department of Paediatrics, University of Szeged, 6725 Szeged, Hungary.

Gabriela Guercio (G)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Priti Singh (P)

Department of Biomedical Sciences, Cornell University, Ithaca, NY 14853.

Selma Witchel (S)

Department of Pediatrics, University of Pittsburgh Medical Center, Children's Hospital of Pittsburgh, University of Pittsburgh, Pittsburgh, PA 15213.

Andrea J Berman (AJ)

Department of Biological Sciences, University of Pittsburgh, Pittsburgh, PA 15213.

Rana Mainpal (R)

Department of Obstetrics, Gynecology & Reproductive Sciences, Magee-Womens Research Institute, University of Pittsburgh, Pittsburgh, PA 15213.

Mehdi Totonchi (M)

Department of Genetics, Reproductive Biomedicine Research Center, Royan Institute for Reproductive Biomedicine, Academic Center for Education, Culture and Research, 8158968433 Tehran, Iran.
Department of Stem Cells and Developmental Biology, Cell Science Research Center, Royan Institute for Stem Cell Biology and Technology, Academic Center for Education, Culture and Research, 8158968433 Tehran, Iran.

Anahita Mohseni Meybodi (A)

Department of Genetics, Reproductive Biomedicine Research Center, Royan Institute for Reproductive Biomedicine, Academic Center for Education, Culture and Research, 8158968433 Tehran, Iran.

Masomeh Askari (M)

Department of Genetics, Reproductive Biomedicine Research Center, Royan Institute for Reproductive Biomedicine, Academic Center for Education, Culture and Research, 8158968433 Tehran, Iran.

Tiphanie Merel-Chali (T)

Human Developmental Genetics Unit, Institut Pasteur, 75724 Paris, France.

Joelle Bignon-Topalovic (J)

Human Developmental Genetics Unit, Institut Pasteur, 75724 Paris, France.

Roberta Migale (R)

Laboratory of Stem Cell Biology and Developmental Genetics, The Francis Crick Institute, NW1 1AT London, United Kingdom.

Mariana Costanzo (M)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Roxana Marino (R)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Pablo Ramirez (P)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Natalia Perez Garrido (N)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Esperanza Berensztein (E)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Mona K Mekkawy (MK)

Division of Human Genetics and Genome Research, National Research Centre, Dokki, Cairo, 12622, Egypt.

John C Schimenti (JC)

Department of Biomedical Sciences, Cornell University, Ithaca, NY 14853.

Rita Bertalan (R)

1st Department of Pediatrics, Semmelweis University, 1083 Budapest, Hungary.

Inas Mazen (I)

Division of Human Genetics and Genome Research, National Research Centre, Dokki, Cairo, 12622, Egypt.

Ken McElreavey (K)

Human Developmental Genetics Unit, Institut Pasteur, 75724 Paris, France.

Alicia Belgorosky (A)

Endocrinology Department, Research Unit Garrahan Consejo Nacional de Investigaciones Cientificas y Tecnologicas, Hospital de Pediatría Garrahan, Ciudad Autonoma de Buenos Aires 1245, Argentina.

Robin Lovell-Badge (R)

Laboratory of Stem Cell Biology and Developmental Genetics, The Francis Crick Institute, NW1 1AT London, United Kingdom.

Aleksandar Rajkovic (A)

Department of Pathology, Obstetrics, Gynecology and Reproductive Sciences, University of California, San Francisco, CA 94158.

Anu Bashamboo (A)

Human Developmental Genetics Unit, Institut Pasteur, 75724 Paris, France; anu.bashamboo@pasteur.fr.

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