Chance or challenge, spoilt for choice? New recommendations on diagnostic and therapeutic considerations in hereditary transthyretin amyloidosis with polyneuropathy: the German/Austrian position and review of the literature.

Diagnostic intervals Follow-up monitoring Gene-silencing therapies Pre-symptomatic carriers TTR amyloidosis TTR stabilizers

Journal

Journal of neurology
ISSN: 1432-1459
Titre abrégé: J Neurol
Pays: Germany
ID NLM: 0423161

Informations de publication

Date de publication:
Oct 2021
Historique:
received: 07 05 2020
accepted: 29 05 2020
revised: 27 05 2020
pubmed: 6 6 2020
medline: 29 9 2021
entrez: 6 6 2020
Statut: ppublish

Résumé

Hereditary transthyretin amyloidosis is caused by pathogenic variants (ATTR

Identifiants

pubmed: 32500375
doi: 10.1007/s00415-020-09962-6
pii: 10.1007/s00415-020-09962-6
pmc: PMC8463516
doi:

Substances chimiques

Prealbumin 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

3610-3625

Informations de copyright

© 2020. The Author(s).

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Auteurs

Maike F Dohrn (MF)

Neuromuscular Outpatient Clinic, Department of Neurology, Medical Faculty, RWTH Aachen University, Aachen, Germany. mdohrn@ukaachen.de.

Michaela Auer-Grumbach (M)

Department of Orthopedics and Trauma Surgery, Medical University of Vienna, Vienna, Austria.

Ralf Baron (R)

Division of Neurological Pain Research and Therapy, Department of Neurology, University Hospital Schleswig-Holstein, Campus Kiel, Kiel, Germany.

Frank Birklein (F)

Department of Neurology, University Medical Center of the Johannes Gutenberg University, Mainz, Germany.

Fabiola Escolano-Lozano (F)

Department of Neurology, University Medical Center of the Johannes Gutenberg University, Mainz, Germany.

Christian Geber (C)

Department of Neurology, Red Cross Pain Centre Mainz, Mainz, Germany.

Nicolai Grether (N)

Department of Neurology, Faculty of Medicine and University Hospital Cologne, Cologne, Germany.

Tim Hagenacker (T)

Department of Neurology, University Hospital Essen, Essen, Germany.

Ernst Hund (E)

Amyloidosis Center Heidelberg, Heidelberg University Hospital, Heidelberg, Germany.
Department of Neurology, Heidelberg University Hospital, Heidelberg, Germany.

Juliane Sachau (J)

Division of Neurological Pain Research and Therapy, Department of Neurology, University Hospital Schleswig-Holstein, Campus Kiel, Kiel, Germany.

Matthias Schilling (M)

Department of Neurology with Institute of Translational Neurology, University Hospital of Muenster, Münster, Germany.

Jens Schmidt (J)

Department of Neurology, University Medical Center Göttingen, Göttingen, Germany.

Wilhelm Schulte-Mattler (W)

Department of Psychiatry and Psychotherapy, University Hospital Regensburg, Regensburg, Germany.

Claudia Sommer (C)

Department of Neurology, University of Würzburg, Würzburg, Germany.

Markus Weiler (M)

Amyloidosis Center Heidelberg, Heidelberg University Hospital, Heidelberg, Germany.
Department of Neurology, Heidelberg University Hospital, Heidelberg, Germany.

Gilbert Wunderlich (G)

Department of Neurology, Faculty of Medicine and University Hospital Cologne, Cologne, Germany.
Center for Rare Diseases, Faculty of Medicine and University Hospital of Cologne, Cologne, Germany.

Katrin Hahn (K)

Department of Neurology, Charité University Medicine, Berlin, Germany.

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Classifications MeSH