Point-Of-Care CAR T-Cell Production (ARI-0001) Using a Closed Semi-automatic Bioreactor: Experience From an Academic Phase I Clinical Trial.


Journal

Frontiers in immunology
ISSN: 1664-3224
Titre abrégé: Front Immunol
Pays: Switzerland
ID NLM: 101560960

Informations de publication

Date de publication:
2020
Historique:
received: 27 09 2019
accepted: 02 03 2020
entrez: 13 6 2020
pubmed: 13 6 2020
medline: 30 3 2021
Statut: epublish

Résumé

Development of semi-automated devices that can reduce the hands-on time and standardize the production of clinical-grade CAR T-cells, such as CliniMACS Prodigy from Miltenyi, is key to facilitate the development of CAR T-cell therapies, especially in academic institutions. However, the feasibility of manufacturing CAR T-cell products from heavily pre-treated patients with this system has not been demonstrated yet. Here we report and characterize the production of 28 CAR T-cell products in the context of a phase I clinical trial for CD19+ B-cell malignancies (NCT03144583). The system includes CD4-CD8 cell selection, lentiviral transduction and T-cell expansion using IL-7/IL-15. Twenty-seven out of 28 CAR T-cell products manufactured met the full list of specifications and were considered valid products.

Identifiants

pubmed: 32528460
doi: 10.3389/fimmu.2020.00482
pmc: PMC7259426
doi:

Banques de données

ClinicalTrials.gov
['NCT03144583']

Types de publication

Clinical Trial, Phase I Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

482

Informations de copyright

Copyright © 2020 Castella, Caballero-Baños, Ortiz-Maldonado, González-Navarro, Suñé, Antoñana-Vidósola, Boronat, Marzal, Millán, Martín-Antonio, Cid, Lozano, García, Tabera, Trias, Perpiña, Canals, Baumann, Benítez-Ribas, Campo, Yagüe, Urbano-Ispizua, Rives, Delgado and Juan.

Références

Cancer Immunol Res. 2017 Jul;5(7):571-581
pubmed: 28550091
J Clin Invest. 2015 Sep;125(9):3392-400
pubmed: 26325036
Blood. 1997 May 15;89(10):3700-7
pubmed: 9160675
Gastroenterology. 2018 Jul;155(1):29-32
pubmed: 29567081
Blood. 2016 Sep 29;128(13):1688-700
pubmed: 27412889
Mol Ther. 2010 Apr;18(4):843-51
pubmed: 20179677
Immunity. 2016 Feb 16;44(2):380-90
pubmed: 26885860
Clin Cancer Res. 2015 Jul 15;21(14):3149-59
pubmed: 25850950
Sci Transl Med. 2015 Sep 2;7(303):303ra139
pubmed: 26333935
Clin Cancer Res. 2006 Oct 15;12(20 Pt 1):6106-15
pubmed: 17062687
Cytotherapy. 2016 Aug;18(8):1002-1011
pubmed: 27378344
Blood. 2013 Dec 12;122(25):4129-39
pubmed: 24055823
Eur J Immunol. 2010 Jul;40(7):1938-49
pubmed: 20432236
N Engl J Med. 2011 Aug 25;365(8):725-33
pubmed: 21830940
N Engl J Med. 2016 Dec 29;375(26):2561-9
pubmed: 28029927
Blood. 2016 Mar 3;127(9):1117-27
pubmed: 26813675
Front Immunol. 2018 Dec 03;9:2740
pubmed: 30559740
Blood. 1994 Oct 1;84(7):2221-8
pubmed: 7919339
Front Immunol. 2018 Jul 27;9:1740
pubmed: 30140266
Transfus Med Hemother. 2019 Feb;46(1):47-54
pubmed: 31244581
N Engl J Med. 2014 Oct 16;371(16):1507-17
pubmed: 25317870
Lancet. 2015 Feb 7;385(9967):517-528
pubmed: 25319501
J Clin Invest. 2017 Sep 1;127(9):3462-3471
pubmed: 28805662
Leukemia. 2016 Feb;30(2):492-500
pubmed: 26369987
Clin Cancer Res. 2017 Mar 1;23(5):1156-1166
pubmed: 27582488
Immunol Rev. 2014 Jan;257(1):127-44
pubmed: 24329794
Leukemia. 2010 Jun;24(6):1160-70
pubmed: 20428207
Trends Mol Med. 2017 May;23(5):430-450
pubmed: 28416139
Blood. 2011 Nov 3;118(18):4817-28
pubmed: 21849486
Drug Des Devel Ther. 2018 Oct 05;12:3343-3356
pubmed: 30323566
Cell Rep. 2017 Dec 12;21(11):3205-3219
pubmed: 29241547
Blood. 2011 Jan 20;117(3):808-14
pubmed: 20971955
J Natl Cancer Inst. 2016 Jan 27;108(7):
pubmed: 26819347
Nat Med. 2018 Jan;24(1):20-28
pubmed: 29155426
J Clin Oncol. 2015 Feb 20;33(6):540-9
pubmed: 25154820
Immunol Rev. 2015 Jan;263(1):68-89
pubmed: 25510272
J Clin Invest. 2008 Jan;118(1):294-305
pubmed: 18060041
Hum Gene Ther. 2016 Oct;27(10):860-869
pubmed: 27562135
Mol Ther. 2013 Apr;21(4):904-12
pubmed: 23423337
Mol Ther Methods Clin Dev. 2018 Dec 06;12:134-144
pubmed: 30623002
Mol Ther Oncolytics. 2016 Jun 15;3:16015
pubmed: 27347557
Cancer Immunol Immunother. 2012 Aug;61(8):1269-77
pubmed: 22274776
J Clin Oncol. 2018 Aug 1;36(22):2267-2280
pubmed: 29812997
Annu Rev Med. 2014;65:333-47
pubmed: 24274181
Nat Med. 2011 Sep 18;17(10):1290-7
pubmed: 21926977
Front Immunol. 2019 Feb 01;10:38
pubmed: 30778344
Sci Transl Med. 2017 Jul 19;9(399):
pubmed: 28724573
Cell Rep. 2017 Oct 3;21(1):17-26
pubmed: 28978471
J Immunother. 2009 Feb-Mar;32(2):169-80
pubmed: 19238016
Cancer Immunol Immunother. 2018 Jul;67(7):1053-1066
pubmed: 29605883
J Clin Oncol. 2015 May 20;33(15):1688-96
pubmed: 25800760
Blood. 2016 Jun 16;127(24):2980-90
pubmed: 27118452
J Exp Med. 1996 Jan 1;183(1):249-59
pubmed: 8551228
Cancer Immunol Immunother. 2017 Nov;66(11):1425-1436
pubmed: 28660319
J Clin Oncol. 2006 May 1;24(13):e20-2
pubmed: 16648493
Blood. 2010 Nov 18;116(20):4099-102
pubmed: 20668228
Cytometry A. 2014 Jan;85(1):25-35
pubmed: 24124072
J Hematol Oncol. 2018 Dec 20;11(1):141
pubmed: 30572922

Auteurs

Maria Castella (M)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.
Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Blood and Tissue Bank (BST), Barcelona, Spain.

Miguel Caballero-Baños (M)

Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.
Hospital Sant Joan de Déu, Barcelona, Spain.

Valentín Ortiz-Maldonado (V)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.

Europa Azucena González-Navarro (EA)

Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.

Guillermo Suñé (G)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.
Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.

Asier Antoñana-Vidósola (A)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.
Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.

Anna Boronat (A)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.

Berta Marzal (B)

Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.

Lucía Millán (L)

Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.

Beatriz Martín-Antonio (B)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.
Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.

Joan Cid (J)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Department of Hemotherapy and Hemostasis, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.

Miquel Lozano (M)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Department of Hemotherapy and Hemostasis, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.

Enric García (E)

Blood and Tissue Bank (BST), Barcelona, Spain.
Apheresis Unit, Hospital Sant Joan de Déu de Barcelona, Barcelona, Spain.

Jaime Tabera (J)

Blood and Tissue Bank (BST), Barcelona, Spain.
Unit of Advanced Therapies, Hospital Clínic de Barcelona, Barcelona, Spain.

Esteve Trias (E)

Unit of Advanced Therapies, Hospital Clínic de Barcelona, Barcelona, Spain.

Unai Perpiña (U)

Stem Cells and Regenerative Medicine Laboratory, Department of Biomedical Sciences, Production and Validation Center of Advanced Therapies (Creatio), Universitat de Barcelona, Barcelona, Spain.

Josep Ma Canals (JM)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Stem Cells and Regenerative Medicine Laboratory, Department of Biomedical Sciences, Production and Validation Center of Advanced Therapies (Creatio), Universitat de Barcelona, Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.

Tycho Baumann (T)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.

Daniel Benítez-Ribas (D)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.

Elías Campo (E)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.
Department of Pathology, Hospital Clínic de Barcelona, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomedical en Red de Cancer, Barcelona, Spain.
Institució Catalana de Recerca i Estudis Avancats, Barcelona, Spain.

Jordi Yagüe (J)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.

Álvaro Urbano-Ispizua (Á)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.
Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.
Department of Biomedicine, School of Medicine, Josep Carreras Leukemia Research Institute, Universitat de Barcelona, Barcelona, Spain.
Immunotherapy Unit Blood and Tissue Bank-Hospital Clínic de Barcelona, Barcelona, Spain.

Susana Rives (S)

Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Déu, Barcelona, Spain.
Institut de Recerca Sant Joan de Déu, Barcelona, Spain.

Julio Delgado (J)

Department of Hematology, Institut Clínic de Malalties Hematològiques i Oncològiques, Hospital Clínic de Barcelona, Barcelona, Spain.
Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.
Centro de Investigación Biomedical en Red de Cancer, Barcelona, Spain.

Manel Juan (M)

Institut D'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Blood and Tissue Bank (BST), Barcelona, Spain.
Department of Immunology, Centro de Diagnóstico Biomédico, Hospital Clínic de Barcelona, Barcelona, Spain.
Hospital Sant Joan de Déu, Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.
Immunotherapy Unit Blood and Tissue Bank-Hospital Clínic de Barcelona, Barcelona, Spain.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH