Efficient hepatic delivery and protein expression enabled by optimized mRNA and ionizable lipid nanoparticle.

Codon optimization Erythropoietin Lipid nanoparticle mRNA delivery mRNA therapy

Journal

Bioactive materials
ISSN: 2452-199X
Titre abrégé: Bioact Mater
Pays: China
ID NLM: 101685294

Informations de publication

Date de publication:
Dec 2020
Historique:
received: 27 05 2020
revised: 02 07 2020
accepted: 04 07 2020
entrez: 22 7 2020
pubmed: 22 7 2020
medline: 22 7 2020
Statut: epublish

Résumé

mRNA is a novel class of therapeutic modality that holds great promise in vaccination, protein replacement therapy, cancer immunotherapy, immune cell engineering

Identifiants

pubmed: 32691013
doi: 10.1016/j.bioactmat.2020.07.003
pii: S2452-199X(20)30130-4
pmc: PMC7355334
doi:

Types de publication

Journal Article

Langues

eng

Pagination

1053-1061

Informations de copyright

© 2020 [The Author/The Authors].

Déclaration de conflit d'intérêts

Z. L. is the founder of Suzhou Ribo Life Science Co. Ltd. The other authors declare no competing financial interests.

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Auteurs

Tongren Yang (T)

School of Life Science, Advanced Research Institute of Multidisciplinary Science, Institute of Engineering Medicine, Key Laboratory of Molecular Medicine and Biotherapy, Beijing Institute of Technology, Beijing, 100081, China.

Chunhui Li (C)

School of Life Science, Advanced Research Institute of Multidisciplinary Science, Institute of Engineering Medicine, Key Laboratory of Molecular Medicine and Biotherapy, Beijing Institute of Technology, Beijing, 100081, China.

Xiaoxia Wang (X)

Institute of Molecular Medicine, Peking University, Beijing, 100871, China.

Deyao Zhao (D)

Institute of Molecular Medicine, Peking University, Beijing, 100871, China.
Department of Radiation Oncology, The First Affiliated Hospital of Zhengzhou University, Erqi, Zhengzhou, 450000, China.

Mengjie Zhang (M)

School of Life Science, Advanced Research Institute of Multidisciplinary Science, Institute of Engineering Medicine, Key Laboratory of Molecular Medicine and Biotherapy, Beijing Institute of Technology, Beijing, 100081, China.

Huiqing Cao (H)

Institute of Molecular Medicine, Peking University, Beijing, 100871, China.

Zicai Liang (Z)

Institute of Molecular Medicine, Peking University, Beijing, 100871, China.
Suzhou Ribo Life Science Co. Ltd., Jiangsu, 215300, China.

Haihua Xiao (H)

Beijing National Laboratory for Molecular Science, State Key Laboratory of Polymer Physical and Chemistry, Institute of Chemistry, Chinese Academy of Science, Beijing, 100190, China.

Xing-Jie Liang (XJ)

Chinese Academy of Sciences (CAS) Key Laboratory for Biomedical Effects of Nanomaterials and Nanosafety, CAS Center for Excellence in Nanoscience, National Center for Nanoscience and Technology of China, Beijing, 100190, China.

Yuhua Weng (Y)

School of Life Science, Advanced Research Institute of Multidisciplinary Science, Institute of Engineering Medicine, Key Laboratory of Molecular Medicine and Biotherapy, Beijing Institute of Technology, Beijing, 100081, China.

Yuanyu Huang (Y)

School of Life Science, Advanced Research Institute of Multidisciplinary Science, Institute of Engineering Medicine, Key Laboratory of Molecular Medicine and Biotherapy, Beijing Institute of Technology, Beijing, 100081, China.
School of Materials and the Environment, Beijing Institute of Technology, Zhuhai, 519085, China.

Classifications MeSH